MedPath

Study to Assess the Efficacy & Safety of KHK4951 in Patients With Diabetic Macular Edema

Phase 2
Recruiting
Conditions
Diabetic Macular Edema (DME)
Interventions
Registration Number
NCT06116916
Lead Sponsor
Kyowa Kirin Co., Ltd.
Brief Summary

The purpose of this study is to evaluate efficacy and safety of KHK4951 eye drops in patients with DME.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
150
Inclusion Criteria
  • Voluntary written informed consent to participate in the study
  • In Korea, participants must be 19 years or older to be enrolled
  • BCVA ETDRS letter score of 78 letters to 35 letters as measured by the ETDRS visual acuity chart in the study eye at screening
  • 500 μm ≥ CST ≥ 325 μm in the study eye at screening
  • HbA1c ≤ 11% at screening
Exclusion Criteria
  • Any signs of proliferative diabetic retinopathy in the study eye

  • History of rubeosis in the study eye

  • Uncontrolled glaucoma in the study eye

  • Aphakia or pseudophakia with AC-IOL in the study eye

  • Active intraocular inflammation in the study eye

  • Any current ocular condition for which visual acuity loss would not improve from resolution of macular edema in the study eye

  • History of rhegmatogenous retinal detachment in the study eye

  • Any current or history of ocular disease other than DME that may confound assessment of the macula or affect central vision in the study eye

  • History of the following therapies in the study eye

    • History of vitrectomy surgery, submacular surgery, or other surgical intervention for DME
    • Periocular or intraocular (sub-Tenon or IVT) corticosteroids within 12 weeks prior to Day 1 corticosteroids
    • Previous intraocular device implantation except PC-IOL
    • Laser (any type) to the macular area within 12 weeks prior to Day 1
    • Peripheral retinal photocoagulation therapy within 12 weeks prior to Day 1
    • Previous treatment with IVT anti-VEGF drugs other than ranibizumab, bevacizumab, aflibercept 2 mg, and their biosimilars
    • Treatment with ranibizumab, bevacizumab, aflibercept 2 mg, or their biosimilars within 12 weeks prior to Day 1. Previously treated patients who received these medications more than 12 weeks prior to Day 1 can be enrolled, but the patients should be diagnosed with nAMD within 3 years prior to Day 1
    • Previous use of Ozurdex® or Iluvien® implant
  • Any current or history of endophthalmitis in either eye

  • History of idiopathic or autoimmune-associated uveitis in either eye

  • Active infectious conjunctivitis, keratitis, scleritis, or endophthalmitis in either eye

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm BKHK4951KHK4951 Middle dose
Arm BAflibercept InjectionKHK4951 Middle dose
Arm CKHK4951KHK4951 Low dose
Arm CAflibercept InjectionKHK4951 Low dose
Arm AAflibercept InjectionKHK4951 High dose
Arm AKHK4951KHK4951 High dose
Primary Outcome Measures
NameTimeMethod
Reduction of 15 or more letters in BCVA (Best corrected visual acuity) as measured by ETDRS visual acuity chart from baselineFor 36 weeks until the end of the trial
Secondary Outcome Measures
NameTimeMethod
The number of aflibercept IVTFor 36 weeks until the end of the trial
Change from baseline in leakage as measured by FA36 Weeks
Change from baseline in SHRM as measured by SD-OCT36 Weeks
Change from baseline in retinal morphology as measured by SD-OCT36 Weeks

Trial Locations

Locations (174)

Barnet Dulaney Perkins Eye Center - Phoenix

🇺🇸

Mesa, Arizona, United States

Retina Associates Southwest, P.C.

