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A Phase 2 Study to Evaluate Efficacy and Safety of AL002 in Participants With Early Alzheimer's Disease

Phase 2
Active, not recruiting
Conditions
Alzheimer Disease
Interventions
Drug: Placebo
Registration Number
NCT04592874
Lead Sponsor
Alector Inc.
Brief Summary

A phase 2 randomized, double blind, placebo controlled study evaluating the efficacy and safety of AL002 in participants with Early Alzheimer's Disease.

Detailed Description

This is a phase 2 randomized, double blind, placebo controlled study evaluating the efficacy and safety of AL002 administered intravenously in participants with Early Alzheimer's Disease.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
328
Inclusion Criteria
  • Diagnosis of Early AD including evidence of brain amyloidosis by CSF or PET
  • MMSE score โ‰ฅ 20 points, CDR Global Score of 0.5 - 1.0, and RBANS score on the DMI โ‰ค95.
  • Study partner who consents to study participation and who cares for/visits the participant at least 10 hours a week
  • Written informed consent must be obtained and documented (from the participant or, where jurisdictions allow it, from their legal decision maker).
Exclusion Criteria
  • Dementia due to a condition other than AD including, but not limited to, FTD, Parkinson's disease, dementia with Lewy bodies, Huntington disease, or vascular dementia. - Dementia due to a condition other than AD including, but not limited to, FTD, Parkinson's disease, dementia with Lewy bodies, Huntington disease, or vascular dementia.
  • Known history of severe allergic, anaphylactic, or other hypersensitivity reactions to chimeric, human, or humanized antibodies or fusion proteins.
  • Current uncontrolled hypertension, diabetes mellitus or thyroid disease. Clinically significant heart disease, liver disease or kidney disease.
  • History or evidence of clinically significant brain disease other than AD.
  • Females who are pregnant or breastfeeding, or planning to conceive within the study period.
  • Any experimental vaccine or gene therapy.
  • History of unresolved cancer.
  • Current use of anticoagulant medications.
  • Residence in a skilled nursing facility, convalescent home, or long term care facility at screening; or requires continuous nursing care.
  • Participant is positive for presence of APOE e4/e4 genotype.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
AL002 Dose 2AL002AL002 every 4 weeks
PlaceboPlaceboPlacebo every 4 weeks
AL002 Dose 1AL002AL002 every 4 weeks
AL002 Dose 3AL002AL002 every 4 weeks
Primary Outcome Measures
NameTimeMethod
Disease progression as measured by the CDR-SBThrough study completion, up to 48 through 96 weeks
Secondary Outcome Measures
NameTimeMethod
Change in RBANS scoreThrough study completion, up to 48 through 96 weeks
Change in ADAS-Cog13 scoreThrough study completion, up to 48 through 96 weeks
Change in ADCS-ADL-MCI scoreThrough study completion, up to 48 through 96 weeks
Change in ADCOMS scoreThrough study completion, up to 48 through 96 weeks
Evaluation of safety and tolerability of AL002: Incidence of adverse eventsThrough study completion, up to 48 through 96 weeks

Incidence of adverse events

Change in MMSE scoreThrough study completion, up to 48 through 96 weeks

Trial Locations

Locations (87)

Brain Matters Research - ERG

๐Ÿ‡บ๐Ÿ‡ธ

Delray Beach, Florida, United States

Georgetown University Medical Center

๐Ÿ‡บ๐Ÿ‡ธ

Washington, District of Columbia, United States

South Florida Neurology Associates

๐Ÿ‡บ๐Ÿ‡ธ

Boca Raton, Florida, United States

Charter Research

๐Ÿ‡บ๐Ÿ‡ธ

Lady Lake, Florida, United States

K2 Medical Research

๐Ÿ‡บ๐Ÿ‡ธ

Maitland, Florida, United States

K2 Winter Garden Ocoee

๐Ÿ‡บ๐Ÿ‡ธ

Ocoee, Florida, United States

Progressive Medical Research

๐Ÿ‡บ๐Ÿ‡ธ

Port Orange, Florida, United States

K2 The Villages

๐Ÿ‡บ๐Ÿ‡ธ

The Villages, Florida, United States

Conquest Clinical Research (Winter Park)

