MedPath

An Open-label Study of Ozanimod in Moderate to Severe Ulcerative Colitis in Clinical Practice

Phase 4
Terminated
Conditions
Colitis, Ulcerative
Interventions
Registration Number
NCT05369832
Lead Sponsor
Bristol-Myers Squibb
Brief Summary

The purpose of this study is to explore the safety, efficacy, effects on quality of life (QOL), and biomarker response of ozanimod in participants with moderate to severely active ulcerative colitis (UC) in clinical practice.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
139
Inclusion Criteria
  • A diagnosis of ulcerative colitis (UC), with signs and symptoms consistent with UC for at least 3 months prior to the first study intervention administration

  • Moderate to severely active UC disease activity, defined as a modified Mayo score of 4 through 9, inclusive, with the following minimum subscores:

    i) An SF subscore ≥ 1, AND ii) An RB subscore ≥ 1, AND iii) An ES ≥ 2 (endoscopy performed within 60 days of the first study intervention administration).

  • Report of a previous colonoscopy that documents extent of disease

Exclusion Criteria
  • Current or recent (within 3 months of screening) evidence of fulminant colitis, toxic megacolon, or bowel perforation
  • Extensive colonic resection or current stoma
  • Colonic dysplasia that has not been removed

Other protocol-defined inclusion/exclusion criteria apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Cohort 2 - Advanced therapy-exposedOzanimod-
Cohort 1 - Advanced therapy-naiveOzanimod-
Primary Outcome Measures
NameTimeMethod
Clinical response as measured by modified Mayo scoreUp to approximately 26 weeks

Cohort 1 and 2

Secondary Outcome Measures
NameTimeMethod
Proportion of participants with Adverse Events (AEs)Up to approximately 2 years

Cohort 1 and 2

Proportion of participants with Serious Adverse Events (SAEs)Up to approximately 2 years

Cohort 1 and 2

Clinical remission by partial Mayo scoreUp to approximately 104 weeks

Cohort 1 and 2

Clinical remission as measured by modified Mayo scoreUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants with change in the Inflammatory Bowel Disease Questionnaire (IBDQ) total score from baselineUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants who achieve endoscopic responseUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants who achieve endoscopic improvementUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants with histo-endoscopic mucosal improvementUp to approximately 26 weeks

Cohort 2 only

Proportion of participants with AEs of interest (AEI)Up to approximately 2 years

Cohort 1 and 2

Clinical response by partial Mayo scoreUp to approximately 104 weeks

Cohort 1 and 2

Proportion of participants with change in total score (≥ 16 points) of IBDQ response from baselineUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants who achieve histological remissionUp to approximately 26 weeks

Cohort 2 only

Corticosteroid-free clinical remission by partial MayoUp to approximately 104 weeks

Cohort 1 and 2

Proportion of participants who achieve histological improvementUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants with IBDQ remission with total score of ≥ 170 pointsUp to approximately 26 weeks

Cohort 1 and 2

Proportion of participants who achieve endoscopic remissionUp to approximately 26 weeks

Cohort 2 only

Corticosteroid-free clinical remission as measured by modified Mayo scoreUp to approximately 26 weeks

Cohort 2 only

Proportion of participants with clinical laboratory abnormalitiesUp to approximately 2 years

Cohort 1 and 2

Proportion of participants with AEs leading to discontinuationUp to approximately 2 years

Cohort 1 and 2

Trial Locations

Locations (85)

Local Institution - 0048

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Dothan, Alabama, United States

Local Institution - 0206

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Chandler, Arizona, United States

Local Institution - 0216

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Gilbert, Arizona, United States

Local Institution - 0125

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Sun City, Arizona, United States

Local Institution - 0195

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Tucson, Arizona, United States

Local Institution - 0045

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North Little Rock, Arkansas, United States

Local Institution - 0162

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Camarillo, California, United States

Local Institution - 0014

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Lancaster, California, United States

Local Institution - 0002

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San Diego, California, United States

Local Institution - 0208

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San Diego, California, United States

Local Institution - 0185

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San Jose, California, United States

Local Institution - 0178

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Littleton, Colorado, United States

Local Institution - 0018

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Clearwater, Florida, United States

Local Institution - 0050

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Homestead, Florida, United States

Local Institution - 0026

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Lighthouse Point, Florida, United States

Local Institution - 0167

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Miami, Florida, United States

