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A Phase I, randomised, double blind, placebo-controlled, dose-escalating study of the safety, tolerability, food effect and pharmacokinetics of single and repeat doses of OCX063 administered orally to healthy volunteers

Phase 1
Completed
Conditions
Fibrotic ocular diseases
Inflammatory ocular diseases
Eye - Diseases / disorders of the eye
Registration Number
ACTRN12619001607167
Lead Sponsor
OccuRx Pty Ltd
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Male
Target Recruitment
64
Inclusion Criteria

Participants who;
- Provide written informed consent prior to any study procedures and agree to adhere to all protocol requirements.
- Are male aged 18 to 45 years old inclusive at the time of consent.
- Are in good general health without clinically significant medical history.
- Have a body mass index (BMI) less than 30kg/m2.
- Have negative Human Immunodeficiency Virus (HIV), Hepatitis B and Hepatitis C Screening test results.
- Agree to practice effective contraception during the study period and for 2 months after their last dose of study drug.

Exclusion Criteria

Participants who;
- Have received any other study drug within 30 days or 5 half-lives prior to Screening (4 months if the previous drug was a new chemical entity), whichever is longer.
- Have received an investigational vaccine within 6 months, a live attenuated vaccine within 60 days or a registered vaccine within 30 days prior to the first dose of the study drug.
- Have received blood products within 1 month prior to Screening.
- Have a history of thyroidectomy or thyroid disease that required medication within the past 12 months.
- Have had serious angioedema episodes within the previous 3 years or requiring angioedema medication in the previous two years.
- Have a bleeding disorder diagnosed by a doctor (e.g. factor deficiency, coagulopathy, or platelet disorder requiring special precautions) or significant bruising or bleeding difficulties with blood draws.
- Have a psychiatric condition that precludes compliance with the protocol; past or present psychoses; past or present bipolar disorder; disorder requiring lithium; or within five years prior to Screening, a history of suicide plan
- Have any clinically significant abnormality at Screening determined by medical history, physical examination, blood chemistry, haematology, urinalysis and a 12-lead electrocardiogram (ECG).
- Have any other condition which in the view of the Investigator is likely to interfere with the study or put the subject at risk.
- Have high risk behaviours for HIV or hepatitis B or C (i.e. injecting drug use, commercial sex work, unsafe sexual practices)
- Have a history of or current clinically significant gastrointestinal, hepatic, renal, cardiovascular, respiratory, endocrine, oncological, immunodeficiency, neurological, metabolic, haematological or autoimmune disorder; or a history of or current tuberculosis, epilepsy, diabetes or glaucoma
- Have clinical signs of active infection and/or a temperature of > 38.0°C at the time of Screening. Study entry may be deferred at the discretion of the Principal Investigator
- Have a positive alcohol breath test or urine screen for drugs of abuse at Screening or check-in, or evidence of drug or alcohol abuse in the investigator’s opinion.
- Are unable to provide a blood sample without undue trauma or distress.
- Have any other medical condition or significant co-morbidities, or any finding during Screening, which may interfere with the study objectives in the investigator’s opinion.
- Have a history of or current clinically relevant social, clinical, or psychiatric condition which, in the opinion of the investigator, makes the participant unsuitable for participation in the study

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Safety and tolerability will be assessed by vital signs, clinical safety labs, electrocardiograms (ECGs), physical exams and adverse events.[Part A and Part B: Daily in-patient monitoring for 3 days plus follow up visit on Day 8<br>Part C: Daily in-patient monitoring for 14 days plus follow up visit on Day 22]
Secondary Outcome Measures
NameTimeMethod
Plasma pharmacokinetics of OCX063, including AUC, Tmax, Cmax, T1/2[Part A and Part B: At 15, 30 minutes and 1, 2, 3, 4, 6, 8, 12, 24, 36, and 48 hours post dose<br><br>Part C: At 15, 30 minutes and 1, 2, 3, 4, 6, 8, 12, and 24 hours post dose, on Day 1 and Day 14, prior to drug administration on Day 8, and on Day 22.];Urine pharmacokinetics of OCX063, including absorption and elimination[Part A and Part B: Pooled samples 0-4, 4-12, 12-24 hours post dose, and a spot urine sample at 24, 36, and 48 hours post dose<br><br>Part C: Pooled samples samples 0-4, 4-12, 12-24 hours post dose, on Day 1 and Day 14, and spot samples prior to drug administration on Day 8, and on Day 22.]
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