๐Ÿ‡บ๐Ÿ‡ธ

Winter Park, Florida, United States

Hattiesburg Clinic

๐Ÿ‡บ๐Ÿ‡ธ

Hattiesburg, Mississippi, United States

KaRa Institute of Neurological Disease

๐Ÿ‡ฆ๐Ÿ‡บ

Macquarie Park, New South Wales, Australia

Okanagan Clinical Trials

๐Ÿ‡จ๐Ÿ‡ฆ

Kelowna, British Columbia, Canada

University Clinic Heidelberg

๐Ÿ‡ฉ๐Ÿ‡ช

Mannheim, Germany

Kawartha Regional Memory Clinic

๐Ÿ‡จ๐Ÿ‡ฆ

Peterborough, Ontario, Canada

Toronto Memory Clinic

๐Ÿ‡จ๐Ÿ‡ฆ

Toronto, Ontario, Canada

Hรดpital Roger Salengro

๐Ÿ‡ซ๐Ÿ‡ท

Lille, Nord, France

Gerontopole

๐Ÿ‡ซ๐Ÿ‡ท

Toulouse, France

Charite Campus Buch

๐Ÿ‡ฉ๐Ÿ‡ช

Berlin, Germany

Fondazione Policlinico Universitario A Gemelli

๐Ÿ‡ฎ๐Ÿ‡น

Roma, Lazio, Italy

Azienda Policlinico Umberto I

๐Ÿ‡ฎ๐Ÿ‡น

Roma, Lazio, Italy

Ospedale S Giovanni Calibita Fatebenefratelli

๐Ÿ‡ฎ๐Ÿ‡น

Roma, Lazio, Italy

ASST degli Spedali Civili di Brescia - Spedali Civili di Brescia

๐Ÿ‡ฎ๐Ÿ‡น

Brescia, Italy

Fondazione IRCCS Cร  Granda Ospedale Maggiore Policlinico

๐Ÿ‡ฎ๐Ÿ‡น

Milano, Italy

Fondazione IRCCS Di Rilievo Nazionale Istituto Nazionale Neurologico Carlo Besta

๐Ÿ‡ฎ๐Ÿ‡น

Milano, Italy

Ospedale Civile di Baggiovara

๐Ÿ‡ฎ๐Ÿ‡น

Modena, Italy

Ospedale degli Infermi

๐Ÿ‡ฎ๐Ÿ‡น

Ponderano, Italy

Brain Research Center Amsterdam

๐Ÿ‡ณ๐Ÿ‡ฑ

Amsterdam, Netherlands

CGM Research Trust

๐Ÿ‡ณ๐Ÿ‡ฟ

Christchurch, New Zealand

NZOZ Wroclawskie Centrum Alzheimerowskie

๐Ÿ‡ต๐Ÿ‡ฑ

Wrocล‚aw, Dolnoslaskie, Poland

Centrum Medyczne NeuroProtect

๐Ÿ‡ต๐Ÿ‡ฑ

Warszawa, Mazowieckie, Poland

SOMED CR

๐Ÿ‡ต๐Ÿ‡ฑ

Warsaw, Poland

Hospital de La Santa Creu i Sant Pau

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Cataluรฑa, Spain

Fundacion CITA Alzheimer Fundazioa

๐Ÿ‡ช๐Ÿ‡ธ

Donostia, Guipuzcoa, Spain

Centro de Atencion Especializada Oroitu

๐Ÿ‡ช๐Ÿ‡ธ

Getxo, Pais Vasco, Spain

Fundacion ACE Instituto Catalan de Neurociencias

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Spain

Hospital Clinic de Barcelona

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Spain

Hospital Universitario Ramon y Cajal

๐Ÿ‡ช๐Ÿ‡ธ

Madrid, Spain

Hospital Universitario Doctor Peset

๐Ÿ‡ช๐Ÿ‡ธ

Valencia, Spain

Hospital Universitari i Politecnic La Fe de Valencia

๐Ÿ‡ช๐Ÿ‡ธ

Valencia, Spain

Hospital Viamed Montecanal

๐Ÿ‡ช๐Ÿ‡ธ

Zaragoza, Spain

The National Hospital for Neurology and Neurosurgery

๐Ÿ‡ฌ๐Ÿ‡ง

London, United Kingdom

Glasgow Memory Clinic

๐Ÿ‡ฌ๐Ÿ‡ง

Motherwell, United Kingdom

Re:Cognition Health Plymouth

๐Ÿ‡ฌ๐Ÿ‡ง

Plymouth, United Kingdom

SMarT Minds WA

๐Ÿ‡ฆ๐Ÿ‡บ

Nedlands, Western Australia, Australia

ATP Clinical Research

๐Ÿ‡บ๐Ÿ‡ธ

Costa Mesa, California, United States

AMITA Health Clinical Research Institute

๐Ÿ‡บ๐Ÿ‡ธ

Elk Grove Village, Illinois, United States

Feinstein Institute For MR

๐Ÿ‡บ๐Ÿ‡ธ

Manhasset, New York, United States

Columbia University College of Physicians and Surgeons

๐Ÿ‡บ๐Ÿ‡ธ

