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Tovorafenib (DAY101) or in Combination With Pimasertib for Participants With Melanoma and Other Solid Tumors

Not Applicable
Terminated
Conditions
Melanoma
Pancreatic Cancer
MAP Kinase Family Gene Mutation
RAS Mutation
Solid Tumor
RAF Mutation
Pilocytic Astrocytoma
Colorectal Cancer
Non Small Cell Lung Cancer
MEK Mutation
Interventions
Registration Number
NCT07121829
Lead Sponsor
Day One Biopharmaceuticals, Inc.
Brief Summary

This is a subprotocol of Master Protocol DAY101-102 and is a Phase 1b/2, multi-center, open label subprotocol of participants ≥12 years of age, with recurrent or progressive solid tumors with alterations in the key proteins of the MAPK pathway, such as tumors that harbor RAS or RAF alterations.

\*Note: Study concluded as Phase 1b only.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
44
Inclusion Criteria
  • Signed informed consent by participant ≥12 years of age; either a Consent or an Assent Form will be provided to the patient based on their capacity, local regulations, and guidelines.
  • Participants must have a report of histologically confirmed diagnosis of tumor and a concurrent MAPK pathway alteration (genomic alterations in RAS, RAF, MEK, or NF1) obtained through a tumor or liquid biopsy as assessed by genomic sequencing, polymerase chain reaction (PCR), fluorescence in situ hybridization (FISH), or another clinically accepted molecular diagnostic method recognized by local laboratory or regulatory agency
  • Participants must have radiographically stable, recurrent or progressive disease that is measurable using the appropriate tumor response criteria eg, (RECIST version 1.1, RANO)
  • Archival tumor tissue should be preferably less than 3 years old. If unavailable, a freshly acquired tumor tissue biopsy or liquid biopsy is required
  • If brain metastases are present, they must have been previously treated and be stable as assessed by radiographic imaging
Exclusion Criteria
  • Known presence of concurrent activating alterations
  • Participants with current evidence or a history of serous retinopathy (SR), retinal vein occlusion (RVO) or ophthalmopathy present at screening or baseline who would be considered at risk for SR or RVO
  • Participants who have an unstable neurological condition, despite adequate treatment (eg, uncontrolled seizures)
  • Participants with history of acute neurological events (such as intracranial or subarachnoid hemorrhage, stroke, intracranial trauma) within the past 6 months
  • History of second malignancy within 3 years prior to study treatment except for curatively treated cervical cancer in situ, non-melanoma skin cancer, or superficial bladder cancer

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Experimental ArmTovorafenibTovorafenib plus pimasertib
Primary Outcome Measures
NameTimeMethod
Number of participants who will report Treatment emergent adverse events (TEAEs) and serious TEAEsUp to 30 days after the last dose of any study drug
Number of participants who will report clinically significant changes in vital signsUp to 30 days after the last dose of any study drug
Number of participants who will report clinically significant changes in clinical chemistry parametersUp to 30 days after the last dose of any study drug
Number of participants who will report clinically significant changes in hematology parametersUp to 30 days after the last dose of any study drug
Number of participants with Dose limiting toxicities (DLTs)Up to 30 days after the last dose of any study drug
Secondary Outcome Measures
NameTimeMethod
Percentage of participants with complete overall response rate (ORR)Up to 30 months

ORR as assessed by the proportion of participants with the best overall confirmed response of complete response (CR) or partial response (PR) according to the appropriate tumor response criteria as assessed by Investigator

Duration of response (DOR)Up to 30 months

The interval from the date of the first documentation of tumor response (CR or PR) that was subsequently confirmed by investigator assessment to the date of first occurrence of radiographic disease progression based on appropriate tumor response criteria as assessed by investigator or death due to any cause, whichever occurs earlier.

Progression Free Survival (PFS)Up to 30 months

The interval from the date of the first dose to the first occurrence of radiographic disease progression based on appropriate tumor response criteria as assessed by investigator or death due to any cause, whichever occurs earlier.

Overall Survival (OS)Up to 30 months

The interval from the date of the first dose until the recorded date of death due to any cause.

Time to ResponseUp to 30 months

Defined in participants with best overall response of CR or PR as determined by Investigator, time to response is defined as the interval from the date of the first dose to date of first documentation of tumor response (CR or PR) that was subsequently confirmed by investigator assessment.

Plasma concentration of DAY101Cycles 1 through Cycle 11 (each cycle is 28 days)
Maximum drug concentration (Cmax) of DAY101Cycle 1, Day 1 through Cycle 1, Day 22
Area Under the Curve from Time Zero to Last Measurable Concentration (AUC 0-last)Cycle 1, Day 1 through Cycle 1, Day 22
Change in gene expression levels in pre and post treatment samples using RNA sequencing (RNA seq) analysis.Up to 30 months
Change in expression levels of phosphorylated ERK (pERK) and Ki67 in pre and post treatment samples using immunohistochemistry methodology.Up to 30 months

Trial Locations

Locations (10)

The Angeles Clinic

🇺🇸

Los Angeles, California, United States

Hoag Health

🇺🇸

Newport Beach, California, United States

University of Colorado Hospital

🇺🇸

Aurora, Colorado, United States

Cancer Specialists of North Florida

🇺🇸

Jacksonville, Florida, United States

Community North Cancer Center

🇺🇸

Indianapolis, Indiana, United States

OHSU Knight Cancer Institute

🇺🇸

Portland, Oregon, United States

UPMC Hillman Cancer Center

🇺🇸

Pittsburgh, Pennsylvania, United States

vanderbilt-Ingram Cancer Center

🇺🇸

Nashville, Tennessee, United States

Princess Margaret Cancer Centre

🇨🇦

Toronto, Ontario, Canada

The Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

The Angeles Clinic
🇺🇸Los Angeles, California, United States

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