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Clinical Trials/JPRN-jRCTs041200037
JPRN-jRCTs041200037
Active, not recruiting
Phase 4

A prospective, multicenter study to evaluate the safety of emicizumab under and after immune tolerance induction in patients with congenital hemophilia A with FVIII inhibitors

Matsushita Tadashi0 sites15 target enrollmentAugust 3, 2020

Overview

Phase
Phase 4
Intervention
Not specified
Conditions
Congenital hemophilia A with FVIII inhibitors
Sponsor
Matsushita Tadashi
Enrollment
15
Status
Active, not recruiting
Last Updated
2 years ago

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
August 3, 2020
End Date
TBD
Last Updated
2 years ago
Study Type
Interventional
Sex
All

Investigators

Sponsor
Matsushita Tadashi

Eligibility Criteria

Inclusion Criteria

  • Patients must meet all of the following criteria for study entry:
  • 1\) Informed Consent Form signed by the patient or the patient's legally authorized representative. Pediatric patients who are capable: Informed Assent Form signed by the patient
  • 2\) Patient or caregiver: Willing and able to comply with all study procedures (including filling out questionnaires on bleeds/drugs used)
  • 3\) Diagnosed with congenital hemophilia A and meets either of the following criteria:
  • a. Will start ITI after study enrollment and has positive FVIII inhibitor titer ( \>\= 0\.6 BU/mL) as evidenced by most recent titer results within 8 weeks before enrollment
  • b. Is already undergoing ITI at study enrollment and has not yet met partial success as evidenced by most recent titer results within 8 weeks before enrollment

Exclusion Criteria

  • Patients who meet any of the following criteria will be excluded from study entry:
  • 1\) Inherited or acquired bleeding disorder other than congenital hemophilia A
  • 2\) Previous (within the last 12 months) or current treatment for thromboembolic disease (with the exception of previous catheter\-associated thrombosis for which anti\-thrombotic treatment is not currently ongoing) or high risk for thromboembolic diseases(e.g. protein S deficiency)
  • 3\) At high risk for thrombotic microangiopathy (TMA) in the opinion of the investigator based on previous or familial history of TMA (e.g., thrombotic thrombocytopenic purpura \[TTP], atypical hemolytic uremic syndrome \[aHUS])
  • 4\) Participating or planning to participate in other intervention trials
  • 5\) Otherwise unsuitable for study participation in the opinion of the investigator

Outcomes

Primary Outcomes

Not specified

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