MedPath

Spinal Muscular Atrophy on Wheels, Using Power Mobility

Not Applicable
Recruiting
Conditions
Spinal Muscular Atrophy
Interventions
Device: power mobility
Registration Number
NCT05589987
Lead Sponsor
University of Castilla-La Mancha
Brief Summary

The group of children diagnosed with Spinal Muscular Atrophy (SMA) has serious restrictions on participation. SMA is a neuromuscular disease that leads to neuromusculoskeletal disorders that limit functional activities, sometimes making it impossible to sit down autonomously and to walk.

Scientific evidence has highlighted the importance of implementing physiotherapy interventions in pediatrics that facilitate the integration and participation of children with reduced mobility in their natural environment through the use of different assisted mobility devices that allow the child to acquire a degree of independence and motivation according to their potential and needs.

For some time, with the aim of offering independent movement opportunities for children with severe motor impairment, adapted electric cars have been used, as they are simple to use and easy for the child and family to incorporate into daily tasks within natural environments. These low-cost motorized devices can generate a very positive impact on the participation of children diagnosed with SMA type I from an early age, after training the family and/or the child himself, guaranteeing the maximum possible safety, comfort, motivation and autonomy.

Due to the above, there is a need to carry out the research project defined below, to generate opportunities for the inclusion of children diagnosed with SMA type I through the use of low-cost electric cars that encourage their participation, motivation and quality of life.

Detailed Description

OBJECTIVES

1. To know the acceptability of an intervention with motorized mobility through electric cars for young children diagnosed with SMA type I.

2. To check the effectiveness of the motorized mobility intervention with electric cars with respect to: (a) mobility and (b) participation of young children with SMA type I with respect to the control group of children who do not use such devices.

3. To identify the barriers and facilitators of the child's participation in their natural environment of a motorized mobility intervention with electric cars in young children with SMA type I.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
20
Inclusion Criteria
  • Diagnosis of SMA type I
  • Ages between 10 months to 5 years.
  • No previous experience with motorized mobility.
Exclusion Criteria
  • severe visual problems
  • Associated disorders that do not correspond to the diagnosis of SMA type I.
  • Families who do not agree to have training in the use of the electric car and continuous monitoring by the corresponding researcher.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Power mobilitypower mobilityThe study will take place in the child's natural environment for 12 weeks.
Primary Outcome Measures
NameTimeMethod
YC-PEM (Young Children's Participation & Environment Measure)baseline, Change from basaline at week 12 and Change from basaline at week 16

to be used for children from zero to five years, explores the frequency of participation in activities. Parents will report their child's participation across home, community and childcare

Photovoicebaseline,Change from basaline at week 12

to record and present everyday realities using photography; promote dialogue and critical reflection of reality and know the strengths and weaknesses of the target audience; and reach decision makers

QUEST (Version 2.0) Quebec User Evaluation of Satisfaction with assistive Technologybaseline and Change from basaline at week 12

the scale includes 12 items rated on a 5-point satisfaction scale. approximately 10-15 minutes are require to complete the evaluation.

Pediatric Evaluation of Disability Inventory-Computer Adaptive-test (PEDI-CAT)baseline, Change from basaline at week 12 and Change from basaline at week 16

It is answered by the children's caregiver and has an item bank divided into two domains:

(1) mobility, which includes 75 items ranging from basic motor skills (e.g., sitting without support) to more difficult motor skills (e.g., running or climbing a step ladder). Additionally, this domain includes the use of walking devices; (2) cognitive/social, which includes 60 items related to interaction (e.g., follows the gaze of another person), communication (e.g., uses gestures to ask for something), everyday cognition (e.g., recognizes his/her name), and self-management (e.g., when upset response without hitting). In these domains, the four-point scores (unable, hard, a little hard, easy) are based on different levels of difficulty. The overall score is transformed in a normative score (based on age) and a continuous score that will be used in the analyses.

Secondary Outcome Measures
NameTimeMethod
Goal Attainment Scaling (GAS)baseline, Change from basaline at week 12

GAS is an objective method of quantifying goal attainment. Goals are scored on a Likert-type scale from -2 (representing no positive change at all from baseline/ regression), -1 (a little less change than expected), 0 (attainment of goal at the expected level), +1 (a little more change than expected), to +2 (attainment of goal at much more than the expected level)

Switch Activationat the end of week 4, 8, and week 12

Switch activation is defined as when the switch is pressed to activate the modified ride-on car and make it "go", thereby moving in space from one place to another

Daily driving journalbaseline, week 12 and week 16

Parents will record the date, duration (minutes) location, and activities during each driving session in a daily driving journal.

Trial Locations

Locations (2)

University of Castilla-La Mancha

🇪🇸

Toledo, Spain

Rocío Castilla-La Palomo-Carrión

🇪🇸

Toledo, Castilla-La Mancha/Toledo, Spain

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