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Sub-optimal Response to Anti-Tumor Necrosis Factor's in Inflammatory Bowel Disease in Emerging Markets

Completed
Conditions
Crohn Disease
Colitis, Ulcerative
Inflammatory Bowel Diseases
Interventions
Drug: Anti-TNF Therapy
Registration Number
NCT03090139
Lead Sponsor
Takeda
Brief Summary

The purpose of this study is to establish the incidence of sub-optimal response to anti-TNF therapy in UC and CD participants.

Detailed Description

Participants with historical diagnosis of CD and UC who were naïve to anti-TNF therapy were observed in this retrospective study. The study will look to identify the local barriers in prescribing anti-TNF therapy, treatment patterns and indicators of sub-optimal response to anti-TNF therapy in UC and CD participants in real-world clinical practice in the EM countries, along with the associated incidence of sub-optimal response and impact on health care resource utilization (HCRU). The will enroll approximately 2000 participants.

The study consists of two periods, eligibility period followed by a data abstraction period. During the eligibility period participants who had initiated first anti-TNF therapy during 01 March 2010 up to 01 March 2015 will be recruited and observed. Participants will be followed up for a period of minimum 2 years (other than death) and a maximum of 5 years from the date of first treatment of anti-TNF therapy for CD and UC (Index date). During the data abstraction period participants who have eligible medical charts will be identified and all retrospective data will be collected.

This multi-center trial will be conducted in Argentina, China, Colombia, Mexico, Russia, Saudi Arabia, Singapore, South Korea, Taiwan and Turkey. The overall time to abstract data during the data extraction period from the web-based electronic data capture (EDC) system will be approximately 1 year from March 2017 to February 2018.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
1731
Inclusion Criteria
  1. Who are 18 years or older at Index Date and diagnosed with UC or CD.
  2. Who were naive to anti-TNF therapy and received their first dose of any anti-TNF therapy (index date) for UC or CD within the Eligibility Period from 01 March 2010 through 01 March 2015.
Exclusion Criteria
  1. Diagnosed with indeterminate/unspecified type of IBD.
  2. Were part of an IBD-related clinical trial during the observational period should be excluded (that is, index date up to the date of chart abstraction).
  3. Who received an anti-TNF therapy for any non-UC or non-CD conditions (example, rheumatoid arthritis, ankylosing spondylitis, psoriasis, or cancer).
  4. Who received an anti-TNF/biologic therapy at any point that was administered outside of the labelled dosing regimen (example, episodic use of anti-TNF therapy).
  5. With UC who had a total colectomy prior to their first anti-TNF therapy.
  6. Charts not available.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
All ParticipantsAnti-TNF TherapyAll participants with diagnosis of UC and CD, who initiated treatment with anti-TNF therapy from 01 March 2010 up to 01 March 2015 will be observed. Retrospective data extraction will be done for eligible participants from March 2017 up to approximately February 2018.
Primary Outcome Measures
NameTimeMethod
Number of Participants With Each Type of Anti-TNF Therapy5 years
Number of Participants With Response to Treatment5 years

Number of participants with response to treatment will be assessed.

Treatment Pattern Results Stratified by Anti-TNF Response Group and by UC or CD Diagnosis5 years

Treatment patterns results were as per the Anti-TNF therapy response from UC and CD participants.

Time-to-switch5 years

The time to switch at which the participant switched to another anti-TNF therapy will be evaluated.

Time-to-first Indicator of Sub-optimal Therapy5 years

Time-to-first indicator of sub-optimal therapy was defined as the occurrence of dose escalation, therapy augmentation, therapy switch, therapy discontinuation, hospitalization, or surgery of participant, which ever occurred first.

Treatment Patterns in UC and CD Participants5 years
Duration of Treatment5 years
Incidence Rate of Sub-optimal Response in UC and CD Participants5 years

Incidence rate will be calculated as the number of events divided by the total person time at risk, for participants under anti-TNF therapy.