New York, New York, United States

University of Rochester Medical Center

๐Ÿ‡บ๐Ÿ‡ธ

Rochester, New York, United States

Abington Neurologic Associates

๐Ÿ‡บ๐Ÿ‡ธ

Abington, Pennsylvania, United States

SUNY Upstate Medical Center

๐Ÿ‡บ๐Ÿ‡ธ

Syracuse, New York, United States

LMU Klinikum der Universitรคt Mรผnchen

๐Ÿ‡ฉ๐Ÿ‡ช

Mรผnchen, Germany

Woodlands Research Network, LLC - ERG

๐Ÿ‡บ๐Ÿ‡ธ

Rogers, Arkansas, United States

ClinCloud, LLC

๐Ÿ‡บ๐Ÿ‡ธ

Maitland, Florida, United States

The Alfred Hospital

๐Ÿ‡ฆ๐Ÿ‡บ

Parkville, Victoria, Australia

Centro de Psiquiatrรญa Biolรณgica Instituto Senecta

๐Ÿ‡ฆ๐Ÿ‡ท

Mendoza, Argentina

Parkwood Institute

๐Ÿ‡จ๐Ÿ‡ฆ

London, Ontario, Canada

Box Hill Hospital

๐Ÿ‡ฆ๐Ÿ‡บ

Box Hill, Victoria, Australia

Alzheimers Research and Treatment Center

๐Ÿ‡บ๐Ÿ‡ธ

Wellington, Florida, United States

Boston Center for Memory

๐Ÿ‡บ๐Ÿ‡ธ

Newton, Massachusetts, United States

Charitรฉ - Universitรคtsmedizin Berlin (CBF)

๐Ÿ‡ฉ๐Ÿ‡ช

Berlin, Germany

Hรดpital de la Pitiรฉ Salpรฉtriรจre

๐Ÿ‡ซ๐Ÿ‡ท

Paris, France

Advanced Clinical Institute

๐Ÿ‡บ๐Ÿ‡ธ

Neptune, New Jersey, United States

Instituto Kremer

๐Ÿ‡ฆ๐Ÿ‡ท

Cรณrdoba, Argentina

Universitรคtsklinikum Ulm

๐Ÿ‡ฉ๐Ÿ‡ช

Ulm, Germany

EUROMEDIS Sp. z o.o.

๐Ÿ‡ต๐Ÿ‡ฑ

Szczecin, Zachodniopomorskie, Poland

True North Clinical Research - New Minas

๐Ÿ‡จ๐Ÿ‡ฆ

New Minas, Nova Scotia, Canada

True North Clinical Research - Halifax

๐Ÿ‡จ๐Ÿ‡ฆ

Halifax, Nova Scotia, Canada

Brain Research Center Den Bosch

๐Ÿ‡ณ๐Ÿ‡ฑ

's-Hertogenbosch, Noord-Brabant, Netherlands

Baycrest Health Sciences

๐Ÿ‡จ๐Ÿ‡ฆ

Toronto, Ontario, Canada

University of Kentucky

๐Ÿ‡บ๐Ÿ‡ธ

Lexington, Kentucky, United States

Bruyรจre Research Institute

๐Ÿ‡จ๐Ÿ‡ฆ

Ottawa, Ontario, Canada

Hopital Lariboisiere

๐Ÿ‡ซ๐Ÿ‡ท

Paris, France

Centre Hospitalier Universitaire de Toulouse

๐Ÿ‡ซ๐Ÿ‡ท

Toulouse, France

Klinikum rechts der Isa der Technischen Universitaet Muenchen

๐Ÿ‡ฉ๐Ÿ‡ช

Mรผnchen, Germany

IRCCS - Centro S. Giovanni di Dio Fatebenefratelli

๐Ÿ‡ฎ๐Ÿ‡น

Brescia, Lombardia, Italy

Azienda Ospedaliero Universitaria Pisana

๐Ÿ‡ฎ๐Ÿ‡น

Pisa, Italy

Re: Cognition Health - Guildford

๐Ÿ‡ฌ๐Ÿ‡ง

Guildford, Surrey, United Kingdom

Banner Alzheimer's Institute

๐Ÿ‡บ๐Ÿ‡ธ

Phoenix, Arizona, United States

Emory University

๐Ÿ‡บ๐Ÿ‡ธ

Atlanta, Georgia, United States

University of Cincinnati MC

๐Ÿ‡บ๐Ÿ‡ธ

Cincinnati, Ohio, United States

Clinical Trial Network

๐Ÿ‡บ๐Ÿ‡ธ

Houston, Texas, United States

Summit Research Network

๐Ÿ‡บ๐Ÿ‡ธ

Portland, Oregon, United States

Re:Cognition Health London

๐Ÿ‡ฌ๐Ÿ‡ง

London, United Kingdom

Re:Cognition Health Bristol

๐Ÿ‡ฌ๐Ÿ‡ง

Bristol, United Kingdom

Axiom Clinical Research FL

๐Ÿ‡บ๐Ÿ‡ธ

Tampa, Florida, United States

Greater Manchester Mental Health NHS Foundation Trust

๐Ÿ‡ฌ๐Ÿ‡ง

Manchester, United Kingdom

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