🇺🇸

Tucson, Arizona, United States

Win Retina

🇺🇸

Arcadia, California, United States

Retina Vitreous Associates Medical Group

🇺🇸

Beverly Hills, California, United States

The Retina Partners

🇺🇸

Encino, California, United States

Salehi Retina Institute, Inc

🇺🇸

Huntington Beach, California, United States

California Eye Specialists Medical Group Inc

🇺🇸

Pasadena, California, United States

Retina Consultants of Southern California

🇺🇸

Redlands, California, United States

Retina Consultants of Southern CO

🇺🇸

Colorado Springs, Colorado, United States

Blue Ocean Clinical Research West

🇺🇸

Clearwater, Florida, United States

Florida Eye Associates

🇺🇸

Melbourne, Florida, United States

Eye Associates of Pinellas

🇺🇸

Pinellas Park, Florida, United States

Ft. Lauderdale Eye Institute

🇺🇸

Plantation, Florida, United States

Retina Vitreous Associates of Florida - Saint Petersburg

🇺🇸

Saint Petersburg, Florida, United States

Southern Vitreoretinal Associates

🇺🇸

Tallahassee, Florida, United States

Center for Retina and Macular Disease - Ophthalmology

🇺🇸

Winter Haven, Florida, United States

Mid Atlantic Retina Specialists - Hagerstown

🇺🇸

Hagerstown, Maryland, United States

Sierra Eye Associates

🇺🇸

Reno, Nevada, United States

Envision Ocular, LLC

🇺🇸

Bloomfield, New Jersey, United States

Vision Research Center Eye Associates of New Mexico

🇺🇸

Albuquerque, New Mexico, United States

Retina Vitreous Surgeons of Central NY, PC

🇺🇸

Liverpool, New York, United States

Ophthalmic Consultants of Long Island

🇺🇸

Oceanside, New York, United States

Retina Vitreous Center in Edmond Oklahoma

🇺🇸

Edmond, Oklahoma, United States

EyeHealth Northwest

🇺🇸

Portland, Oregon, United States

Wills Eye Health System

🇺🇸

Bethlehem, Pennsylvania, United States

Eye Care Specialists

🇺🇸

Kingston, Pennsylvania, United States

Retina Consultants of Charleston - (RCA Network Site)

🇺🇸

Charleston, South Carolina, United States

Charleston Neuroscience Institute (RCA Network Site)

🇺🇸

Ladson, South Carolina, United States

Black Hills Regional Eye Institute - Ophthalmology

🇺🇸

Rapid City, South Dakota, United States

Charles Retina Institute

🇺🇸

Germantown, Tennessee, United States

Retina Research Institute of Texas

🇺🇸

Abilene, Texas, United States

Austin Retina Associates - Ophthalmology/Retina (RCA Network site)

🇺🇸

Austin, Texas, United States

Austin Clinical Research, LLC

🇺🇸

Austin, Texas, United States

Retina Consultants of Texas

🇺🇸

Bellaire, Texas, United States

Texas Retina Associates

🇺🇸

Fort Worth, Texas, United States

Retinal Consultants of Texas- San Antonio (RCA Network site)

🇺🇸

San Antonio, Texas, United States

Retina Consultants of Texas (RCA Network Site)

