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Post-trial Access Program of Idursulfase-IT Along With Elaprase in Children With Hunter Syndrome

Conditions
Hunter Syndrome
Registration Number
NCT05795361
Lead Sponsor
Takeda
Brief Summary

As the HGT-HIT-046 (NCT01506141) and SHP609-302 (NCT02412787) studies will be closed, this post-trial access (PTA) program provides TAK-609 to participants in these studies for whom the benefit:risk ratio of continued treatment with idursulfase-IT remains positive.

Detailed Description

Not available

Recruitment & Eligibility

Status
AVAILABLE
Sex
Male
Target Recruitment
Not specified
Inclusion Criteria
  1. Participants will have completed the treatment period of the HGT-HIT-046 (NCT01506141) or SHP609-302 (NCT02412787) study prior to the first dose on this program.
  2. Participant and/or a parent(s)/legal guardian is informed of the nature of this compassionate post-trial access program and can provide written informed consent for themselves or the child to participate (with assent from the child when appropriate prior to treatment).
Exclusion Criteria
  1. Participant has a condition that in the opinion of the treating physician may compromise their safety.
  2. Participant has a known hypersensitivity to idursulfase-IT or its components.

Study & Design

Study Type
EXPANDED_ACCESS
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (22)

Phoenix Childrens Hospital

🇺🇸

Phoenix, Arizona, United States

The Nemours Foundation

🇺🇸

Wilmington, Delaware, United States

Jackson Memorial Hospital University of Miami

🇺🇸

Miami, Florida, United States

Ann and Robert H Lurie Childrens Hospital of Chicago

🇺🇸

Chicago, Illinois, United States

Washington University

🇺🇸

Washington, Missouri, United States

Board of Regents of the University of Nebraska

🇺🇸

Omaha, Nebraska, United States

The Regents of the University of California

🇺🇸

Oakland, California, United States

Joseph M. Sanzari Children's Hospital

🇺🇸

Hackensack, New Jersey, United States

NYU Langone Medical Center

🇺🇸

New York, New York, United States

The University of North Carolina

🇺🇸

Chapel Hill, North Carolina, United States

The Cleveland Clinic Foundation

🇺🇸

Cleveland, Ohio, United States

Randall Children's Hospital at Legacy Emanuel

🇺🇸

Portland, Oregon, United States

The Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

UPMC Childrens Hospital of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

Vanderbilt Children's Hospital

🇺🇸

Nashville, Tennessee, United States

Division of Medical Genetics, University of Utah

🇺🇸

Salt Lake City, Utah, United States

Seattle Children's Hospital - PIN

🇺🇸

Seattle, Washington, United States

Queensland Childrens Hospital

🇦🇺

South Brisbane, Queensland, Australia

Instituto Nacional de Pediatria

🇲🇽

Coyoacan, Ciudad De Mexico, Mexico

H.C.U. de Valladolid

🇲🇽

Valladolid, Mexico

Hospital Universitario Reina Sofia

🇪🇸

Cordoba, Spain

Royal Manchester Children's Hospital - PPDS

🇬🇧

Manchester, United Kingdom

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