MedPath

Efficacy and Safety Study of Rimegepant for the Preventative Treatment of Migraine in Pediatric Subjects

Phase 3
Recruiting
Conditions
Migraine
Interventions
Drug: Placebo
Registration Number
NCT05156398
Lead Sponsor
Pfizer
Brief Summary

The purpose of this study is to compare the efficacy and safety of rimegepant to placebo as a preventative treatment for migraine in children and adolescents ≥ 6 to \<18 years with episodic migraine.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
640
Inclusion Criteria
  1. Subject has at least a 6 month history of migraine (with or without aura) and including the following:

    1. 14 or less headache days per month during the 3 month period prior to the Screening Visit

    2. 6 or more migraine days during the Observation Period

    3. 14 or less headache days during the Observation Period

    4. Pediatric Migraine Disability Assessment Scale (PedMIDAS) Disability Score of >10 to ≤50, indicating mild (score of 11 to 30) or moderate (score of 31 to 50) disruption in daily activities, as assessed at the Baseline (Randomization) Visit

    5. Ability to verbally distinguish migraine attacks from tension/cluster or other types of headaches

    6. Migraine attacks, on average, lasting 4 - 72 hours if untreated

    7. Subjects on prophylactic migraine medication are permitted to remain on therapy if the dose has been stable for at least 3 months (12 weeks) prior to the Screening Phase, and the dose is not expected to change during the course of the study. 2) Male and female subjects ≥ 6 to <18 years; subjects must be less than 18 at the time of signing assent / consent.

      3)Subjects must have a weight of ≥40 kg (child cohort requirement ≥15 kg) at the Screening Visit.

Exclusion Criteria
  1. Subjects with a history of basilar migraine, cluster headaches, or hemiplegic migraine
  2. The subject has a continuous migraine (defined as an unrelenting headache) within 1 month prior to Screening Visit.
  3. The subject has a history or diagnosis of complications of migraine
  4. The subject has a confounding and clinically significant pain syndrome that may interfere with the subject's ability to participate in this study.
  5. The subject has any current psychiatric condition that is uncontrolled and/or untreated for a minimum of 6 months prior to the Screening Visit. Subjects with a lifetime history of psychosis and/or mania are excluded.
  6. History of suicidal behavior or the subject is at risk of self-harm or harm to others.
  7. History of major psychiatric disorder.
  8. The subject has a current diagnosis or history of substance abuse
  9. The subject has a history of moderate or severe head trauma or other neurological disorder (including seizure disorder) or systemic medical disease that is, in the investigator's opinion, likely to affect central nervous system functioning.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Rimegepant / BHV3000RimegepantRimegepant 75mg or 50mg (2 X 25mg) ODT
Matching PlaceboPlaceboMatching placebo 75mg or 50mg (2 X 25mg) ODT
Primary Outcome Measures
NameTimeMethod
Change from baseline in the mean number of migraine days per month as measured over the 12-week double-blind phase of the study in adolescents with episodic migraine3 months (12 weeks)

Reduction from baseline in mean number of migraine days per month

Secondary Outcome Measures
NameTimeMethod
Achievement of at least a 50% reduction from baseline in mean monthly migraine days over the course of the double-blind phase in adolescents with episodic migraine3 months (12 weeks)
Change from baseline in the mean number of migraine days per month over the entire course of the double-blind treatment phase in children and children and adolescents combined with episodic migraine.3 months (12 weeks)
Compare the use of acute migraine-specific medications (triptans) based on the change from baseline in monthly acute migraine specific medication days.3 months (12 weeks)

Measured in each month and over the course of the entire double-blind treatment phase in adolescents, children and adolescents and children combined.

Change from baseline in the mean number of migraine days per month in the first 4 weeks (Weeks 1 through 4) of the double-blind treatment phase in adolescents with episodic migraine.Weeks 1 through 4 of treatment
The mean change from baseline in the Pediatric Quality of Life (PedsQL™) total score at Week 12 of the double-blind treatment phase in adolescents with episodic migraine.Total score at week 12
Change from baseline on the proportion of subjects that have at least a 50% reduction in the mean number of moderate to severe migraine days per month.3 months (12 weeks)

Measured over the entire course of the double-blind treatment phase in children and children and adolescents combined with episodic migraine.

Evaluate the safety and tolerability of rimegepant as a preventative treatment for migraine in children and adolescents.72 Weeks

This will be evaluated by the number of subjects with treatment related adverse events by severity.

Evaluate the frequency of hepatic-related adverse events in subjects treated with rimegepant.72 Weeks

Measured by discontinuations in treated subjects due to elevated liver function tests.

