MedPath

Study Evaluating Neratinib Versus Lapatinib Plus Capecitabine For ErbB2 Positive Advanced Breast Cancer

Phase 2
Completed
Conditions
Advanced Breast Cancer
Breast Cancer
Interventions
Registration Number
NCT00777101
Lead Sponsor
Puma Biotechnology, Inc.
Brief Summary

This is a study of an experimental drug (neratinib) versus a combination of drugs (lapatinib and capecitabine) in women who have erbB-2 (HER-2) positive metastatic or locally advanced breast cancer. The goal of this study is to compare the two regimens in shrinking tumors and extending the lives of women with erbB2 (HER2) positive breast cancer. The study will also compare the safety of the two regimens and to compare quality of life of patients taking the two regimens.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
233
Inclusion Criteria
  • Stage IIIB, IIIC, or IV erbB2 (HER2) positive breast cancer
  • Prior use of Herceptin (trastuzumab), and a taxane
  • Adequate cardiac and renal function
Exclusion Criteria
  • More than 2 prior Herceptin (trastuzumab) regimens or prior use of Xeloda (capecitabine) and / or Tykerb (lapatinib) [Tyverb]
  • Bone as the only site of disease
  • Active central nervous system metastases (subjects should be stable and off anticonvulsants and steroids)
  • Significant gastrointestinal disorder with diarrhea as major symptom

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
NeratinibNeratinib-
Lapatinib plus CapecitabineLapatinib-
Lapatinib plus CapecitabineCapecitabine-
Primary Outcome Measures
NameTimeMethod
Progression Free SurvivalFrom randomization date to progression or death, assessed up to 69 months

Progression Free Survival, Measured in Months, for Subjects Randomized. Investigator assessment. The time interval from the date of randomization until the earliest date of progression per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) or death due to any cause. For subjects without death or progression, censorship was at the last valid tumor assessment.

Secondary Outcome Measures
NameTimeMethod
Overall Survival (OS)From randomization date to death, assessed up to 69 months

Overall Survival (OS) was defined as the time from randomization to death due to any cause. Subjects last known to be alive were censored at the last date of last contact or the data cutoff employed for the analysis, whichever was earlier.

Clinical Benefit RateFrom randomization date to progression or last tumor assessment, assessed up to 69 months

Clinical benefit rate (CR, PR, or SD = 24 weeks) for women For ErbB2 Positive Advanced Breast Cancer. Clinical benefit rate was the percentage of subjects who achieved overall tumor response per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) v1.0: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Stable Disease (SD), Neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD, taking as reference the smallest sum diameters while on study.

Clinical Benefit (CB) = CR + PR + SD \>= 24 weeks.

Objective Response Rate (ORR).From randomization date to progression or last tumor assessment, assessed up to 69 months

Objective Response Rate, investigator assessment. The ORR was defined as the percentage of participants demonstrating a confirmed objective response, either Complete Response (CR) or Partial Response (PR) during the study per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) v.1.0: Complete Response (CR), disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; and Non-PD for non-target lesions, and no new lesions.

Duration of ResponseFrom start date of response to first PD, assessed up to 69 months after the first subject was randomized.

Duration of response was measured from the time at which response criteria were met for complete response (CR) or partial response (PR) (whichever status was recorded first) until the first date of recurrence or progressive disease (PD) or death. For subjects without death or progression, censorship was at the last valid tumor assessment per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) v1.0: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions.

Time to CNS MetastasesFrom randomization date to first CNS symptom or lesions

Time to symptomatic or progressive Central nervous system (CNS) lesions. Time to symptomatic or progressive CNS lesions was the time from the date of randomization until the date of progressive disease (PD) considering CNS lesions only (ie, appearance of newly diagnosed CNS lesions or progressive CNS lesions).

Frequency of CNS Metastases (Frequency)From randomization date to first CNS symptom or lesions

The percent of patients with symptomatic or progressive CNS lesions was the proportion of subjects who had PD considering CNS lesions only, according to RECIST criteria.

Trial Locations

Locations (152)

The Medical Oncology Centre of Rosebank

🇿🇦

Johannesburg, Gauteng, South Africa

Division of Medical Oncology, Department of Medicine

🇹🇭

Bangkok-noi, Bangkok, Thailand

Broomfield Hospital

🇬🇧

Chelmsford, Essex, United Kingdom

University of Florida

🇺🇸

Jacksonville, Florida, United States

Mercy Research Institute

🇺🇸

Miami, Florida, United States

Oncology Partners Network

🇺🇸

Cincinnati, Ohio, United States

Oca Hospital / Monterrey International Research Center

🇲🇽

Monterrey, Nuevo Leon, Mexico

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

AKH Wien Universitaetsklinik fuer Innere Medizin I Klinische Abteilung für Onkologie

