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Autosomal Dominant Retinitis Pigmentosa: Prevalence of Known Genes Identification of New Loci / Genes

Not Applicable
Completed
Conditions
Autosomal Dominant Retinitis Pigmentosa
Interventions
Genetic: genetic analysis
Registration Number
NCT01235624
Lead Sponsor
University Hospital, Montpellier
Brief Summary

Identify new genes responsible for autosomal dominant retinitis pigmentosa (ADRP), one of the most common causes of hereditary diseases of the retina, and thus better understand the mechanisms involved of the disease."

Detailed Description

Two hundred and fifty samples from unrelated patients, from which 150 were provided by the national reference center of rare disease in Montpellier and 100 recruited in the 9 participating centers over a period of two years."To identify the missing genes, we proceed in two steps. A first step in selecting families negative for the 8 major genes genes, by systematic sequencing of exons most frequently involved. A second step in finding new loci / genes by locus exclusion using microsatellite markers and SNP genotyping.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
1161
Inclusion Criteria
  • retinitis pigmentosa diagnosed
  • Autosomal dominant transmission diagnosed
  • Aged from 5 to 80 years
  • Informed consent
  • Affiliated or benefit from an insurance regimen
Exclusion Criteria

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
patientgenetic analysisPatient suffering of adRP that accept to participate at this study have a blood prelevement for genetic analysis (intervention)
Primary Outcome Measures
NameTimeMethod
identification of unknown loci and genes responsible of Autosomal dominant retinitis pigmentosa (adRP)for 5 years
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

CHRU Montpellier

🇫🇷

Montpellier, France

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