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efficacy and safety of deferasirox in patients with non-transfusion dependent thalassemia

Phase 1
Conditions
iron overload in patients with non-transfusion dependent thalassemia
MedDRA version: 20.0Level: HLTClassification code 10022979Term: Iron excessSystem Organ Class: 100000004861
Therapeutic area: Diseases [C] - Blood and lymphatic diseases [C15]
Registration Number
EUCTR2012-000650-64-GB
Lead Sponsor
ovartis Pharma Services AG
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
134
Inclusion Criteria

• Male or female aged = 10 years with non-transfusion-dependent congenital or chronic anemias inclusive of beta-thalassemia intermedia, HbE beta-thalassemia or alpha-thalassemia intermedia (HbH disease)
• LIC = 5 mg Fe/g dw measured by R2 MRI at screening
• Serum ferritin = 300 ng/mL at screening (two consecutive values at least 14 days apart from each other)
Additional inclusion criteria as per full protocol may apply
Are the trial subjects under 18? yes
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range
F.1.3 Elderly (>=65 years) yes
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

• HbS-beta Thalassemia
• Anticipated regular transfusion program during the study
• Any blood transfusion 6 months prior to study start
• Significant proteinuria
• creatinine clearance =40 ml/min
• serum creatinine >ULN; ALT >5xULN
Additional exclusion criteria as per full protocol may apply

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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