Trial Locations

Locations (93)

Wojewodzki Specjalistyczny Szpital Dzieciecy

🇵🇱

Krakow, Malopolskie, Poland

Diamond Headache Clinic

🇺🇸

Chicago, Illinois, United States

The Belinga Clinic

🇺🇸

Fort Smith, Arkansas, United States

Advanced Investigative Medicine, Inc.

🇺🇸

Hawthorne, California, United States

Velocity Clinical Research San Diego

🇺🇸

La Mesa, California, United States

Colorado Springs Neurological Associates

🇺🇸

Colorado Springs, Colorado, United States

Advanced Neurosciences Research, LLC

🇺🇸

Fort Collins, Colorado, United States

Meridian Clinical Research, LLC

🇺🇸

Portsmouth, Virginia, United States

Synergy Healthcare

🇺🇸

Bradenton, Florida, United States

Accel Research Sites Network - Edgewater Clinical Research Unit

🇺🇸

Edgewater, Florida, United States

Direct Helpers Research Center

🇺🇸

Hialeah, Florida, United States

New Med Research, Inc

🇺🇸

Hollywood, Florida, United States

Complete Health Research

🇺🇸

Ormond Beach, Florida, United States

D&H Tamarac Research Center LLC

🇺🇸

Tamarac, Florida, United States

Santos Research Center, CORP

🇺🇸

Tampa, Florida, United States

Augusta University

🇺🇸

Augusta, Georgia, United States

WR-Mount Vernon Clinical Research, LLC

🇺🇸

Sandy Springs, Georgia, United States

Extraordinary Family Healthcare

🇺🇸

Snellville, Georgia, United States

Renew Health Clinical Research LLC

🇺🇸

Snellville, Georgia, United States

Northwest Clinical Trials, Inc.

🇺🇸

Boise, Idaho, United States

Safe Haven Clinical Research

🇺🇸

Clinton, Mississippi, United States

University of Missouri - Investigational Pharmacy

🇺🇸

Columbia, Missouri, United States

Velocity Clinical Research, Inc.

🇺🇸

Grand Island, Nebraska, United States

Papillion Research Center/CCT Research

🇺🇸

Papillion, Nebraska, United States

Renown Regional Medical Center

🇺🇸

Reno, Nevada, United States

Dent Neurosciences Research Center, Inc.

🇺🇸

Amherst, New York, United States

Montefiore Medical Center

🇺🇸

Bronx, New York, United States

Carolina Institute for Clinical Research, LLC

🇺🇸

Fayetteville, North Carolina, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Velocity Clinical Research

🇺🇸

Cincinnati, Ohio, United States

Lynn Health Science Institute

🇺🇸

Oklahoma City, Oklahoma, United States

Coastal Pediatric Research

🇺🇸

Charleston, South Carolina, United States

Tribe Clinical Research LLC

🇺🇸

Greenville, South Carolina, United States

Avera McKennan Hospital & University Health Center

🇺🇸

Sioux Falls, South Dakota, United States

Avera Medical Group Pediatric Specialists

🇺🇸

Sioux Falls, South Dakota, United States

Avera Research Institute

🇺🇸

Sioux Falls, South Dakota, United States

Monroe Carell Jr Children's Hospital at Vanderbilt

🇺🇸

Nashville, Tennessee, United States

Alina Clinical Trials, LLC.

🇺🇸

Dallas, Texas, United States

North Texas Center for Clinical Research

🇺🇸

Frisco, Texas, United States

DM Clinical Research - Cy Fair

🇺🇸

Houston, Texas, United States

SCLA Management - Drop Box

🇺🇸

Houston, Texas, United States

SCLA Management Office

🇺🇸

Houston, Texas, United States

NeuroCare Plus

🇺🇸

Houston, Texas, United States

Red Star Research, LLC

🇺🇸

Lake Jackson, Texas, United States

DCT-McAllen Primary Care Research, LLC dba Discovery Clinical Trials

🇺🇸

McAllen, Texas, United States

DCT-Stone Oak, LLC dba Discovery Clinical Trials

🇺🇸

San Antonio, Texas, United States

Texas Institute for Neurological Disorders

🇺🇸

Sherman, Texas, United States

DM Clinical Research (Administrative Office Only)