Secondary Outcome Measures
NameTimeMethod
Number of Participants With UC Achieving Clinical Response Based on Mayo ScoresBaseline up to 5 years

Clinical response is defined as a decrease in the partial Mayo Score of at least 2 points and \>=25% from baseline, with an accompanying decrease in rectal bleeding subscore of \>=1 point from baseline or absolute rectal bleeding subscore of less than or equal to (\<=) 1 point. Mayo score is an instrument designed to measure disease activity of UC. It consists of 3 subscores: stool frequency, rectal bleeding, and physician global assessment of disease severity, each graded from 0 to 3 with higher scores indicating more severe disease. These scores are summed to give a total score range of 0 to 9; where higher scores indicating more severe disease.

Number of Participants with Predictors of Sub-optimal Therapy in UC or CD ParticipantsBaseline up to 5 years

The predictors of sub-optimal response will be assessed through multivariate analysis using logistic regression or other appropriate statistical methods. Multivariate analyses may be conducted to derive predictors of sub-optimal response to anti-TNF therapy globally and individually.

Number of Participants With CD Achieving Clinical Response Based on Harvey Bradshaw Index (HBI)Baseline up to 5 years

Clinical response is defined as a decrease in HBI score of greater than or equal to (\>=) 3 points from baseline. HBI score is used to measure the disease activity of CD. It consists of clinical parameters: abdominal pain (0-3, higher score means more severe pain), number of liquid stools per day, abdominal mass (0-3, where higher score means presence of swelling in the abdomen), and complications (score 1 per item). Total score is the sum of individual parameters. The score ranges from a minimum score of 0 to no pre-specified maximum score as it depends on the number of liquid stools, where higher scores indicating more severe disease.

Number of Participants with Inflammatory Bowel Disease (IBD) Related Surgeries and Hospitalisation2 years prior to index anti-TNF therapy

IBD-related surgeries and hospitalisation will be conducted in the two years prior to index anti-TNF therapy in UC or CD participants.

Number of Participants with Co-morbiditiesBaseline
Health Care Resources Utilisation (HCRU)Baseline up to 7 years

HCRU will be calculated for physician clinic visits, emergency department visits, IBD-related surgeries, invasive procedures, imaging, and in-participant admissions related to UC or CD, or related complications as available in the medical record and captured in the electronic case report form (eCRF).

Physician Survey QuestionnaireBaseline

The physician survey questionnaire will include questions on local accessibility to infusion centres, potential restrictions of prescription, potential local difficulties for drug access (example, reimbursement process, economic burden), and other reasons for participants compliant with the local label to not receive anti-TNF therapy.

Trial Locations

Locations (76)

Hospital Italiano

🇦🇷

Ciudad Autonoma Buenos Aires, Buenos Aires, Argentina

Hospital Italiano de La Plata

🇦🇷

La Plata, Buenos Aires, Argentina

Hospital Aleman

🇦🇷

Ciudad Autonoma Buenos Aires, Argentina

Hospital Britanico de Buenos Aires

🇦🇷

Ciudad Autonoma Buenos Aires, Argentina

Hospital Privado Centro Medico de Cordoba

🇦🇷

Cordoba, Argentina

Peking Union Medical College Hospital

🇨🇳

Beijing, Beijing, China

The Sixth Affiliated Hospital of Sun Yat-Sen University

🇨🇳

Guangzhou, Guangdong, China

The Affiliated Drum Tower Hospital of Nanjing University

🇨🇳

Nanjing, Jiangsu, China

First Affiliated Hospital of Dalian Medical University

🇨🇳

Dalian, Liaoning, China

Ruijin Hospital, Shanghai Jiaotong Uni. School of Med.

🇨🇳

Huangpu, Shanghai, China

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Hospital Italiano
🇦🇷Ciudad Autonoma Buenos Aires, Buenos Aires, Argentina

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