🇺🇸

The Woodlands, Texas, United States

Strategic Clinical Research Group, LLC

🇺🇸

Willow Park, Texas, United States

University of Vermont Fletcher Allen Health Care

🇺🇸

Burlington, Vermont, United States

Retina Group of Washington

🇺🇸

Fairfax, Virginia, United States

Eye Clinic Albury Wodonga

🇦🇺

Albury, New South Wales, Australia

South West Retina

🇦🇺

Liverpool, New South Wales, Australia

Marsden Eye Specialists

🇦🇺

Parramatta, New South Wales, Australia

Strathfield Retina Clinic

🇦🇺

Strathfield, New South Wales, Australia

Sydney Eye Hospital

🇦🇺

Sydney, New South Wales, Australia

Sydney Retina Clinic & Day Surgery

🇦🇺

Sydney, New South Wales, Australia

Adelaide Eye and Retina Centre

🇦🇺

Adelaide, South Australia, Australia

Hobart Eye Surgeons

🇦🇺

Hobart, Tasmania, Australia

Centre for Eye Research Australia

🇦🇺

East Melbourne, Victoria, Australia

MIYAKE Eye Hospital

🇯🇵

Nagoya-shi, Aiti-ken, Japan

Aichi Medical University Hospital - Ophthalmology

🇯🇵

Nagakute, Aiti, Japan

Toho University Medical Center Sakura Hospital

🇯🇵

Sakura, Chiba, Japan

Kurume University Hospital

🇯🇵

Kurume, Fukuoka, Japan

Minamitohoku Eye Clinic

🇯🇵

Koriyama, Fukushima, Japan

Caress Sapporo Tokeidai Memorial Hospital

🇯🇵

Sapporo, Hokkaidô, Japan

Kobe University Hospital - Ophthalmology

🇯🇵

Kobe, Hyôgo, Japan

Kozawa Eye Hospital and Diabetes Center

🇯🇵

Mito, Ibaraki, Japan

Kagawa University Hospital

🇯🇵

Kita-gun, Kagawa, Japan

Shinshu University Hospital - Ophthalmology

🇯🇵

Matsumoto, Nagano, Japan

Nara Medical University Hospital - Ophthalmology

🇯🇵

Kashihara, Nara, Japan

Kansai Medical University Medical Center

🇯🇵

Hirakata, Osaka, Japan

Kindai University Hospital

🇯🇵

Osakasayama-shi, Osaka, Japan

Muramatsu Clinic Muramatsu Eye Clinic - Ophthalmology

🇯🇵

Susono, Shizuoka, Japan

Jichi Medical University Hospital

🇯🇵

Shimotsuke, Tochigi, Japan

Nihon University Hospital

🇯🇵

Chiyoda, Tokyo, Japan

Tokyo Medical University Hachioji Medical Center

🇯🇵

Hachiōji, Tokyo, Japan

Tokyo Medical Center

🇯🇵

Meguro-ku, Tokyo, Japan

Keio University Hospital - Ophthalmology

🇯🇵

Shinjuku-Ku, Tokyo, Japan

Hayashi Eye Hospital - Ophthalmology

🇯🇵

Fukuoka, Japan

Fukushima Medical University Hospital - Ophthalmology

🇯🇵

Fukushima, Japan

Rakuwakai Otowa Hospital

🇯🇵

Kyoto, Japan

Saitama Red Cross Hospital

🇯🇵

Saitama, Japan

Osaka Metropolitan University Hospital

🇯🇵

Osaka, Ôsaka, Japan

Keimyung University Dongsan Hospital

🇰🇷

Daegu, Dalseo-gu, Korea, Republic of

Pusan National University Hospital

🇰🇷

Busan, Gudeok-ro, Korea, Republic of

Seoul National University Bundang Hospital

🇰🇷

Seongam, Gyeonggido, Korea, Republic of

CHA Bundang Medical Center, CHA University

🇰🇷

Seongnam-si, Gyeonggido, Korea, Republic of

Yeungnam University Hospital

🇰🇷

Daegu, Nam-gu, Korea, Republic of

Gachon University Gil Medical Center

🇰🇷

Incheon, Namdong-gu, Korea, Republic of

Korea University Anam Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Severance Hospital, Yonsei University Health System

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Kim Eye hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Kyung Hee University Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

The Catholic Univ of KOR, SSMH

🇰🇷

Seoul, Korea, Republic of

Barnet Dulaney Perkins Eye Center - Phoenix

🇺🇸

Mesa, Arizona, United States

Retina Associates Southwest, P.C.

🇺🇸

Tucson, Arizona, United States

Win Retina

🇺🇸

Arcadia, California, United States

Retina Vitreous Associates Medical Group

🇺🇸

Beverly Hills, California, United States

The Retina Partners

🇺🇸

Encino, California, United States

Salehi Retina Institute, Inc

🇺🇸

Huntington Beach, California, United States

California Eye Specialists Medical Group Inc

🇺🇸

Pasadena, California, United States

Retina Consultants of Southern California

🇺🇸

Redlands, California, United States

Retina Consultants of Southern CO

🇺🇸

Colorado Springs, Colorado, United States

Blue Ocean Clinical Research West

🇺🇸

Clearwater, Florida, United States

Florida Eye Associates

🇺🇸

Melbourne, Florida, United States

Eye Associates of Pinellas

🇺🇸

Pinellas Park, Florida, United States

Ft. Lauderdale Eye Institute

🇺🇸

Plantation, Florida, United States

Retina Vitreous Associates of Florida - Saint Petersburg

🇺🇸

Saint Petersburg, Florida, United States

Southern Vitreoretinal Associates

🇺🇸

Tallahassee, Florida, United States

Center for Retina and Macular Disease - Ophthalmology

🇺🇸

Winter Haven, Florida, United States

Mid Atlantic Retina Specialists - Hagerstown

🇺🇸

Hagerstown, Maryland, United States

Sierra Eye Associates

🇺🇸

Reno, Nevada, United States

Envision Ocular, LLC

🇺🇸

Bloomfield, New Jersey, United States

Vision Research Center Eye Associates of New Mexico

🇺🇸

Albuquerque, New Mexico, United States

Retina Vitreous Surgeons of Central NY, PC

🇺🇸

Liverpool, New York, United States

Ophthalmic Consultants of Long Island

🇺🇸

Oceanside, New York, United States

Retina Vitreous Center in Edmond Oklahoma

🇺🇸

Edmond, Oklahoma, United States

EyeHealth Northwest

🇺🇸

Portland, Oregon, United States

Wills Eye Health System

🇺🇸

Bethlehem, Pennsylvania, United States

Eye Care Specialists

🇺🇸

Kingston, Pennsylvania, United States

Retina Consultants of Charleston - (RCA Network Site)

🇺🇸

Charleston, South Carolina, United States

Charleston Neuroscience Institute (RCA Network Site)

🇺🇸

Ladson, South Carolina, United States

MIYAKE Eye Hospital

🇯🇵

Nagoya, Aichi, Japan

Black Hills Regional Eye Institute - Ophthalmology

🇺🇸

Rapid City, South Dakota, United States

Charles Retina Institute

🇺🇸

Germantown, Tennessee, United States

Retina Research Institute of Texas

🇺🇸

Abilene, Texas, United States

Austin Retina Associates - Ophthalmology/Retina (RCA Network site)

