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ong-term, prospective study evaluating clinical and molecular biomarkers of epileptogenesis in a genetic model of epilepsy - Tuberous Sclerosis Complex.

Completed
Conditions
Epilepsy
Tuberous Sclerosis Complex
10039911
Registration Number
NL-OMON41140
Lead Sponsor
Instytut Pomnik-Centrum Zdrowia Dziecka (IPCZD)/ The Children's Memorial Health Institute
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
10
Inclusion Criteria

- Male or female infants with a definite diagnosis of TSC (Roach criteria; Roach 1998, or DNA confirmed);
- Age up to 4 months at the moment of enrolment;
- No clinical seizures seen by caregivers or on baseline videoEEG recording;
- Written informed consent of caregivers. It is possible to give consent for the observational part of the study only. In this case, the child will not enter the RCT.

Exclusion Criteria

- Any type of seizures observed till baseline visit;
- Antiepileptic treatment at or prior to study entry;
- Contraindications to MRI;
- Any severe and/or uncontrolled medical condition that is considered by the investigator as possibly affecting the EPISTOP analyses or procedures. For example non TSC related malformation of brain development or acquired brain damage.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>The primary parameter is the assessment of (a set of) molecular and clinical<br /><br>biomarkers in full analysis set of patients. </p><br>
Secondary Outcome Measures
NameTimeMethod
<p>Key secondary parameter is the efficacy and safety of preventative<br /><br>antiepileptic treatment in patients diagnosed with epilepsy after epileptiform<br /><br>discharges (group A) in comparison to patients diagnosed with epilepsy after<br /><br>the onset of clinical seizures (including both patients in group B as well as<br /><br>patients who presented with clinical seizures after inclusion but before EEG<br /><br>abnormalities were seen). The parameters of efficacy assessment include: the<br /><br>distribution of seizure free patients, proportion of patients with drug<br /><br>resistant seizures, proportion of patients with normalized EEG, the<br /><br>neurodevelopmental outcome recognized as the results in a battery of<br /><br>neuropsychologiscal tests performed at the age of 24 months. </p><br>
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