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Cytarabine and Daunorubicin With or Without Gemtuzumab Ozogamicin in Treating Older Patients With Acute Myeloid Leukemia or Myelodysplastic Syndromes

Phase 3
Completed
Conditions
Leukemia
Myelodysplastic Syndromes
Interventions
Registration Number
NCT00121303
Lead Sponsor
Stichting Hemato-Oncologie voor Volwassenen Nederland
Brief Summary

RATIONALE: Drugs used in chemotherapy, such as cytarabine and daunorubicin, work in different ways to stop the growth of cancer cells, either by killing the cells or by stopping them from dividing. Monoclonal antibodies, such as gemtuzumab ozogamicin, can block cancer growth in different ways. Some block the ability of cancer cells to grow and spread. Others find cancer cells and help kill them or carry cancer-killing substances to them. It is not yet known whether cytarabine and daunorubicin followed by gemtuzumab ozogamicin is more effective than cytarabine and daunorubicin in treating acute myeloid leukemia or myelodysplastic syndromes.

PURPOSE: This randomized phase III trial is studying cytarabine and two different doses of daunorubicin to see how well they work compared to cytarabine and daunorubicin followed by gemtuzumab ozogamicin in treating older patients with acute myeloid leukemia or myelodysplastic syndromes.

Detailed Description

OBJECTIVES:

Primary

* Compare the event-free and disease-free survival of older patients with acute myeloid leukemia, refractory anemia with excess blasts (RAEB), or RAEB in transformation treated with induction therapy comprising cytarabine in combination with two different doses of daunorubicin followed by cytarabine alone with or without post-induction therapy comprising gemtuzumab ozogamicin.

Secondary

* Compare the complete remission rate in patients treated with these regimens.

* Compare the overall survival of patients treated with these regimens.

* Compare the toxicity of these regimens in these patients.

* Determine the probability of relapse and death during first complete remission in patients treated with post-induction gemtuzumab ozogamicin.

* Correlate prognostic factors (e.g., CD33 positivity, multidrug resistance phenotype, or cytogenetics) with probability of complete remission and overall, event-free, and disease-free survival of patients treated with these regimens.

OUTLINE: This is a randomized, multicenter study. Patients are stratified according to participating center and diagnosis (acute myeloid leukemia \[AML\] vs myelodysplastic syndromes \[MDS\]) for induction therapy. Patients are stratified according to participating center, diagnosis (AML vs MDS), induction treatment arm (I vs II), and response to induction therapy (complete remission \[CR\] vs no CR) for post-induction therapy.

* Induction therapy (course 1): Patients are randomized to 1 of 2 induction treatment arms.

* Arm I: Patients receive cytarabine IV continuously on days 1-7 and daunorubicin IV over 3 hours on days 1-3.

* Arm II: Patients receive cytarabine as in arm I and daunorubicin as in arm I but at a higher dose.

Approximately 28-35 days after the start of course 1 (or sooner if the bone marrow shows evidence of resistant disease), patients in both arms proceed to course 2 of induction therapy.

* Induction therapy (course 2): All patients receive cytarabine IV over 6 hours twice daily on days 1-6.

After completion of course 2, patients undergo assessment of remission status. Patients who do not achieve CR are removed from the study. Patients achieving CR proceed to post-induction therapy and undergo a second randomization.

* Post-induction therapy: Patients are randomized to 1 of 2 post-induction treatment arms.

* Arm I: Patients receive no further chemotherapy.

* Arm II: Patients receive gemtuzumab ozogamicin IV over 2 hours on days 1, 29, and 57 in the absence of disease relapse or unacceptable toxicity.

After completion of study treatment, patients are followed monthly for 1 year, every 3 months for 2 years, every 4-6 months for 2 years, and then periodically thereafter.

PROJECTED ACCRUAL: A total of 600 patients will be accrued for this study within 4-5 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
600
Inclusion Criteria

Not provided

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Exclusion Criteria

Not provided

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Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm A low dose DaunocytarabineInduction 45 mg Dauno
Arm A low dose Daunodaunorubicin hydrochlorideInduction 45 mg Dauno
ARM B high dose DaunocytarabineInduction 90 mg Dauno
ARM B high dose Daunodaunorubicin hydrochlorideInduction 90 mg Dauno
Arm 2 Mylotarggemtuzumab ozogamicinPost induction treatment with Mylotarg
Primary Outcome Measures
NameTimeMethod
Event-free survival after induction therapy
Disease-free survival after maintenance therapy
Secondary Outcome Measures
NameTimeMethod
Probability of relapse and death in first CR after maintenance therapy
Overall survival after maintenance therapy
Overall survival after induction therapy
Complete remission (CR) rate after induction therapy
Toxicity after induction therapy
Toxicity after maintenance therapy

Trial Locations

Locations (6)

University Hospital of Wales

🇬🇧

Cardiff, Wales, United Kingdom

Medway Maritime Hospital

🇬🇧

Gillingham Kent, England, United Kingdom

North Hampshire Hospital

🇬🇧

Basingstoke, England, United Kingdom

Maidstone Hospital

🇬🇧

Maidstone, England, United Kingdom

Royal Cornwall Hospital

🇬🇧

Truro, Cornwall, England, United Kingdom

Kent and Canterbury Hospital

🇬🇧

Canterbury, England, United Kingdom

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