MedPath

Extension Study of Iron Chelation Therapy With Deferasirox in Patients With Transfusional Iron Overload

Phase 2
Completed
Conditions
Transfusional Iron Overload
Interventions
Registration Number
NCT00379483
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

A 1-year randomized Phase IIa core trial followed by a prolongation of 5 to 9 months was conducted to investigate the efficacy and safety of deferasirox in patients aged ≥ 18 years with transfusion-dependent iron overload.

The objective of this extension study is to assess the long-term safety of deferasirox and to provide treatment in patients with transfusional iron overload.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
66
Inclusion Criteria
  • Patients with transfusional iron overload who have successfully completed the one year chelation treatment in the deferasirox trial or the food-effect sub-study and who were considered by the investigator eligible to continue chelation therapy with deferasirox
Read More
Exclusion Criteria
  • Pregnant or breast feeding patients
  • Patients being considered by the investigator potentially unreliable and/or a history of non-compliance
Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Arm 1Deferasirox-
Primary Outcome Measures
NameTimeMethod
Long-term safety and tolerability of ICL670, at 3, 4, and 5 years treatmentat 3, 4, 5 years
Secondary Outcome Measures
NameTimeMethod
Change in liver iron content measured by SQUID, at 3, 4, and 5 yearsat 3, 4, 5 years

Trial Locations

Locations (1)

Novartis Investigative Site

🇮🇹

Torino, Italy

© Copyright 2025. All Rights Reserved by MedPath