🇦🇹

Wien, Austria

BC Cancer Agency - Vancouver Centre

🇨🇦

Vancouver, British Columbia, Canada

University of Oklahoma Health Sciences Center Dept. of Hematology Oncology

🇺🇸

Oklahoma City, Oklahoma, United States

Northwest Cancer Specialists, PC

🇺🇸

Portland, Oregon, United States

Hakuaikai Medical Corporation Sagara Hospital

🇯🇵

Kagoshima, Japan

Purchase Cancer Group

🇺🇸

Paducah, Kentucky, United States

Ashland-Bellefonte Cancer Center

🇺🇸

Ashland, Kentucky, United States

MetroHealth Medical Center, Cancer Care Center

🇺🇸

Cleveland, Ohio, United States

HOPE Oncology

🇺🇸

Richardson, Texas, United States

The Center for Cancer and Blood Disorders

🇺🇸

Fort Worth, Texas, United States

Hematology Oncology Associates, P.C.

🇺🇸

Stamford, Connecticut, United States

Redwood Regional Medical Group, Inc.

🇺🇸

Santa Rosa, California, United States

Hematology Oncology Associates

🇺🇸

Loxahatchee Groves, Florida, United States

Hematology Oncology Associates of the Treasure Coast

🇺🇸

Port Saint Lucie, Florida, United States

Cancer Centers of Florida

🇺🇸

Orlando, Florida, United States

Cancer Care Specialists Of Central Illinois

🇺🇸

Decatur, Illinois, United States

Oncology Specialists, SC

🇺🇸

Park Ridge, Illinois, United States

Floyd Memorial Cancer Center of Indiana

🇺🇸

New Albany, Indiana, United States

Weill Cornell Medical College New York-Presbyterian Hospital Weill, Cornell Breast Center

🇺🇸

New York, New York, United States

Hematology Oncology of Indiana

🇺🇸

Indianapolis, Indiana, United States

New York Oncology Hematolgy, PC

🇺🇸

Troy, New York, United States

Lancaster Cancer Center

🇺🇸

Lancaster, Pennsylvania, United States

Cookeville Regional Medical Center

🇺🇸

Cookeville, Tennessee, United States

Center for Biomedical Research

🇺🇸

Knoxville, Tennessee, United States

Thompson Cancer Survival Center Thompson Oncology Group

🇺🇸

Knoxville, Tennessee, United States

Texas Oncology, P.A.

🇺🇸

Austin, Texas, United States

University of Tennessee Cancer Institute

🇺🇸

Memphis, Tennessee, United States

Cancer Care Network of South Texas-HOAST

🇺🇸

San Antonio, Texas, United States

Medical Oncology Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

UMHAT Tzaritza Yoanna

🇧🇬

Sofia, Bulgaria

District Dispensary for Oncology Diseases Internal Unit- Sofia EOOD, Dept. of Chemotherapy

🇧🇬

Sofia, Bulgaria

Mount Hospital

🇦🇺

West Perth, Australia

Institut Jules Bordet Unite du Chimiotherapie

🇧🇪

Brussels, Belgium

Interdistrict Dispensary for Oncology Diseases -Internal Unit- Department Oncotherapy and Palliative Care

🇧🇬

Varna, Bulgaria

University Hospital Center Zagreb

🇭🇷

Zagreb, Croatia

Centre Hospitalier Affilie Universitaire de Quebec Hopital du St-Sacrement

🇨🇦

Quebec, Canada

General Hospital Varazdin

🇭🇷

Varazdin, Croatia

University Hospital Sestre Milosrdnice

🇭🇷

Zagreb, Croatia

Fakultni nemocnice Olomouc Klinika onkologie

🇨🇿

Olomouc, Czechia

Centre Oscar Lambret Departement de senologie

🇫🇷

Lille, France

Centre Hospitalier Lyon Sud

🇫🇷

Pierre Benite, France

Nationales Centrum fuer Tumorerkrankungen Sektion Gynaekologische Onkologie

🇩🇪

Heidelberg, Germany

CHU de Poitiers Service d'oncologie medicale

🇫🇷

Poitiers, France

Institut Gustave ROUSSY Service de Pathologie mammaire

🇫🇷

Villejuif, France

Universitaetsklinikum Hamburg-Eppendorf Klinik und Poliklinik fuer Gynaekologie

🇩🇪

Hamburg, Germany

Theagenio Anticancer Hospital of Thessaloniki

🇬🇷

Thessaloníki, Greece

Department of Clinical Oncology, Tuen Mun Hospital

🇭🇰

Hong Kong, Hong Kong

Josa Andras Oktatokorhaz / Onkoradiologiai Osztaly

🇭🇺

Nyiregyhaza, Hungary

Bacs-Kiskun Megyei Korhaz Onkoradiologiai Kozpont

🇭🇺

Kecskemet, Hungary

Fovarosi Onkormanyzat Szent Janos Korhaza es Eszak-budai Egyesitett Korhazai, Onkologia

