MedPath

Recombinant Factor VIIa (rFVIIa) for Hemorrhagic Stroke Trial

Phase 3
Recruiting
Conditions
Intracerebral Hemorrhage
Interventions
Biological: Recombinant Activated Factor VII (rFVIIa)
Biological: Placebo
Registration Number
NCT03496883
Lead Sponsor
Joseph Broderick, MD
Brief Summary

The objective of the rFVIIa for Acute Hemorrhagic Stroke Administered at Earliest Time (FASTEST) Trial is to establish the first treatment for acute spontaneous intracerebral hemorrhage (ICH) within a time window and subgroup of patients that is most likely to benefit. The central hypothesis is that rFVIIa, administered within 120 minutes from stroke onset with an identified subgroup of patients most likely to benefit, will improve outcomes at 180 days as measured by the Modified Rankin Score (mRS) and decrease ongoing bleeding as compared to standard therapy.

Detailed Description

The investigators will perform a global, Phase III, randomized, double-blind controlled trial of rFVIIa plus best standard therapy vs. placebo and best standard therapy alone. The investigators will include participants with a volume of ICH ≥ 2 and \< 60 cc, no more than a small volume of intraventricular hemorrhage (IVH) (IVH score ≤ 7), age ≥ 18 and ≤ 80, Glasgow Coma Scale of ≥ 8, and treated within 120 minutes from stroke onset. To minimize time-to-treatment, the study will use emergency research informed consent procedures (including exception from informed consent (EFIC) in the United States) and mobile stroke units (MSUs), with a goal of ½ of participants treated within 90 minutes, as accomplished in the NINDS t-PA trials. The FASTEST Trial will include approximately 100 hospital sites and at least 15 MSUs in the NINDS-funded StrokeNet and key global institutions with large volumes of ICH patients and the ability to treat them within 120 minutes of stroke onset. Recruitment of 860 participants over 3½ years is planned. Countries participating in the trial include the United States, Canada, Japan, Germany, Spain, and the United Kingdom. Involving other countries may be possible in the future depending upon recruitment needs.

Participants will be randomized in a double-blinded fashion to rFVIIa 80 µg/kg dose (maximum 10 mg dose) or placebo. Participants in both arms will receive best standard therapy as per published AHA Guidelines for ICH, including a target systolic blood pressure of 140 mm Hg. The primary outcome (ordinal mRS with the following categories: 0-2, 3, and 4-6) will be determined at 180 days, but participants will be followed by remote assessment at 30 days and 90 days. To measure growth of ICH, all participants will have a standard of care baseline non-contrast CT of the head and a repeat scan at 24 hours. Centralized volumetric measurements of ICH, IVH, and edema will be performed for both time points.

Novo Nordisk A/S will manufacture and supply rFVIIa as a research medication for use in the FASTEST Trial. Novo Nordisk A/S will also manufacture and supply matching placebo that is identical to rFVIIa in appearance and administration.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
860
Inclusion Criteria
  1. Patients aged 18-80 years, inclusive
  2. Patients with spontaneous ICH
  3. Able to treat with study medication (rFVIIa/placebo) within 120 minutes of stroke onset or last known well
  4. Efforts to obtain informed consent per EFIC guidelines (U.S.) or adherence to country-specific emergency research informed consent regulations (Canada, Germany, Spain, U.K., Japan)
Exclusion Criteria
  1. Score of 3 to 7 on the Glasgow Coma Scale
  2. Secondary ICH related to known causes (e.g., trauma, aneurysm, arteriovenous malformation (AVM), oral anticoagulant use (vitamin K antagonists or novel oral anticoagulants) within the past 7 days, coagulopathy, etc.)
  3. ICH volume < 2 cc or ≥ 60 cc
  4. Blood filling 2/3 or more of one lateral ventricle of the brain, OR, blood filling at least 1/3 of both lateral ventricles.
  5. Pre-existing disability (mRS > 2)
  6. Symptomatic thrombotic or vaso-occlusive disease in past 90 days (e.g., cerebral infarction, myocardial infarction, pulmonary embolus, deep vein thrombosis, or unstable angina)
  7. Clinical or EKG evidence of ST elevation consistent with acute myocardial ischemia
  8. Brainstem location of hemorrhage (patients with cerebellar hemorrhage may be enrolled)
  9. Refusal to participate in study by patient, legal representative, or family member
  10. Known or suspected thrombocytopenia (unless current platelet count documented above 50,000/μL)
  11. Unfractionated heparin use with abnormal PTT
  12. Pro-coagulant drugs within 24 hours prior to patient enrollment into the FASTEST trial (example, tranexamic acid or aminocaproic acid)
  13. Low-molecular weight heparin use within the previous 24 hours
  14. Recent (within 90 days) carotid endarterectomy or coronary or cerebrovascular angioplasty or stenting
  15. Advanced or terminal illness or any other condition the investigator feels would pose a significant hazard to the patient if rFVIIa were administered
  16. Recent (within 30 days) participation in any investigational drug or device trial or earlier participation in any investigational drug or device trial for which the duration of effect is expected to persist until to the time of FASTEST enrollment
  17. Planned withdrawal of care or comfort care measures
  18. Patient known or suspected of not being able to comply with trial protocol (e.g., due to alcoholism, drug dependency, or psychological disorder)
  19. Known or suspected allergy to trial medication(s), excipients, or related products
  20. Contraindications to study medication
  21. Previous participation in this trial (previously randomized)
  22. Females of childbearing potential who are known to be pregnant or within 12 weeks post-partum and/or lactating at time of enrollment