🇺🇸

Austin, Texas, United States

Austin Clinical Research, LLC

🇺🇸

Austin, Texas, United States

Retina Consultants of Texas

🇺🇸

Bellaire, Texas, United States

Texas Retina Associates

🇺🇸

Fort Worth, Texas, United States

Retinal Consultants of Texas- San Antonio (RCA Network site)

🇺🇸

San Antonio, Texas, United States

Retina Consultants of Texas (RCA Network Site)

🇺🇸

The Woodlands, Texas, United States

Strategic Clinical Research Group, LLC

🇺🇸

Willow Park, Texas, United States

University of Vermont Fletcher Allen Health Care

🇺🇸

Burlington, Vermont, United States

Retina Group of Washington

🇺🇸

Fairfax, Virginia, United States

Eye Clinic Albury Wodonga

🇦🇺

Albury, New South Wales, Australia

South West Retina

🇦🇺

Liverpool, New South Wales, Australia

Marsden Eye Specialists

🇦🇺

Parramatta, New South Wales, Australia

Strathfield Retina Clinic

🇦🇺

Strathfield, New South Wales, Australia

Sydney Eye Hospital

🇦🇺

Sydney, New South Wales, Australia

Sydney Retina Clinic & Day Surgery

🇦🇺

Sydney, New South Wales, Australia

Adelaide Eye and Retina Centre

🇦🇺

Adelaide, South Australia, Australia

Hobart Eye Surgeons

🇦🇺

Hobart, Tasmania, Australia

Centre for Eye Research Australia

🇦🇺

East Melbourne, Victoria, Australia

Aichi Medical University Hospital - Ophthalmology

🇯🇵

Nagakute, Aichi, Japan

Toho University Medical Center Sakura Hospital

🇯🇵

Sakura, Chiba, Japan

Kurume University Hospital

🇯🇵

Kurume, Fukuoka, Japan

Minamitohoku Eye Clinic

🇯🇵

Koriyama, Fukushima, Japan

Caress Sapporo Tokeidai Memorial Hospital

🇯🇵

Sapporo, Hokkaidô, Japan

Kobe University Hospital - Ophthalmology

🇯🇵

Kobe, Hyôgo, Japan

Kozawa Eye Hospital and Diabetes Center

🇯🇵

Mito, Ibaraki, Japan

Kagawa University Hospital

🇯🇵

Kita-gun, Kagawa, Japan

Shinshu University Hospital - Ophthalmology

🇯🇵

Matsumoto, Nagano, Japan

Nara Medical University Hospital - Ophthalmology

🇯🇵

Kashihara, Nara, Japan

Kansai Medical University Medical Center

🇯🇵

Hirakata, Osaka, Japan

Kindai University Hospital

🇯🇵

Osakasayama, Osaka, Japan

Muramatsu Clinic Muramatsu Eye Clinic - Ophthalmology

🇯🇵

Susono, Shizuoka, Japan

Jichi Medical University Hospital

🇯🇵

Shimotsuke, Tochigi, Japan

Nihon University Hospital

🇯🇵

Chiyoda, Tokyo, Japan

Tokyo Medical University Hachioji Medical Center

🇯🇵

Hachiōji, Tokyo, Japan

Tokyo Medical Center

🇯🇵

Meguro, Tokyo, Japan

Keio University Hospital - Ophthalmology

🇯🇵

Shinjuku, Tokyo, Japan

Hayashi Eye Hospital - Ophthalmology

🇯🇵

Fukuoka, Japan

Fukushima Medical University Hospital - Ophthalmology

🇯🇵

Fukushima, Japan

Rakuwakai Otowa Hospital

🇯🇵

Kyoto, Japan

Saitama Red Cross Hospital

🇯🇵

Saitama, Japan

Osaka Metropolitan University Hospital

🇯🇵

Osaka, Ôsaka, Japan

Keimyung University Dongsan Hospital

🇰🇷

Daegu, Dalseo-gu, Korea, Republic of

Pusan National University Hospital

🇰🇷

Busan, Gudeok-ro, Korea, Republic of

Seoul National University Bundang Hospital

🇰🇷

Seongam, Gyeonggido, Korea, Republic of

CHA Bundang Medical Center, CHA University

🇰🇷

Seongnam-si, Gyeonggido, Korea, Republic of

Yeungnam University Hospital

🇰🇷

Daegu, Nam-gu, Korea, Republic of

Gachon University Gil Medical Center

🇰🇷

Incheon, Namdong-gu, Korea, Republic of

Korea University Anam Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Severance Hospital, Yonsei University Health System

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Kim Eye hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

Kyung Hee University Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi, Korea, Republic of

The Catholic Univ of KOR, SSMH

🇰🇷

Seoul, Korea, Republic of

© Copyright 2025. All Rights Reserved by MedPath