MedPath

Taste Evaluation of Different Liquid Formulations With Eliglustat

Phase 1
Completed
Conditions
Gaucher Disease
Interventions
Registration Number
NCT02422654
Lead Sponsor
Genzyme, a Sanofi Company
Brief Summary

Primary Objective:

The purpose of this study is to assess the palatability of eliglustat prototype liquid formulations in healthy subjects.

Detailed Description

The total duration of the study for each subject will be approximately 5 weeks (screening period from Day -28 to Day -2, treatment period of 3 days, and follow-up call on Day 5).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
8
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
Concentration 2 eliglustat in vehicle BeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 2 eliglustat in vehicle EeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 1 eliglustat in vehicle AeliglustatSingle dose of 5 mL solution held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 1 eliglustat in vehicle BeliglustatSingle dose of 5 mL solution held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 1 eliglustat in vehicle CeliglustatSingle dose of 5 mL solution held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 1 eliglustat in vehicle DeliglustatSingle dose of 5 mL solution held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 1 eliglustat in vehicle EeliglustatSingle dose of 5 mL solution held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 2 eliglustat in vehicle AeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 2 eliglustat in vehicle CeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 2 eliglustat in vehicle DeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 3 eliglustat in vehicle AeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 3 eliglustat in vehicle DeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 3 eliglustat in vehicle CeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 3 eliglustat in vehicle BeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Concentration 3 eliglustat in vehicle EeliglustatSingle dose of 5 mL liquid formulation held in the mouth for 15 seconds with swishing but with no ingestion
Primary Outcome Measures
NameTimeMethod
Measurement of palatability by 100 mm visual analogue scale (VAS) for overall acceptabilityEach day for 3 days 30 minutes post expectorating the sample
Secondary Outcome Measures
NameTimeMethod
Subject's taste preference questionnaire from most preferred to least preferred of the 5 different liquid formulationsup to 3 days

Trial Locations

Locations (1)

Investigational Site Number 840001

🇺🇸

Evansville, Indiana, United States

Investigational Site Number 840001
🇺🇸Evansville, Indiana, United States

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