MedPath

To Investigate Safety and Efficacy of NovoEight® (rFVIII) During Long-term Treatment of Haemophilia A in Japan

Completed
Conditions
Congenital Bleeding Disorder
Haemophilia A
Interventions
Registration Number
NCT02207218
Lead Sponsor
Novo Nordisk A/S
Brief Summary

This study is conducted in Asia. The aim of this study is to evaluate the safety and efficacy of NovoEight® (recombinant factor VIII) in patients with haemophilia A in Japan in the setting of routine clinical practice.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
40
Inclusion Criteria
  • Informed consent obtained before any study-related activities. Study-related activities are any procedure related to recording of data according to the protocol
  • Male and female patients with the diagnosis of haemophilia A
  • Age range is 0 year and above
  • A decision to initiate treatment with commercially available NovoEight® has been made by the patient/parent and the physician
Exclusion Criteria
  • Known or suspected allergy to study product(s) or related products
  • Previous participation in this study. Participation is defined as informed consent obtained
  • Mental incapacity, unwillingness or language barriers precluding adequate understanding or cooperation

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
NovoEight®turoctocog alfa-
Primary Outcome Measures
NameTimeMethod
Frequency of Adverse Events (AEs)Week 0- 104
Secondary Outcome Measures
NameTimeMethod
Consumption of NovoEight® per month (IU/kg BW/month) for preventionWeek 0- 104
Frequency of Serious Adverse Reactions (SARs)Week 0- 104
Haemostatic effect of NovoEight® during surgical procedures assessed by evaluation according to a predefined four point scale: Excellent, Good, Moderate, or NoneWeek 0- 104
Annualised bleeding rate for patients using NovoEight® for preventive regimenWeek 0- 104
Total consumption of NovoEight® per patient (prevention, treatment of bleeds and surgery) per year (IU/kg BW/year/patient)Week 0- 104
Consumption of NovoEight® (IU/kg BW) from the day of surgery until the day of return to preventive regimen or on-demand treatment regimenWeek 0- 104
Frequency of Adverse Reactions (ARs)Week 0- 104
Haemostatic effect of NovoEight® in the treatment of bleeds according to a predefined four point scale: Excellent, Good, Moderate, or None for patients with preventive regimen and on-demand treatment regimen, respectivelyWeek 0- 104
Consumption of NovoEight® per bleed (IU/kg BW/bleeding episode)Week 0- 104
Frequency of Serious Adverse Events (SAEs)Week 0- 104

Trial Locations

Locations (1)

Novo Nordisk Investigational Site

🇯🇵

Tokyo, Japan

© Copyright 2025. All Rights Reserved by MedPath