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Clinical Trials/NL-OMON54546
NL-OMON54546
Recruiting
Not Applicable

Implementation of pharmacokinetic-guided dosing of DDAVP and VWF-containing concentrates in von Willebrand disease - OPTI-CLOT: To Wi

Overview

Phase
Not Applicable
Intervention
Not specified
Conditions
Not specified
Sponsor
Erasmus MC, Universitair Medisch Centrum Rotterdam
Enrollment
160
Status
Recruiting
Last Updated
2 years ago

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
TBD
End Date
TBD
Last Updated
2 years ago
Study Type
Interventional

Investigators

Eligibility Criteria

Inclusion Criteria

  • \- No minimum or maximum age at inclusion date;
  • \- Hemorrhagic symptoms or a family history of von Willebrand disease with
  • historically lowest levels of VWF:Ag \<0\.60 IU/ml and/or VWF:Act \<0\.60 IU/ml
  • and/or VWF:CB \<0\.60 and/or FVIII \<0\.40 IU/ml;
  • \- Need for DDAVP\-testing (arm A); and/or
  • \- Need for a medical intervention requiring DDAVP and/or VWF replacement
  • therapy (arm B) (arm B); or
  • \- (Future) Bleeding requiring DDAVP and/or VWF replacement therapy (arm C); or
  • \- Receiving or requiring prophylaxis with VWF\-containing concentrate due severe
  • and/or recurrent bleeding episode (arm D).

Exclusion Criteria

  • \- Any other known hemostatic abnormalities;
  • \- Acquired VWD;
  • \- Presence of VWF antibodies (\>0\.2 BU)
  • \- Withdrawal of (parental) informed consent.

Outcomes

Primary Outcomes

Not specified

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