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A Study of BBI608 in Adult Patients With Advanced, Refractory Hematologic Malignancies

Phase 1
Completed
Conditions
Hematologic Malignancy
Interventions
Registration Number
NCT02352558
Lead Sponsor
Sumitomo Pharma America, Inc.
Brief Summary

This is a multicenter, open label, Phase 1 dose-escalation study of BBI608 administered to patients with relapsed, refractory hematologic malignancies, including multiple myeloma, lymphoma, and others.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
15
Inclusion Criteria
  1. Signed written informed consent must be obtained and documented according to the International Conference on Harmonisation (ICH) and be in accordance with local regulatory requirements
  2. A histologically confirmed hematologic malignancy that is advanced, relapsed, or refractory to standard, currently available anti-cancer treatment options
  3. ≥ 18 years of age
  4. Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 1 at dose escalation phase and of ≤ 2 at dose expansion phase
  5. Male or female patients of child-producing potential must agree to use contraception or avoidance of pregnancy measures during the study and for 30 days after their last dose
  6. Females of childbearing potential must have a negative serum pregnancy test
  7. Aspartate transaminase (AST) ≤ 2.5 x upper limit of normal (ULN) and alanine transaminase (ALT) ≤ 2.5 × upper limit of normal (ULN). Patients whose disease involves the liver and who have laboratory values of AST ≤ 3.5 ULN, AST ≤ 3.5 ULN, and albumin ≥ 35g/L may be enrolled if agreed upon by the Principal Investigator and Medical Monitor for the Sponsor
  8. Total bilirubin < 1.5 x ULN, except for cases in which elevation of total bilirubin is due to elevated levels of unconjugated bilirubin consistent with a diagnosis of Gilbert's Syndrome
  9. Life expectancy ≥ 3 months
Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm 1BBI608Patients with multiple myeloma treated with BBI608
Arm 5BBI608Patients with multiple myeloma treated with BBI608 and dexamethasone
Arm 9BBI608Patients with chronic lymphocytic leukemia treated with BBI608 and ibrutinib
Arm 2BBI608Patients with lymphoma treated with BBI608
Arm 3BBI608Patients with acute myeloid leukemia or myelo-dysplastic syndrome treated with BBI608
Arm 4BBI608Patients with chronic myeloid leukemia treated with BBI608
Arm 6BBI608Patients with multiple myeloma treated with BBI608 and bortezomib
Arm 7BBI608Patients with chronic myeloid leukemia treated with BBI608 and imatinib
Arm 8BBI608Patients with chronic lymphocytic leukemia treated with BBI608
Arm 5DexamethasonePatients with multiple myeloma treated with BBI608 and dexamethasone
Arm 6BortezomibPatients with multiple myeloma treated with BBI608 and bortezomib
Arm 7ImatinibPatients with chronic myeloid leukemia treated with BBI608 and imatinib
Arm 9IbrutinibPatients with chronic lymphocytic leukemia treated with BBI608 and ibrutinib
Primary Outcome Measures
NameTimeMethod
Determination of the safety and tolerability of BBI608 administered as monotherapy and in combination with dexamethasone, bortezomib, imatinib or ibrutinib by assessing dose-limiting toxicities (DLTs)4 weeks
Secondary Outcome Measures
NameTimeMethod
Pharmacokinetic profile of BBI608 when administered in monotherapy and in combination with dexamethasone, bortezomib, imatinib or ibrutinib as assessed by maximum plasma concentration and area under the curve-5min, 0, 0.25, 0.5, 1, 1.5, 2, 3, 4, 5, 8, 11, 12 hours on day 1, cycles 1 and 2
Pharmacodynamic activity of BBI608 when administered in monotherapy and in combination with dexamethasone, bortezomib, imatinib or ibrutinib as assessed by biomarker analysis20 weeks

Histopathology and Cancer Stem Cell assays will be performed to provide information of the biomarkers on patient blood samples collected on-study, as well as on (if available) bone marrow, other biopsied patient tumor tissue, and archival samples.

Assessment of the preliminary anti-tumor activity by performing tumor assessments20 weeks

Trial Locations

Locations (8)

Virginia Oncology Associates

🇺🇸

Norfolk, Virginia, United States

West Clinic

🇺🇸

Germantown, Tennessee, United States

Northwest Cancer Specialists, PC

🇺🇸

Vancouver, Washington, United States

Rocky Mountain Cancer Centers

🇺🇸

Denver, Colorado, United States

Indiana University

🇺🇸

Indianapolis, Indiana, United States

Cancer Care Centers of South Texas

🇺🇸

San Antonio, Texas, United States

Cancer Care Centers of South Texas - HOAST

🇺🇸

San Antonio, Texas, United States

Virginia Cancer Specialists, P.C.

🇺🇸

Fairfax, Virginia, United States

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