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Reduction by Pasireotide of the Effluent Volume in High-output Enterostomy in Patients Refractory to Usual Medical Treatment

Phase 2
Completed
Conditions
Enterostomy
Interventions
Drug: Placebo
Registration Number
NCT02713776
Lead Sponsor
Hospices Civils de Lyon
Brief Summary

During rectal or complex digestive surgery with multiple digestive resections and anastomosis, the creation of enterostomy is a common procedure. In France, it is estimated that 20000 patients have an ileostomy and 16000 new digestive stomas are formed each year with approximately 30% of enterostomy. Enterostomy might sometimes give high-output not controlled with usual medical treatment (e.g loperamide ± codeine) and exposes the patients to important hydro-electrolytic loss leading to a risk for dehydration, electrolyte abnormalities and acute renal failure. This risk implies parenteral correction which may extend hospital stay and delay home return.

Somatostatin analogues (octreotide, lanreotide and pasireotide) could reduce digestive secretions and decrease digestive peristalsis. Nevertheless, somatostatin analogues are not routinely used for the treatment of patients with high-output enterostomy and their efficacy in the indication (off-label) was only tested in small case series. Pasireotide (SOM230, SIGNIFOR®) is currently indicated for the treatment of patients with Cushing's disease for whom surgery is not an option or for whom surgery has failed.

As the efficacity of pasireotide in patients with high-output enterostomy refractory to usual medical treatment associated with an oral fluid restriction has never been demonstrated before, there is a need to perform a pilot, double-blind, randomized, placebo-controlled trial evaluating its impact on reduction of the effluent volume.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
57
Inclusion Criteria
  • Male and Female patients ≥ 18 years old ;
  • Patients who underwent an intestinal surgery with enterostomy repair in the three weeks preceding the inclusion ;
  • Patients with high-output ileostomy or jejunostomy > 1000 ml/24h ;
  • Patients with failure of treatment combining oral fluid restriction and loperamide (up to 8 capsules/24h) +/- codeine syrup (10 mg x 3/24h) during 5 days ;
  • Patients who gave its written informed consent to participate to the study ;
  • Patients affiliated to a social insurance regime.
Exclusion Criteria
  • Male and Female patients < 18 years old ;
  • Patients who did not give its written informed consent to participate to the study ;
  • Patients who received somatostatin analogues during the month before inclusion ;
  • Patients with symptomatic cholelithiasis or acute or chronic pancreatitis ;
  • Patients with uncontrolled diabetes (with HbA1c (glycated hemoglobin) > 8%) ;
  • Patients who are hypothyroid and not on adequate replacement therapy ;
  • Patients who have congestive heart failure (NYHA (New York Heart Association) Class III or IV), unstable angina, sustained ventricular tachycardia, ventricular fibrillation, advanced heart block or a history of clinically significant bradycardia or acute myocardial infarction within the 6 months preceding randomization ;
  • Patients with history of syncope or family history of idiopathic sudden death ;
  • Patients with screening or baseline (predose) : QT interval corrected for heart rate using Fridericia's correction (QTcF) QTcF > 450 msec (male), QTcF > 460 msec (female) (QT interval corrected for heart rate using Fridericia's correction) ;
  • Patients with not corrected hypokalaemia and/or hypomagnesaemia ;
  • Patients with liver disease such as cirrhosis, chronic active hepatitis, or chronic persistent hepatitis, or patients with alanine transaminase/aspartate transaminase (ALT/AST) > 2 x Upper Limit of Normal (ULN), serum bilirubin > 2 x ULN ;
  • Patients with Child-Pugh C cirrhosis ;
  • Female patients who are pregnant or lactating, or are of childbearing potential and not practicing a medically acceptable method of birth control ;
  • Patients with abnormal coagulation (PT and/or APTT elevated by 30% above normal limits) or patients receiving anticoagulants that affect PT (prothrombin time) or activated partial thromboplastin time (APTT) ;
  • Patients with known hypersensitivity to somatostatin analogues or any other component of the pasireotide LAR ;
  • Patients under guardianship ;
  • Patients nonaffiliated to a social insurance regime.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboPlacebo by subcutaneous injection twice a day during 3 days and 1 intramuscular injection of placebo on Day 4 morning.
PasireotidePasireotidePasireotide 0.9 mg by subcutaneous injection twice a day during 3 days and 1 intramuscular injection of pasireotide Long Acting Release (LAR) 60mg on Day 4 morning.
Primary Outcome Measures
NameTimeMethod
Compare the efficacy of pasireotide versus placebo in reduction of high-outputEvaluated 72 hours after first injection of treatment

Decrease of enterostomy output (ml/24H)within the 72 hours after first injection of treatment

Secondary Outcome Measures
NameTimeMethod
Estimate the success rate of pasireotide and placebo1 week after first injection of treatment

Number of normal renal function patients in both arms with an enterostomy output than 800 millimeters (mL) /24h within a week after first injection of treatment allowing discontinuation of intravenous perfusion.

Incidence of treatment - Emergent Adverse Eventsduring treatment (4 days), one week, two weeks, three weeks and one month after treatment

Nature, number and grade of adverse events observed throughout the study

Compare the incidence of premature closure of stoma due to high-output with pasireotide versus placebo2 months after enterostomy creation

Rate of premature closure of stoma due to high-output (before 2 months after creation) in both arms

Evaluate the economic impact of pasireotide in this indication2 months from the inclusion of the patient in the study

Costs of taking care of patients from French Public Health Insurance perspective in both arms

Compare the decrease in the length of hospitalization with pasireotide versus placebo1 month after the end of treatment

Duration of hospitalization in days in both arms

Trial Locations

Locations (14)

Centre Leon Berard

🇫🇷

Lyon, France

Centre Hospitalier Lyon Sud

🇫🇷

Pierre-Bénite, France

Chu Albert Michallon

🇫🇷

La Tronche, France

Bordeaux Chu - Hopital Haut-Leveque

🇫🇷

Pessac, France

Hopital Saint Antoine

🇫🇷

Paris, France

Hopital Beaujon

🇫🇷

Clichy, France

Institut Regional Du Cancer Val D'Aurelle

🇫🇷

Montpellier, France

Chu Rouen Ch. Nicolle

🇫🇷

Rouen, France

Chu Caremeau

🇫🇷

Nîmes, France

Chu Estaing

🇫🇷

Clermont-Ferrand, France

Chu Amiens-Picardie

🇫🇷

Amiens, France

Hôpital Claude HURIEZ - CHRU Lille

🇫🇷

Lille, France

Chu Marseille - Hopital Nord

🇫🇷

Marseille, France

Toulouse - Chu Purpan

🇫🇷

Toulouse, France

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