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Recombinant Activated Factor VII (rFVIIa)Recombinant Activated Factor VII (rFVIIa)rFVIIa given as IV injection over 2 minutes within 120 minutes of stroke onset
PlaceboPlaceboMatching placebo given as IV injection over 2 minutes within 120 minutes of stroke onset
Primary Outcome Measures
NameTimeMethod
Modified Rankin Scale (mRS)180 days

Ordinal distribution with the following steps: 0-2, 3, 4-6

Secondary Outcome Measures
NameTimeMethod
Change in the volume of ICH and ICH+IVHBetween baseline CT and 24-hour CT

As measured by non-contrast CT of the head

mRS180 days

Ordinal distribution

EQ-5D90 days

Quality of life scale

Trial Locations

Locations (89)

University of Alabama Hospital

🇺🇸

Birmingham, Alabama, United States

St. Joseph's Hospital and Medical Center

🇺🇸

Phoenix, Arizona, United States

Kaiser Permanente Baldwin Park Medical Center

🇺🇸

Baldwin Park, California, United States

Mills Peninsula Medical Center

🇺🇸

Burlingame, California, United States

Kaiser Permanente Downey Medical Center

🇺🇸

Downey, California, United States

Kaiser Permanente Fontana Medical Center

🇺🇸

Fontana, California, United States

Kaiser Permanente South Bay Medical Center

🇺🇸

Harbor City, California, United States

UCSD Health La Jolla

🇺🇸

La Jolla, California, United States

Kaiser Permanente Los Angeles Medical Center

🇺🇸

Los Angeles, California, United States

Kaiser Permanente West Los Angeles Medical Center

🇺🇸

Los Angeles, California, United States

Ronald Reagan UCLA Medical Center

🇺🇸

Los Angeles, California, United States

UC Irvine Medical Center,

🇺🇸

Orange, California, United States

Kaiser Permanente Riverside Medical Center

🇺🇸

Riverside, California, United States

UC Davis Medical Center

🇺🇸

Sacramento, California, United States

UCSD Medical Center - Hillcrest Hospital

🇺🇸

San Diego, California, United States

San Francisco General Hospital

🇺🇸

San Francisco, California, United States

UF Health Shands Hospital

🇺🇸

Gainesville, Florida, United States

Mayo Clinic

🇺🇸

Jacksonville, Florida, United States

Grady Memorial Hospital

🇺🇸

Atlanta, Georgia, United States

WellStar Kennestone Hospital

🇺🇸

Marietta, Georgia, United States

The Queen's Medical Center

🇺🇸

Honolulu, Hawaii, United States

Northwestern Memorial Hospital

🇺🇸

Chicago, Illinois, United States

University of Chicago Medical Center

🇺🇸

Chicago, Illinois, United States

Central DuPage Hospital

🇺🇸

Winfield, Illinois, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

UMass Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

M Health Fairview Ridges Hospital,

🇺🇸

Burnsville, Minnesota, United States

M Health Fairview Southdale Hospital

🇺🇸

Edina, Minnesota, United States

M Health Fairview St. John's Hospital

🇺🇸

Maplewood, Minnesota, United States

M Health Fairview University of Minnesota Medical Center Hospital,

🇺🇸

Minneapolis, Minnesota, United States

Mayo Clinic Saint Marys Campus

🇺🇸

Rochester, Minnesota, United States

Regions Hospital

🇺🇸

St Paul, Minnesota, United States

Barnes Jewish Hospital

🇺🇸

St. Louis, Missouri, United States

North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Mount Sinai West

🇺🇸

New York, New York, United States

The Mount Sinai Hospital

🇺🇸

New York, New York, United States

Stony Brook University Hospital

