A B2-agonist as a CFTR activator in CF Part II
- Conditions
- Cystic Fibrosis
- Registration Number
- NL-OMON24538
- Lead Sponsor
- niversity Medical Center Utrecht
- Brief Summary
ot applicable
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Pending
- Sex
- Not specified
- Target Recruitment
- 20
Inclusion Criteria
CFTR genotype compound/A455E or compound/R117H
- Already had a rectal biopsy to produce an organoid
Exclusion Criteria
- Severe acute exacerbation or pulmonary infection during last four weeks (needing intravenous treatment and/or systemic corticosteroids)
- Known cardiovascular medical history like cardiac failure, arrhythmias, ischemic cardiac disease, long QT interval syndrome and hypertension
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Pulmonary function (spirometry and airway resistance measured with the bodybox and Rint)
- Secondary Outcome Measures
Name Time Method