MedPath

Direct Acting Antiviral-Post Authorization Safety Study

Completed
Conditions
Hepatocellular Carcinoma
Hepatitis C
Registration Number
NCT03707080
Lead Sponsor
Target PharmaSolutions, Inc.
Brief Summary

This is an independent optional sub-study parallel to TARGET-HCC (NCT02954094). The purpose of Direct-Acting Antiviral-Post Authorization Safety Study (DAA-PASS) is to investigate the impact of exposure to direct-acting antivirals (DAAs) on early recurrence of hepatocellular carcinoma (HCC) in hepatitis C virus (HCV)-infected patients following successful HCC treatment interventions.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
42
Inclusion Criteria
  • Current participant in TARGET-HCC
  • Adults, age ≥18 years
  • First diagnosis of HCC (mixed HCC/cholangiocarcinoma may be included). Diagnosis may be histological/cytological and/or radiological.
  • BCLC Stage A
  • Underwent, undergoing, or planned to undergo therapy for HCC, with exception that transplant as prior or planned treatment for HCC is excluded.
  • HCV RNA positive

Screening

Exclusion Criteria
  • Inability to provide informed consent
  • HCC-free imaging (as defined in Section 9.1.1) after treatment of initial HCC prior to Screening (see Section 9.2.9 for imaging details)
  • Prior liver transplantation
  • Hepatitis B Virus (HBV) surface antigen positive (HBsAg)
  • Previously treated with direct-acting antiviral agents (not DAA-naïve); Note that prior (peg)IFN and/or ribavirin therapy is allowed

Enrollment Inclusion Criteria:

  • Continued participation in TARGET-HCC
  • No recurrence or progression of initial HCC beyond BCLC Stage A prior to Enrollment/Baseline
  • HCC-free imaging (as defined in Section 9.1.1) at Enrollment/Baseline (see Section 9.2.9 for imaging details; participants may remain in Screening until an HCC-free image is obtained)
  • Remains DAA-naïve (prior therapy with (peg)IFN and/or ribavirin is allowed)

Enrollment Exclusion Criteria:

  • Liver transplantation since Screening

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Time to HCC recurrence - Prospective Cohortup to 24 months

Time to HCC recurrence associated with DAA therapy relative to no DAA therapy in the prospective cohort.

Secondary Outcome Measures
NameTimeMethod
Number of events of early HCC recurrence - Prospective Cohortup to 24 months

Number of events (early HCC recurrence) associated with DAA therapy relative to no DAA therapy in the prospective cohort.

Number of events of early HCC recurrence - Prospective Cohort relative to Historical Cohortup to 24 months

Number of events (early HCC recurrence) associated with DAA therapy in the prospective cohort relative to no DAA therapy in the historical cohort.

historical cohort of HCV patients not exposed to DAA with initial HCC diagnosis and subsequent successful treatment of HCC.

Time to HCC recurrence - Prospective Cohort relative to Historical Cohortup to 24 months

Time to HCC recurrence associated with DAA therapy in the prospective cohort relative to no DAA therapy in the historical cohort.

Trial Locations

Locations (61)

Clinical Research Institute@ Methodist Dallas Medical Center

🇺🇸

Dallas, Texas, United States

Piedmont Atlanta Hospital

🇺🇸

Atlanta, Georgia, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Rutgers-Robert Wood Johnson Medical School

🇺🇸

New Brunswick, New Jersey, United States

Georgetown University

🇺🇸

Washington, District of Columbia, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

Emory University Hospital

🇺🇸

Atlanta, Georgia, United States

Norris Comprehensive Cancer Center

🇺🇸

Los Angeles, California, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Stanford University

🇺🇸

Palo Alto, California, United States

California Liver Research Institute

🇺🇸

Pasadena, California, United States

University of California - Davis Clinical Trials

🇺🇸

Sacramento, California, United States

University of Florida Hepatology Research at CTRB

🇺🇸

Gainesville, Florida, United States

Hospital Universitario Politècnic La Fe

🇪🇸

Valencia, Spain

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

Universitätsklinikum Magdeburg

🇩🇪

Magdeburg, Germany

Penn State Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Northwestern University Division of Gastroenterology and Hepatology

🇺🇸

Chicago, Illinois, United States

Gastro Florida

🇺🇸

Clearwater, Florida, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

Tampa General Medical Group

🇺🇸

Tampa, Florida, United States

Schiff Center for Liver Diseases

🇺🇸

Miami, Florida, United States

Mercy Medical Center

🇺🇸

Baltimore, Maryland, United States

Tulane University School of Medicine

🇺🇸

New Orleans, Louisiana, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Southern Therapy and Advanced Research LLC

🇺🇸

Jackson, Mississippi, United States

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

IRCCS "Casa Sollievo della Sofferenza"

🇮🇹

San Giovanni Rotondo, Italy

Hôpitaux Universitaires Paris Centre

🇫🇷

Paris, France

Weill Cornell Medical College

🇺🇸

New York, New York, United States

Saint Louis University

🇺🇸

Saint Louis, Missouri, United States

Carolinas HealthCare System Center for Liver Disease

🇺🇸

Charlotte, North Carolina, United States

Humanitas Mirasole IRCCS

🇮🇹

Rozzano, Italy

Charité - Universitätsmedizin Berlin

🇩🇪

Berlin, Germany

Wenatchee Valley Hospital & Clinics

🇺🇸

Wenatchee, Washington, United States

A.O.U.P. di Palermo

🇮🇹

Palermo, Italy

Hospital Puerta de Hierro Majadahonda

🇪🇸

Madrid, Spain

Clínica Universidad de Navarra

🇪🇸

Pamplona, Spain

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

🇮🇹

Milan, Italy

CHU de Nice - Hôpital L'Archet 2

🇫🇷

Nice, France

Hospital Universitario Virgen del Rocío

🇪🇸

Sevilla, Spain

Banner University Medical Center

🇺🇸

Phoenix, Arizona, United States

University of California - San Francisco

🇺🇸

San Francisco, California, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

Providence Health & Services Cancer Clinical Trials

🇺🇸

Portland, Oregon, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Research Specialists of Texas

🇺🇸

Houston, Texas, United States

Harborview Medical Center

🇺🇸

Seattle, Washington, United States

Vanderbilt University Medical Center - GI Research Office

🇺🇸

Nashville, Tennessee, United States

University of Texas Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Northwell Health - Center for Liver Disease

🇺🇸

Manhasset, New York, United States

Universitätsklinikum Leipzig

🇩🇪

Leipzig, Germany

Bon Secours Liver Institute of Virginia

🇺🇸

Richmond, Virginia, United States

Baylor Scott & White All Saints

🇺🇸

Fort Worth, Texas, United States

Hospital Universitario Marques de Valdecilla

🇪🇸

Santander, Spain

New York University Langone Health

🇺🇸

New York, New York, United States

Universitätsklinikum Frankfurt

🇩🇪

Frankfurt, Germany

University of Virginia Transplant Center

🇺🇸

Charlottesville, Virginia, United States

University of Florida - Health Gastroenerology

🇺🇸

Jacksonville, Florida, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

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