🇭🇺

Budapest, Hungary

Istituto Regina Elena, Struttura Complessa Oncologia Medica A

🇮🇹

Roma, Italy

Orszagos Onkologiai Intezet "B" Belgyogyaszati osztaly

🇭🇺

Budapest, Hungary

Szegedi Tudomanyegyetem Onkoterapias Klinika

🇭🇺

Szeged, Hungary

Aichi Cancer Center

🇯🇵

Aichi, Japan

National Hospital Organization Hokkaido Cancer Center

🇯🇵

Sapporo, Hokkaido, Japan

National Hospital Organization Kyushu Cancer Center

🇯🇵

Fukuoka, Japan

Hiroshima City Hospital

🇯🇵

Hiroshima, Japan

National Cancer Center Hospital

🇯🇵

Tsukiji, Tokyo, Japan

Chiba Cancer Center

🇯🇵

Chiba, Japan

Kyoto University Hospital

🇯🇵

Kyoto, Japan

National Cancer Center Hospital East

🇯🇵

Chiba, Japan

Saitama Cancer Center

🇯🇵

Saitama, Japan

Jichi Medical University Hospital

🇯🇵

Tochigi, Japan

National Hospital Organization Osaka National Hospital

🇯🇵

Osaka, Japan

Niigata Cancer Center Hospital

🇯🇵

Niigata, Japan

St. Luke's International Hospital

🇯🇵

Tokyo, Japan

King Hussein Cancer Centre

🇯🇴

Amman, Jordan

Yonsei University Health System - Severance Hospital

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Bialostockie Centrum Onkologii im. M. Sklodowskiej-Curie w Bialymstoku Specjalistyczny Szpital Onkologiczn

🇵🇱

Bialystok, Poland

Uniwersyteckie Centrum Kliniczne w Gdansku Klinika Onkologii i Radioterapii

🇵🇱

Gdansk, Poland

Szpital Uniwersytecki w Krakowie Oddzial KIiniczny Kliniki Onkologii

🇵🇱

Krakow, Poland

Centrum Onkologii Ziemi Lubelskiej im. SW. Jana z Dukli

🇵🇱

Lublin, Poland

Metropolitan Oncology Center

🇵🇷

San Juan, Puerto Rico

Institutul Oncologic "Prof. Dr. Alex. Trestioreanu"

🇷🇴

Bucuresti, Romania

Spitalul Universitar de Urgenta

🇷🇴

Bucuresti, Romania

Scientific Research Institute of Oncology N.N. Petrov

🇷🇺

Pesochny, Saint Petersburg, Russian Federation

Spitalul Clinic Judetean

🇷🇴

Sibiu, Romania

GUZ Perm Regional Oncology Dispensary

🇷🇺

Perm, Russian Federation

SIH Leningrad Regional Oncology Dispensary

🇷🇺

Saint Petersburg, Russian Federation

Klinicko Bolnicki Centar (KBC) Bezanijska Kosa (Medical Centre ''Bezanijska Kosa'' (MCBK))

🇷🇸

Belgrade, Serbia

SIH Oncology Dispensary # 2 Of Department of Public Health

🇷🇺

Sochi, Russian Federation

St. Petersburg State Medical University I.P.Pavlov of Roszdrav

🇷🇺

Saint Petersburg, Russian Federation

Eastleigh Breast Care Centre

🇿🇦

Lynnwood, Gauteng, South Africa

Corporacio Sanitaria Parc Tauli Servicio de Oncologia

🇪🇸

Sabadell, Barcelona, Spain

Hospital Mutua de Terrassa Servicio de Oncologia

🇪🇸

Terrassa, Barcelona, Spain

Hospital Clinico Universitario de Valencia Servicio de Hematologia y Oncologia

🇪🇸

Valencia, Spain

Abteilung fuer Onkologie Departement für Innere

🇨🇭

Zuerich, Switzerland

Royal Marsden NHS Foundation Trust & Institute of Cancer Research

🇬🇧

London, United Kingdom

The Royal Marsden NHS Foundation Trust & Institute of Cancer Research

🇬🇧

London, United Kingdom

UC Irvine Medical Center

🇺🇸

Orange, California, United States

Arizona Oncology Associates HOPE

🇺🇸

Tucson, Arizona, United States

Rocky Mountain Cancer Center

🇺🇸

Denver, Colorado, United States

Centro Oncologico M.D. Anderson Internacional

🇪🇸

Madrid, Spain

Palm Beach Institute of Hematology & Oncology

🇺🇸

Boynton Beach, Florida, United States

Centro Hospitalario de Jaen Servicio de Oncologia

🇪🇸

Jaen, Spain

Central Indiana Cancer Centers

🇺🇸

Fishers, Indiana, United States

Owsley Brown Frazier Cancer Center (OBFCC)

