MedPath

A Study of Lanadelumab (Takhzyro) and Icatibant (Firazyr®) in Persons With HAE in China

Recruiting
Conditions
Hereditary Angioedema (HAE)
Interventions
Other: No intervention
Registration Number
NCT06346899
Lead Sponsor
Takeda
Brief Summary

The Chinese health authority has approved lanadelumab to prevent Hereditary Angioedema (HAE) attacks in persons of 12 years and older. It has also approved icatibant to treat acute HAE attacks in persons 2 years and older.

One of the main aims of this study is to learn about the number of HAE attacks in 1 month in Chinese persons with HAE during their treatment with lanadelumab. The other main aim is to learn how much time is needed to resolve acute HAE attacks when treated with icatibant. Other aims of this study are to learn more about side effects of lanadelumab and icatibant treatment as well as to collect additional information on the treatment with lanadelumab, such as the dose and how often it needs to be given, reasons for stopping the treatment with lanadelumab and how long it was taken until stopping. Participants will be treated by their doctors according to routine medical practice. Only data already available in the medical records of the participants will be reviewed and collected during this study.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
130
Inclusion Criteria

Not provided

Read More
Exclusion Criteria

Not provided

Read More

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Group L: LanadelumabNo interventionParticipants with HAE who have used only lanadelumab during the study-level retrospective observation period will be observed retrospectively from the start date of the participant-level overall baseline period until the end of participant-level retrospective observation period.
Group I: IcatibantNo interventionParticipants with HAE who have used only icatibant during the study-level retrospective observation period will be observed retrospectively from the start date of the participant-level overall baseline period until the end of participant-level retrospective observation period.
Group B: Lanadelumab + IcatibantNo interventionParticipants with HAE who have used both lanadelumab and icatibant during the study-level retrospective observation period will be observed retrospectively from the start date of the participant-level overall baseline period until the end of participant-level retrospective observation period.
Primary Outcome Measures
NameTimeMethod
Median Time to Complete Attack Resolution for Icatibant Treated ParticipantsFrom the first dose of study drug up to approximately 3 years 8 months

Time to complete attack resolution among icatibant-treated participants during the retrospective observation period is defined as the time between icatibant first injection and the earliest time of complete resolution of symptoms for each attack during the retrospective observation period that was treated with icatibant.

Monthly Rate of HAE Attacks for Each Lanadelumab-treated Participant During the Lanadelumab Exposure PeriodFrom the first dose of study drug up to approximately 3 years 8 months

The HAE monthly attack rate is defined as the total number of attacks that occurred when the participant was in a lanadelumab exposure period, divided by the total lanadelumab exposure time (in days), multiplied by 28 days.

Secondary Outcome Measures
NameTimeMethod
Frequency Administration of Lanadelumab Among Lanadelumab-treated Participant During the Lanadelumab Exposure PeriodFrom the first dose of study drug up to approximately 3 years 8 months

Frequency administration of lanadelumab among lanadelumab-treated participant during the lanadelumab exposure period will be assessed.

Number of Participants with Adverse Events (AEs) and Serious Adverse Events (SAEs) During Lanadelumab and Icatibant Exposure PeriodFrom the first dose of study drug up to approximately 3 years 8 months

An AE is any untoward medical occurrence in a participant administered a studied drug and which does not necessarily have to have a causal relationship with the studied drug. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, a new disease or worsening in severity or frequency of a concomitant disease, temporally associated with the use of a studied drug, whether or not the event is considered causally related to the use of the product. An SAE is any untoward medical occurrence that at any dose: results in death, life-threatening, requires inpatient hospitalization or prolongation of existing hospitalization, results in persistent, significant disability/incapacity, a congenital abnormality/birth defect, an important medical event in the opinion of the healthcare provider, may jeopardize the participant or may require intervention to prevent one of the other outcomes listed in the definition above.

Dosage of Lanadelumab Among Lanadelumab-treated Participant During the Lanadelumab Exposure PeriodFrom the first dose of study drug up to approximately 3 years 8 months

Dosage of lanadelumab used during the lanadelumab exposure period will be assessed.

Number of Participants with Reasons of Discontinuation of Lanadelumab During the Lanadelumab Exposure PeriodFrom the first dose of study drug up to approximately 3 years 8 months

Number of participants with reasons of discontinuation of lanadelumab during the lanadelumab exposure period will be assessed.

Time to Lanadelumab Discontinuation Among Lanadelumab-treated Participant During the Lanadelumab Exposure PeriodFrom the first dose of study drug up to approximately 3 years 8 months

The time to lanadelumab discontinuation is defined as the time from lanadelumab initiation to the first lanadelumab discontinuation.

Trial Locations

Locations (13)

The Second Affiliated hospital of Xian Jiaotong University

🇨🇳

Xian, Shanxi, China

West China Hospital of Sichuan University

🇨🇳

Chengdu, Sichuan, China

The First Affiliated Hospital of Fujian Medical University

🇨🇳

Fuzhou, Fujan, China

The First Affiliated Hospital ,Sun Yat-sen University

🇨🇳

Guangzhou, Guangdong, China

The Second Affiliated Hospital of Guangzhou Medical University

🇨🇳

Guangzhou, Guangdong, China

Henan Provincial People's Hospital

🇨🇳

Zhengzhou, Henan, China

The First Hospital of China Medical University

🇨🇳

Shenyang, Liaoning, China

Tongji Hospital,Tongji Medical College,Huazhong University of Science & Technology

🇨🇳

Wuhan, Hubei, China

Renji Hospital Affiliated to Shanghai Jiaotong University School of Medicine

🇨🇳

Shanghai, Shanghai, China

Qianfo Mountain Hospital, Shandong Province

🇨🇳

Jinan, Shandong, China

Shanxi Bethune hospital

🇨🇳

Taiyuan, Shanxi, China

First Affiliated hospital of Kunming Medical University

🇨🇳

Kunming, Yunnan, China

The Second Affiliated hospital Zhejiang University School of Medicine

🇨🇳

Hangzhou, Zhejiang, China

© Copyright 2025. All Rights Reserved by MedPath