🇺🇸

Tomball, Texas, United States

Victoria Clinical Research Group

🇺🇸

Victoria, Texas, United States

South Ogden Family Medicine Ogden Clinic/CCT Research

🇺🇸

South Ogden, Utah, United States

Children's and Women's Health Centre of British Columbia

🇨🇦

Vancouver, British Columbia, Canada

Children's Hospital of Eastern Ontario

🇨🇦

Ottawa, Ontario, Canada

Centre Hospitalier Intercommunal de Créteil

🇫🇷

Créteil, France

Centre Hospitalier Universitaire de Montpellier

🇫🇷

Montpellier, France

Hopital des Enfants

🇫🇷

Toulouse, France

Unita di Neurologia, Azienda Ospedaliera San Giuseppe Moscati

🇮🇹

Avellino, Avellino/campania, Italy

UOSVD Centro Epilessia ed EEG dellEta Evolutiva

🇮🇹

Bari, BARI / Puglia, Italy

Spedali Civili di Brescia

🇮🇹

Brescia, Brescia/lombardy, Italy

Azienda Ospedaliero Universitaria Meyer

🇮🇹

Florence, Florence/tuscany, Italy

Sapienza Universita di Roma Polo Pontino - ICOT, Headache clinic

🇮🇹

Latina, Latina/lazio, Italy

Ospedale Pediatrico Bambino Gesu

🇮🇹

Roma, Lazio, Italy

IRCCS San Raffaele

🇮🇹

Roma, Lazio, Italy

Istituto Neurologico "Carlo Besta" Fondazione IRCCS

🇮🇹

Milano, Lombardia, Italy

U.O. Neuropsichiatria Infantile, IRCCS Fondazione Mondino

🇮🇹

Pavia, Lombardia, Italy

Dipartimento Materno Infantile e Scienze UroGinecologiche - UOC Pediatria

🇮🇹

Roma, Italy

Jinnouchi Neurosurgical Clinic

🇯🇵

Kasuga-shi, Fukuoka, Japan

Hikita Pediatric Clinic

🇯🇵

Kiryu-shi, Gunma, Japan

Konan Medical Center

🇯🇵

Higashinada-ku Kobe-shi, Hyōgo, Japan

Yamaguchi Clinic

🇯🇵

Nishinomiya-shi, Hyōgo, Japan

Mito Kyodo General Hospital

🇯🇵

Mito-shi, Ibaraki, Japan

Tanaka Neurosurgery & Headache Clinic

🇯🇵

Kagoshima-city, Kagoshima, Japan

Atago Hospital

🇯🇵

Kochi-shi, Kōchi, Japan

Sendai Headache and Neurology Clinic

🇯🇵

Taihaku-ku Sendai-shi, Miyagi, Japan

Tennouji Dai Brain Clinic

🇯🇵

Abeno-ku Osaka-shi, Osaka, Japan

Tominaga Clinic

🇯🇵

Naniwa-ku, Osaka, Japan

Saitama Neuropsychiatric Institute

🇯🇵

Chuo-ku Saitama-shi, Saitama, Japan

Tokyo Headache Clinic

🇯🇵

Shibuya-ku, Tokyo, Japan

Tokyo Medical University Hospital

🇯🇵

Shinjuku-ku, Tokyo, Japan

LIAC Hiroshima City Hospital Organization Hiroshima City Hiroshima Citizens Hospital

🇯🇵

Hiroshima, Japan

MIGRE Polskie Centrum Leczenia Migreny Anna Gryglas-Dworak

🇵🇱

Wroclaw, Dolnoslaskie, Poland

NZOZ Neuromed M. i M. Nastaj Sp. P.

🇵🇱

Lublin, Lubelskie, Poland

MTZ Clinical Research Powered by Pratia

🇵🇱

Warszawa, Mazowieckie, Poland

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS

🇵🇱

Katowice, Slaskie, Poland

Neurologia Slaska Centrum Medyczne

🇵🇱

Katowice, Slaskie, Poland

Clinical Research Center Sp. z o.o. MEDIC-R Sp. k.

🇵🇱

Poznan, Wielkopolskie, Poland

Next Stage Sp. Z o.o.

🇵🇱

Warsaw, WOJ. Mazowieckie, Poland

Hospital Universitari Parc Tauli

🇪🇸

Sabadell, Barcelona, Spain

Hospital Clinico Universitario de Valladolid (HCUV)

🇪🇸

Valladolid, Castilla Y LEON, Spain

Hospital Alvaro Cunqueiro

🇪🇸

Vigo, Galicia, Spain

Hospital Clinico Universitario de Santiago de Compostela

🇪🇸

Santiago de Compostela, LA Coruna, Spain

Instituto de Investigaciones del Sueno

🇪🇸

Madrid, Spain

Virgen del Rocio Hospital

🇪🇸

Sevilla, Spain

Hospital Universitario y Politecnico La Fe

🇪🇸

Valencia, Spain

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