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Safety and Efficacy of Tarperprumig in Adult Participants With Anti-Neutrophil Cytoplasmic Antibody (ANCA)-Associated Vasculitis

Not Applicable
Not yet recruiting
Conditions
Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis
Interventions
Drug: Placebo
Registration Number
NCT07160608
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Brief Summary

The primary objective of this study is to evaluate the safety and tolerability of tarperprumig in participants with newly diagnosed or relapsing anti-neutrophil cytoplasmic antibody (ANCA)-associated vasculitis.

Detailed Description

Not available

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
75
Inclusion Criteria
  • Newly diagnosed or relapsing ANCA-associated vasculitis, GPA and MPA subtypes consistent with the 2022 ACR/EULAR classification criteria for GPA and MPA for whom treatment with rituximab or cyclophosphamide is considered.
  • Positive test for antibodies to either PR3-ANCA or MPO-ANCA at Screening or in the past by a quantitative assay (for example, ELISA, bead assay).
  • At least one major item, or at least 3 minor items, or at least 2 renal items in the BVAS.
Exclusion Criteria
  • Other systemic diseases that, in the judgment of the Investigator, constitute the primary illness, including but not limited to: eosinophilic granulomatosis with polyangiitis (EGPA), systemic lupus erythematosus, IgA nephropathy and/or IgA associated vasculitis with or without Henoch-Schonlein purpura, rheumatoid vasculitis, Sjogren's syndrome, anti-GBM disease, cryoglobulinemic vasculitis, autoimmune hemolytic anemia, or mixed connective tissue disease.
  • Alveolar hemorrhage requiring invasive pulmonary ventilation support at Screening.
  • Any diseases or conditions that, in the judgment of the Investigator, present a substantial clinical risk to participate in this study.
  • For patients with a previous diagnosis of CKD, patients known to have a stable eGFR for greater than 3 months prior to Screening and a decline less than 25% of previous eGFR at Screening will be excluded.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Tarperprumig Group 1TarperprumigParticipants will be administered tarperprumig dose regimen #1 or dose regimen #2.
Tarperprumig Group 2PlaceboParticipants will be administered tarperprumig dose regimen #1 or dose regimen #2.
Tarperprumig Group 2TarperprumigParticipants will be administered tarperprumig dose regimen #1 or dose regimen #2.
Placebo Group 3PlaceboParticipants will be administered placebo.
Primary Outcome Measures
NameTimeMethod
Number of Participants With Treatment-emergent Adverse Events (TEAEs)Baseline through Week 70
Secondary Outcome Measures
NameTimeMethod
Number of Participants Achieving Disease Remission at Week 26Week 26
Number of Participants Achieving Sustained Remission at Week 52Week 52
Number of Participants Achieving a Birmingham Vasculitis Activity Score (BVAS) of 0Baseline through Week 52
Number of Participants Experiencing a Relapse After Previously Achieving Disease Remission at Week 26Week 26 through Week 70
Time to First Relapse After Having Achieved Disease Remission at Week 26Week 26 through Week 70
Change from Baseline in Vasculitis Damage IndexBaseline, Weeks 26, and 52
Time to First Occurrence of BVAS of 0Baseline through Week 52
Change from Baseline in BVASBaseline, Weeks 26, and 52
Change from Baseline in Estimated Glomerular Filtration RateBaseline, Weeks 26, and 52
Change from Baseline in Proteinuria Based on Spot Urine Protein-Creatinine RatioBaseline, Weeks 26, and 52
Change from Baseline in Proteinuria Based on Spot Urine Albumin-Creatinine RatioBaseline, Weeks 26, and 52
Change from Baseline in HematuriaBaseline, Weeks 26, and 52

Trial Locations

Locations (1)

Research Site

🇬🇧

Manchester, United Kingdom

Research Site
🇬🇧Manchester, United Kingdom

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