Natural History Study of MNGIE
- Conditions
- Mitochondrial Neurogastrointestinal Encephalomyopathy
- Registration Number
- NCT04245917
- Lead Sponsor
- Entrada Therapeutics, Inc.
- Brief Summary
Non-interventional, prospective, multicenter, natural history study of patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- SUSPENDED
- Sex
- All
- Target Recruitment
- 60
- Has MNGIE
- Substance abuser
Study & Design
- Study Type
- OBSERVATIONAL
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method MNGIE Clinical Course 5 years To evaluate the clinical course of MNGIE patients
- Secondary Outcome Measures
Name Time Method
Related Research Topics
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Trial Locations
- Locations (5)
Children's Hospital Colorado
🇺🇸Aurora, Colorado, United States
Columbia University
🇺🇸New York, New York, United States
Baylor St Luke's Medical Center and Texas Children's Hospital at Baylor College of Medicine
🇺🇸Houston, Texas, United States
Ege University Medical Faculty; Department of Pediatrics
🇹🇷Bornova, Izmir, Turkey
Gazi Üniversitesi Tıp Fakültesi
🇹🇷Ankara, Turkey
Children's Hospital Colorado🇺🇸Aurora, Colorado, United States