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Oxford Pre-cancerous Lymphoproliferative Disorders Study

Active, not recruiting
Conditions
Pre-cancerous Lymphoproliferative Disorders
Registration Number
NCT04023747
Lead Sponsor
University of Oxford
Brief Summary

OxPLoreD is an observational cohort study to identify clinical, genomic and immunological predictive markers of progression to malignant disease. Open to individuals diagnosed in the last 3 years with high count MBL, Binet Stage A CLL, Immunoglobulin G/A/M (IgG, IgA, IgM) MGUS, asymptomatic WM not requiring treatment and smouldering myeloma not requiring treatment.

Detailed Description

The purpose of the study is to monitor patients with early stage lymphoproliferative disorders not meeting criteria for treatment, including early stage Chronic Lymphocytic Leukaemia (CLL), Monoclonal B-cell Lymphocytosis (MBL), Monoclonal Gammopathy of Uncertain Significance (MGUS), asymptomatic Waldenstroms Macroglobulinaemia (WM) and Smouldering Myeloma (SM).

Each of these disorders has a pre-cancerous phase when abnormalities can be seen in the blood, however treatment may not be required. A minority of people with early stage lymphoproliferative disorders will go on to need treatment for blood or bone marrow cancer.

Currently the investigators do not have a reliable way to predict which of these individuals with these disorders are more likely to develop a blood or bone marrow cancer. By studying a large group of individuals over time we hope to discover more about what factors might predict progression. The investigators may be able to identify markers which identify individuals who are more or less likely to develop blood or bone marrow cancer. These markers might be particular symptoms, gene changes called mutations or levels of particular molecules or cells in the blood or bone marrow. In the longer term this may enable us to identify those people who would benefit from certain types of treatment or from receiving treatment at an earlier stage and also to confidently reassure those who will never progress.

Patients will be studied for up to 5 years with blood, bone marrow and saliva samples taken at key time-points to help answer these questions. In addition to looking for these markers we will also collect information about:

* What it is like to live with one of these conditions

* How many people with these conditions develop other significant medical conditions, such as serious infections, thrombosis (blood clots) or other types of cancer.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
574
Inclusion Criteria
  1. Patients diagnosed within the previous three years with one of the following:

    1. High count monoclonal B-cell lymphocytosis (MBL) i.e. clonal B-cell population 0.5-4.9 109/L
    2. Rai Stage 0-2/ Binet Stage A or Stage B Chronic Lymphocytic Leukaemia not meeting the IWCLL criteria for treatment
    3. IgG or IgA Monoclonal Gammopathy of Uncertain Significance meeting one of the following criteria:

    i) IgA paraprotein >10g/L or

    ii) IgG paraprotein >15g/L or

    iii) IgA/IgG paraprotein below these cut-offs but kappa:lambda light chain ratio of

    • <0.1 to >3.0 (For OUH participants or sites with no pre-defined cut offs for high risk MGUS) or
    • within the cut off criteria of the local laboratory ranges for high risk MGUS

    iv) Patients not meeting the cut-offs defined in points i) to iii) but who are referred to secondary care e.g. due to general practitioner (GP) concern or for investigation of symptoms

    d. IgM Monoclonal Gammopathy of Uncertain Significance meeting one of the following criteria: i) IgM paraprotein >10g/L or

    ii) IgM paraprotein <10g/L and difference between the kappa and lambda light chains of >50mg/L

    iii) Patients not meeting the cut-offs defined in point i) and ii) but who are referred to secondary care e.g. due to GP concern or investigation of symptoms

    e) Asymptomatic smouldering Waldenstrom's Macroglobulinaemia not meeting the criteria for treatment f) Smouldering myeloma not meeting the criteria for treatment

  2. Eastern Cooperative Oncology Group (ECOG) performance status of 0,1 or 2

  3. Age 16 years and over

  4. Sign written informed consent

  5. The patient is willing and able to comply with the protocol for the duration of the study and scheduled follow-up visits and examinations

Exclusion Criteria
  1. Pregnant or breast-feeding women. Pregnant or breast-feeding women may be re-screened following delivery and/or cessation of breastfeeding, as appropriate
  2. Previous chemotherapy or immunotherapy for any haematological cancers
  3. Treatment with any other investigational agent, or participation in an interventional clinical trial within 28 days prior to enrolment.
  4. Patients in cohort 2 or 3 on anticoagulation for a diagnosis of pulmonary embolus or deep vein thrombosis within the last 3 months or with a mechanical heart valve or any other condition causing a significant risk of thromboembolism. Participants who are anticoagulated for atrial fibrillation are eligible, but will be asked to interrupt anticoagulation 3 days prior to bone marrow examination
  5. Other psychological, social or medical condition, physical examination finding or laboratory abnormality that the investigator considers would make the patient a poor study candidate or could interfere with protocol compliance or the interpretation of study results.
  6. Any other malignancy that requires active surgical or chemotherapeutic Patients on long term hormone therapies (e.g. Tamoxifen) are permitted to enrol at the discretion of investigator, after considering the overall clinical context
  7. Any significant concurrent medical resulting in life-expectancy (including but no limited to renal, Hepatic, haematological gastrointestinal, endocrine pulmonary neurological, cerebral or psychiatric disease
  8. For cohort 3: Any contraindication for MRI- presence of any metallic foreign body, eGFR <30 and allergy to gadolinium contrast

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
The identification of predictive markers of progression to malignant diseaseDuration of the study (5 years)

Relevant markers will be identified from the analysis of the clinical data in combination with the genomic and immunological data from the samples collected. The markers will be combined to produce a single probability risk score. The choice of relevant markers will be guided by emerging evidence and techniques under the guidance of the study scientific advisory board.

Secondary Outcome Measures
NameTimeMethod
To study other clinically significant events, not inevitably due to disease progression in this patient cohortDuration of study (5 years)

Assessed by analysing suspected unexpected serious adverse reactions (SUSARs) reported

Patient reported outcome measures (PROM) via approved quality of life questionnaires.Duration of study (5 years)

Analysis of approved questionnaires: EORTC QLQ-MY20

Production of evidence-based standard of care guidelines for the monitoring and follow-up of patients with these pre-cancerous conditionsDuration of study (5 years)

The identification of relevant markers can be used to create guidelines for optimal monitoring of patients with these pre-cancerous conditions

Trial Locations

Locations (17)

Queens Medical Centre

🇬🇧

Nottingham, United Kingdom

St George's Hospital

🇬🇧

London, United Kingdom

North Tyneside General Hospital

🇬🇧

North Shields, United Kingdom

Derriford Hospital

🇬🇧

Plymouth, United Kingdom

South Tyneside District Hospital

🇬🇧

South Shields, United Kingdom

Epsom Hospital

🇬🇧

London, United Kingdom

King's College Hospital

🇬🇧

London, United Kingdom

Leicester Royal Infirmary

🇬🇧

Leicester, United Kingdom

Russells Hall Hospital

🇬🇧

Dudley, United Kingdom

James Paget Hospital

🇬🇧

Great Yarmouth, United Kingdom

Churchill Hospital, Oxford University Hospitals Trust

🇬🇧

Oxford, United Kingdom

Poole Hospital

🇬🇧

Poole, United Kingdom

Sunderland Royal Hospital

🇬🇧

Sunderland, United Kingdom

Musgrove Park Hospital

🇬🇧

Taunton, United Kingdom

Clatterbridge Cancer Centre

🇬🇧

Liverpool, United Kingdom

Northern Centre for Cancer Care

🇬🇧

Newcastle, United Kingdom

Royal Bournemouth Hospital

🇬🇧

Bournemouth, United Kingdom

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