🇺🇸

Louisville, Kentucky, United States

Mater Private Centre for HOCA

🇦🇺

South Brisbane, Queensland, Australia

Western Hospital

🇦🇺

Footscray, Victoria, Australia

Hospital of County Veszprem

🇭🇺

Veszprem, Hungary

Ospedale Misericordia e Dolce c/o UO Oncologia Medica

🇮🇹

Prato, Italy

Hyogo Cancer Center

🇯🇵

Hyogo, Japan

Kumamoto Municipal Hospital

🇯🇵

Kumamoto, Japan

Tokai University Hospital

🇯🇵

Kanagawa, Japan

Shizuoka Cancer Center

🇯🇵

Shizuoka, Japan

The Cancer Institute Hospital of Japanese Foundation for Cancer Research Department of Medical Oncology

🇯🇵

Tokyo, Japan

Tokyo Metropolitan Cancer&Infectious disease Ctr Komagome Hp

🇯🇵

Tokyo, Japan

Centrul de Oncologie Medicala

🇷🇴

Iasi, Romania

Ryazan State Medical University I.P.Pavlov of Federal Agency in Healthcare and Social Development

🇷🇺

Ryazan, Russian Federation

Russian Oncology Research Centre of RAMS

🇷🇺

Moscow, Russian Federation

GUZ City Clinical Oncology Dispensary

🇷🇺

Saint Petersburg, Russian Federation

Republican Clinical Oncology Dispensary of Ministry of Healthcare of Bashkortostan Republic

🇷🇺

Ufa, Russian Federation

Institute of Oncology and Radiology of Serbia

🇷🇸

Belgrade, Serbia

Johns Hopkins Singapore International Medical Centre

🇸🇬

Singapore, Singapore

Institute for Oncology Department for Medical Oncology

🇸🇮

Ljubljana, Slovenia

Hospital Central de Asturias Servicio de Oncologia, Planta Baja Oeste, Edificio Principal

🇪🇸

Oviedo, Asturias, Spain

GVI Oncology Trial Unit Room 110 Panorama Medical Centre

🇿🇦

Kraaifontein, Western Cape Province, South Africa

Hospital San Pedro de Alcantara Servicio de Oncologia

🇪🇸

Caceres, Spain

Complejo Hospitalario U. de A Coruña Hospital Teresa Herrera Servicio de Oncologia

🇪🇸

A Coruña, Spain

Hospital General Universitario de Alicante Servicio de Oncologia

🇪🇸

Alicante, Spain

Hospital Provincial (Reina Sofia) Servicio de Oncologia

🇪🇸

Cordoba, Spain

Hospital Universitario Dr. Josep Trueta Servicio de Oncologia

🇪🇸

Gerona, Spain

Hospital Universitario Miguel Servet Servicio de Oncologia

🇪🇸

Zaragoza, Spain

Instituto Valenciano de Oncologia Servicio de Oncologia

🇪🇸

Valencia, Spain

University of Lausanne Hospitals CHUV

🇨🇭

Lausanne, Switzerland

Kantonsspital Winterthur Medizinische Onkologie

🇨🇭

Winterthur, Switzerland

Aptium Oncology/Comprehensive Cancer Center at Desert Regional Medical Center

🇺🇸

Palm Springs, California, United States

Robert R. Carroll, MD, PA

🇺🇸

Gainesville, Florida, United States

Allegheny General Hospital Allegheny Cancer Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Southwest Cancer Care

🇺🇸

Murrieta, California, United States

Missouri Cancer Associates

🇺🇸

Columbia, Missouri, United States

Midwestern Regional Medical Center

🇺🇸

Zion, Illinois, United States

Arena Oncology Associates, PC

🇺🇸

Lake Success, New York, United States

Capitol Comprehensive Cancer Care Clinic

🇺🇸

Jefferson City, Missouri, United States

El Paso Cancer Treatment Center - West

🇺🇸

El Paso, Texas, United States

Hopelands Oncology Centre

🇿🇦

Durban, KwaZulu Natal, South Africa

East Texas Medical Center Cancer Institute, Tyler Hematology Oncology

🇺🇸

Tyler, Texas, United States

Hospital Gregorio Marañon Servicio de Oncologia

🇪🇸

Madrid, Spain

National Cancer Center

🇰🇷

Goyang-si, Gyeonggi-do, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Korea, Republic of

Hospital Germans Trias i Pujol Servicio de Oncologia

🇪🇸

Badalona, Barcelona, Spain

Queen Mary Hospital

🇭🇰

Hong Kong, Hong Kong

UNIMED Medical Institute, Comprehensive Centre for Breast Diseases

🇭🇰

Hong Kong, Hong Kong

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