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Study of ISIS 304801 versus placebo Administered Subcutaneously to Patients with Partial Lipodystrophy

Phase 1
Conditions
Partial lipodystrophy
MedDRA version: 20.0Level: PTClassification code 10053857Term: Partial lipodystrophySystem Organ Class: 10040785 - Skin and subcutaneous tissue disorders
Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]
Registration Number
EUCTR2015-000493-35-DE
Lead Sponsor
Akcea Therapeutics, Inc.
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
60
Inclusion Criteria

1. Clinical diagnosis of FPL plus diagnosis of type 2 diabetes mellitus and
hypertriglyceridemia.

2. Diagnosis of Type 2 diabetes mellitus as defined by International Diabetes Federation guidelines made at least 6 months prior to the screening visit

3. Hypertriglyceridemia is defined as Fasting TG = 500 mg/dL (= 5.7
mmol/L) at Screening and qualification visit.
Are the trial subjects under 18? no
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 57
F.1.3 Elderly (>=65 years) yes
F.1.3.1 Number of subjects for this age range 3

Exclusion Criteria

1. A diagnosis of generalized lipodystrophy

2. A diagnosis of acquired partial lipodystrophy (APL)

3. Acute pancreatitis within 4 weeks of Screening

4. History within 6 months of Screening of acute or unstable cardiac ischemia (myocardial infarction, acute coronary syndrome, new onset angina), stroke, transient ischemic attack or unstable congestive heart failure requiring a change in medication

5. Major surgery within 3 months of Screening

6. Platelet count
7. Have any other conditions in the opinion of the investigator which could interfere with the patient participating in our completing the study

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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