🇺🇸

Stony Brook, New York, United States

Wake Forest Baptist Medical Center

🇺🇸

Winston-Salem, North Carolina, United States

University of Cincinnati Medical Center

🇺🇸

Cincinnati, Ohio, United States

OSU Wexner Medical Center

🇺🇸

Columbus, Ohio, United States

Riverside Methodist Hospital

🇺🇸

Columbus, Ohio, United States

Toledo Hospital

🇺🇸

Toledo, Ohio, United States

St. John Medical Center

🇺🇸

Tulsa, Oklahoma, United States

Providence St. Vincent Medical Center

🇺🇸

Portland, Oregon, United States

Temple University Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Medical University of South Carolina University Hospital

🇺🇸

Charleston, South Carolina, United States

Prisma Health Greenville Memorial Hospital

🇺🇸

Greenville, South Carolina, United States

Memorial Hermann Memorial City Medical Center

🇺🇸

Houston, Texas, United States

Memorial Hermann-Texas Medical Center

🇺🇸

Houston, Texas, United States

University of Utah Healthcare

🇺🇸

Salt Lake City, Utah, United States

VCU Medical Center

🇺🇸

Richmond, Virginia, United States

University of Calgary - Foothills Medical Centre

🇨🇦

Calgary, Alberta, Canada

University of Alberta Hospital

🇨🇦

Edmonton, Alberta, Canada

Vancouver General Hospital

🇨🇦

Vancouver, British Columbia, Canada

Hamilton General Hospital

🇨🇦

Hamilton, Ontario, Canada

Ottawa Hospital Research Institute

🇨🇦

Ottawa, Ontario, Canada

Sunnybrook Health Sciences Center

🇨🇦

Toronto, Ontario, Canada

St. Michaels Hospital

🇨🇦

Toronto, Ontario, Canada

University of Montreal Hospital

🇨🇦

Montreal, Quebec, Canada

University Hospital Heidelberg

🇩🇪

Heidelberg, Baden-Württemberg, Germany

Clinic Frankfurt Hoechst

🇩🇪

Frankfurt, Hessen, Germany

University Hospital Augsburg

🇩🇪

Augsburg, Germany

Charite University Medicine Berlin

🇩🇪

Berlin, Germany

University Hospital Tuebingen

🇩🇪

Tuebingen, Germany

National Cerebral and Cardiovascular Center

🇯🇵

Suita, Osaka, Japan

Kyushu Medical Center

🇯🇵

Fukuoka, Japan

Gifu University Hospital

🇯🇵

Gifu, Japan

Kagoshima City Hospital

🇯🇵

Kagoshima, Japan

Kobe City Medical Center General Hospital

🇯🇵

Kobe, Japan

Japanese Red Cross Kyoto Daini Hospital

🇯🇵

Kyoto, Japan

Iwate Prefectural Central Hospital

🇯🇵

Morioka, Japan

Niigata City General Hospital

🇯🇵

Niigata, Japan

KMU University Hospital

🇯🇵

Osaka, Japan

NHO Osaka National Hospital

🇯🇵

Osaka, Japan

Nakamura Memorial Hospital

🇯🇵

Sapporo, Japan

Jichi Medical University Hospital

🇯🇵

Shimotsuke, Japan

Kyorin University Hospital

🇯🇵

Tokyo, Japan

Toranomon Hospital

🇯🇵

Tokyo, Japan

Hospital Universitari Germans Trias i Pujol

🇪🇸

Badalona, Barcelona, Spain

Vall d'Hebron University Hospital (VHUH)

🇪🇸

Horta, Barcelona, Spain

Bellvitge University Hospital,

🇪🇸

L'Hospitalet de Llobregat, Barcelona, Spain

Santa Creu and Sant Pau Hospital

🇪🇸

Barcelona, Catalonia, Spain

Girona University Hospital

🇪🇸

Girona, Catalonia, Spain

Arnau de Vilanova University Hospital

🇪🇸

Lleida, Catalonia, Spain

John Radcliffe Hospital

🇬🇧

Oxford, Oxfordshire, United Kingdom

Royal Stoke University Hospital

🇬🇧

Stoke-on-Trent, Staffordshire, United Kingdom

Royal Victoria Infirmary

🇬🇧

Newcastle upon Tyne, United Kingdom

Queens Medical Centre

🇬🇧

Nottingham, United Kingdom

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