JPRN-jRCT2080222577已完成3 期
Clinical Trial of EPI-743 in Patients with Leigh Syndrome [Extended Treatment Study]
适应症
试验速览
- 阶段
- 3 期
- 状态
- 已完成
- 入组人数
- 5
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional
入排标准
- 年龄范围
- ot applicable 至 ot applicable（—）
- 性别
- All
入选标准
- •- Patients with Leigh syndrome who have completed the preceding study and are willing to continue to receive EPI-743
- •- Patients who had no safety problems in the preceding study and are judged by the investigator or subinvestigator to be eligible for continuation of EPI-743
排除标准
- •- Allergy to EPI-743 or sesame oil
- •- Allergy to vitamin E
研究者
相似试验
进行中（未招募）
3 期
Clinical study on PTC743 in Patients with Leigh's Encephalomyelopathy (Continued Dosing Study)eigh's encephalomyelopathyJPRN-jRCT2031200224Penematsa Vinay12
已完成
2 期
Safety and Efficacy Study of EPI-743 in Children With Leigh SyndromeLeigh SyndromeNCT01721733PTC Therapeutics35
未知
3 期
A Phase 3 study of S-474474 in patients with essential hypertensioHypertensionJPRN-jRCT2080221505SHIONOGI & CO., LTD.
已完成
2 期
EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological ImpairmentMethylmalonic Aciduria and Homocystinuria,Cblc TypeRetinopathyGenetic DiseaseNCT01793090Bambino Gesù Hospital and Research Institute30
已完成
2 期
Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh SyndromeLeigh SyndromeNCT02352896PTC Therapeutics30