Local Institution - 0003

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Naples, Florida, United States

Local Institution - 0058

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Orange Park, Florida, United States

Local Institution - 0205

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Orlando, Florida, United States

Local Institution - 0037

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Palm Harbor, Florida, United States

Local Institution - 0179

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Wellington, Florida, United States

Local Institution - 0027

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Roswell, Georgia, United States

Local Institution - 0198

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Arlington Heights, Illinois, United States

Local Institution - 0051

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Chicago, Illinois, United States

Local Institution - 0098

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Gurnee, Illinois, United States

Local Institution - 0192

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Kansas City, Kansas, United States

Local Institution - 0181

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Topeka, Kansas, United States

Local Institution - 0200

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Baton Rouge, Louisiana, United States

Local Institution - 0171

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Chevy Chase, Maryland, United States

Local Institution - 0191

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Glen Burnie, Maryland, United States

Local Institution - 0199

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Boston, Massachusetts, United States

Local Institution - 0196

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Worcester, Massachusetts, United States

Local Institution - 0174

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Plymouth, Minnesota, United States

Local Institution - 0084

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Brooklyn, New York, United States

Local Institution - 0184

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Ocean Springs, Mississippi, United States

Local Institution - 0024

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Chesterfield, Missouri, United States

Local Institution - 0180

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Englewood, New Jersey, United States

Local Institution - 0187

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New York, New York, United States

Local Institution - 0059

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New York, New York, United States

Local Institution - 0176

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New York, New York, United States

Local Institution - 0170

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Utica, New York, United States

Local Institution - 0005

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Cincinnati, Ohio, United States

Local Institution - 0061

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Mentor, Ohio, United States

Local Institution - 0060

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Providence, Rhode Island, United States

Local Institution - 0177

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Cordova, Tennessee, United States

Local Institution - 0168

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Nashville, Tennessee, United States

Local Institution - 0038

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Bellaire, Texas, United States

Local Institution - 0138

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Dallas, Texas, United States

Local Institution - 0036

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Houston, Texas, United States

Local Institution - 0163

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Houston, Texas, United States

Local Institution - 0052

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Houston, Texas, United States

Local Institution - 0129

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Katy, Texas, United States

Local Institution - 0161

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Lubbock, Texas, United States

Local Institution - 0039

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Mansfield, Texas, United States

Local Institution - 0201

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San Antonio, Texas, United States

Local Institution - 0043

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San Antonio, Texas, United States

Local Institution - 0166

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San Marcos, Texas, United States

Local Institution - 0046

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Tyler, Texas, United States

Local Institution - 0091

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Webster, Texas, United States

Local Institution - 0193

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Ogden, Utah, United States

Local Institution - 0189

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Tacoma, Washington, United States

Local Institution - 0169

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Salt Lake City, Utah, United States

Local Institution - 0197

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Lynchburg, Virginia, United States

Local Institution - 0130

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Seattle, Washington, United States

Local Institution - 0017

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Madison, Wisconsin, United States

Local Institution - 0165

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Apple Valley, California, United States

OM Research LLC - Lancaster - ClinEdge - PPDS

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Lancaster, California, United States

Local Institution - 0209

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Los Angeles, California, United States

Gastro Florida

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Clearwater, Florida, United States

Gastroenterology Group of Naples

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Naples, Florida, United States

Local Institution - 0183

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Louisville, Kentucky, United States

Local Institution - 0049

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Miami Lakes, Florida, United States

Wellness Clinical Research-Miami Florida

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Miami Lakes, Florida, United States

Local Institution - 0213

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Weldon Spring, Missouri, United States

NYU Langone Health -Inflammatory Bowel Disease Center

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New York, New York, United States

Carolina Digestive Diseases

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Greenville, North Carolina, United States

University of Cincinnati Physicians Company

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Cincinnati, Ohio, United States

Local Institution - 0188

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Columbus, Ohio, United States

Novel Research LLC

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Bellaire, Texas, United States

Ace Clinical Research Group: Digestive Health Associates

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Houston, Texas, United States

Houston Methodist Hospital

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Houston, Texas, United States

GI Alliance: Mansfield - TDDC

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Mansfield, Texas, United States

San Antonio Gastroenterology

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San Antonio, Texas, United States

Tyler Research Institute, LLC

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Tyler, Texas, United States

University of Wisconsin Hospital and Clinics

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Madison, Wisconsin, United States

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