MedPath

What is the Optimal Follow-up for Patients With Systemic Sclerosis?

Not Applicable
Not yet recruiting
Conditions
Systemic Sclerosis
Interventions
Other: Outpatient Clinic
Registration Number
NCT05103553
Lead Sponsor
Leiden University Medical Center
Brief Summary

Systemic sclerosis (SSc) is a complex multisystem rheumatic autoimmune disease. Currently, evidence based guidelines for frequency and intensity of follow-up of SSc patients are not available. Based on expert consensus annual extensive evaluation is recommended. To provide comprehensive multidisciplinary care integrated with evaluation of organ involvement and as such, reducing health care utilization while improving the quality of care for the patient, the "Leiden Combined Care in SSc (CCISS) pathway" was started in 2009. Data collected on disease progression in the patients that participate in this care pathway show that 50% of the patients have relatively mild disease, without any disease progression over time. Therefore there is a need for tailor made care in SSc patients in accordance to disease activity. To enable this, a prediction model was developed that can identify patients with low risk for disease progression.

Detailed Description

Objectives: To evaluate in SSc patients with low risk for disease progression 1) whether assessment in an outpatient clinic setting is an acceptable alternative for evaluation in the Care Pathway. Outcome parameters we will evaluate include 1) health care utilization, 2) patients' perception of the disease and delivery of care, 3) health-related quality of life and 4) disease progression. Health care utilization as primary outcome is defined as number of contacts with heath care providers during 12 months.

Study population: Patients with a clinical diagnosis of SSc that participated in the Combined Care in Systemic Sclerosis cohort from Leiden University Medical Center (LUMC), or in the comparable care pathway of the Haga hospital and Haaglanden Medical Center (HMC), and that have had at least two care pathway evaluations are eligible to participate in this study.

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
250
Inclusion Criteria
  1. Participation in the prospective Haga, HMC or LUMC cohort
  2. Clinical diagnosis of SSc
  3. Age of ≥18 years
  4. >= two evaluations in the Care Pathway
  5. Low or intermediate risk for disease progression according to the prediction model
  6. Written informed consent
Exclusion Criteria
  1. Patients with SSc who are part of ongoing (randomized) trials
  2. Patients who have had an autologous stem cell transplantation in the past five years
  3. Patients with SSc who were categorized as high risk for disease progression according to the prediction model.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Annual screening at outpatient clinicOutpatient ClinicAfter signing informed consent, patients with low risk for disease progression (in the low or intermediate risk group) wil be randomized into the intervention group (annual assessment at the outpatient clinic). Due to the nature of the intervention, the randomization will not be blinded, as this is not possible.
Primary Outcome Measures
NameTimeMethod
Health care utilization BaselineBaseline

Includes different health-care services: rheumatologist, other medical specialists, General Practioner (GP), health professionals, hospital admission, hospital based day-care. Number of contacts/visits within previous 6 months will be counted.

Health care utilization after 6 months6 months

Includes different health-care services: rheumatologist, other medical specialists, General Practioner (GP), health professionals, hospital admission, hospital based day-care. Number of contacts/visits within previous 6 months will be counted.

Health care utilization after 12 months12 months

Includes different health-care services: rheumatologist, other medical specialists, General Practioner (GP), health professionals, hospital admission, hospital based day-care. Number of contacts/visits within previous 6 months will be counted.

Health care utilization after 18 months18 months

Includes different health-care services: rheumatologist, other medical specialists, General Practioner (GP), health professionals, hospital admission, hospital based day-care. Number of contacts/visits within previous 6 months will be counted.

Health care utilization after 24 months24 months

Includes different health-care services: rheumatologist, other medical specialists, General Practioner (GP), health professionals, hospital admission, hospital based day-care. Number of contacts/visits within previous 6 months will be counted.

Secondary Outcome Measures
NameTimeMethod
health-related quality of life using 36-item short form survey (SF-36)Baseline, 6 months, 12 months, 18 months, 24 months

SF-36 is a set of generic, coherent, and easily administered quality-of-life measures. Rely upon patient self-reporting.

health-related quality of life using EuroQol 5D (EQ5D)Baseline, 6 months, 12 months, 18 months, 24 months

comprises 5 dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. each dimension has 5 levels varying from no problems until extreme problems. Each answer results in a 1-digit number that expresses the level selected for that dimension. The digits for the five dimensions can be combined into a 5-digit number that describes the patient's health state.The EQ visual analogue scale (VAS) records the patient's self-rated health on a vertical visual analogue scale, where the endpoints are labelled 'The best health you can imagine' and 'The worst health you can imagine'. The VAS can be used as a quantitative measure of health outcome that reflect the patient's judgement.

Disease progressionBaseline, 6 months, 12 months, 18 months, 24 months

Defined as progression in different organ systems.

Illness perception using the validated instrument Brief Illness Perception Questionnaire (BIPQ )Baseline, 6 months, 12 months, 18 months, 24 months

A nine-item scale designed to rapidly assess the cognitive and emotional representations of illness. Each question is be answered with a number on a scale of 0 until 10.

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