MedPath

A Study of Brigatinib in Participants With Anaplastic Lymphoma Kinase-Positive (ALK+), Advanced Non-Small-Cell Lung Cancer (NSCLC) Progressed on Alectinib or Ceritinib

Phase 2
Completed
Conditions
ALK-positive Advanced NSCLC
Interventions
Registration Number
NCT03535740
Lead Sponsor
Ariad Pharmaceuticals
Brief Summary

The primary purpose of this study is to determine the efficacy of brigatinib by confirmed objective response rate (ORR) by response evaluation criteria in solid tumors (Response Evaluation Criteria in Solid Tumors \[RECIST\]), in participants with ALK+ locally advanced or metastatic NSCLC whose disease has progressed on therapy with alectinib or ceritinib.

Detailed Description

The drug being tested in this study is called brigatinib (AP26113). Brigatinib is being tested to treat people who have anaplastic lymphoma kinase-positive (ALK+), advanced non-small-cell lung cancer (NSCLC).

The study will enroll approximately 103 patients. Participants will be assigned to the treatment group:

• Brigatinib

All participants will be asked to take brigatinib 90 mg tablet in lead-in period for 7 days, followed by brigatinib 180 mg at the same time each day throughout the study. Participants with progressive disease had an option to receive an escalated dose of brigatinib 240 mg as per investigator's discretion in case no toxicities (greater than grade 2) are experienced.

This multicenter trial will be conducted worldwide. The overall time to participate in this study is approximately 3 years. Participants will make multiple visits to the clinic, and 30 days after last dose of study drug for a follow-up assessment.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
103
Inclusion Criteria
  1. Have histologically or cytologically confirmed stage IIIB (locally advanced or recurrent and not a participant for curative therapy) or stage IV non-small-cell lung cancer (NSCLC).

  2. Must meet both of the following 2 criteria:

    1. Have documentation of anaplastic lymphoma kinase (ALK) rearrangement by a positive result from any laboratory test® approved by the food and drug administration (FDA) or Have documented ALK rearrangement by a different test (non-FDA-approved local lab tests) and have provided tumor sample to the central laboratory. (Note: Central laboratory ALK rearrangement testing results are not required to be obtained before randomization.)
    2. Had been on any one of the ALK tyrosine kinase inhibitor (TKIs) (alectinib, ceritinib, crizotinib) for at least 12 weeks before progression.
  3. Had progressive disease (PD) while on alectinib or ceritinib

  4. Had alectinib or ceritinib as the most recent ALK inhibitor therapy.

  5. Have at least 1 measurable lesion per response evaluation criteria in solid tumors (RECIST) version 1.1 as assessed by the investigator.

  6. Had recovered from toxicities related to prior anticancer therapy to national cancer institute common terminology criteria for adverse events (NCI CTCAE), version 4.03, Grade <=1. (Note: Treatment-related alopecia or peripheral neuropathy that are Grade >1 are allowed if deemed irreversible.) and have adequate major organ functions.

  7. Have a life expectancy of ≥3 months.

Exclusion Criteria
  1. Had received any prior ALK-targeted TKI other than crizotinib, alectinib, or ceritinib.
  2. Had received both alectinib and ceritinib.
  3. Had previously received more than 3 regimens of systemic anticancer therapy for locally advanced or metastatic disease.
  4. Had symptomatic brain metastasis (parenchymal or leptomeningeal). Participants with asymptomatic brain metastasis or who have stable symptoms that did not require an increased dose of corticosteroids to control symptoms in the past 7 days before the first dose of brigatinib may be enrolled.
  5. Had current spinal cord compression (symptomatic or asymptomatic and detected by radiographic imaging). Participants with leptomeningeal disease and without cord compression are allowed.
  6. Had a cerebrovascular accident or transient ischemic attack within 6 months before first dose of brigatinib.
  7. Had an ongoing or active infection, including, but not limited to, the requirement for intravenous antibiotics.
  8. Had malabsorption syndrome or other gastrointestinal (GI) illness that could affect oral absorption of brigatinib.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Brigatinib 90 mg/180 mg with Optional Dose Escalation to 240 mgBrigatinibBrigatinib 90 mg, tablets, orally, once daily for 7 days, followed by Brigatinib 180 mg, tablets, orally, once daily for until objective disease progression per Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1, as assessed by the investigator, or intolerable toxicity. Participants who experienced progression on the 180 mg dose and had not experienced toxicities greater than Grade 2 had the option to receive brigatinib 240 mg QD based on investigator's discretion, up to 20 months until data cut-off: 30 September 2020. Participants who experienced progression on any doses but judged as still benefiting from the study treatment by the investigator may continue to use the current dose, up to study end.
Primary Outcome Measures
NameTimeMethod
Confirmed Objective Response Rate (ORR) Using RECIST v1.1 as Assessed by the Independent Review Committee (IRC)Up to approximately 20 months from the start of enrollment till data cut-off 30 September 2020

Confirmed ORR is defined as the percentage of the participants who are confirmed to have achieved complete response (CR) or partial response (PR), per RECIST version 1.1 (confirmed ≥4 weeks after initial response), after the initiation of study treatment. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis and PR: at least a 30% decrease in the sum of the longest diameters (SLD) of target lesions taking as reference the Baseline sum diameters.

Secondary Outcome Measures
NameTimeMethod
Confirmed ORR Using RECIST v1.1 as Assessed by the InvestigatorUntil the radiological disease progression or study end (approximately 3 years)

Confirmed ORR is defined as the percentage of the participants who are confirmed to have achieved CR or PR, per RECIST version 1.1 (confirmed ≥4 weeks after initial response), after the initiation of study treatment. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis and PR: at least a 30% decrease in the SLD of target lesions taking as reference the baseline sum diameters.

Progression-Free Survival (PFS) as Assessed by the Investigator and IRCUntil the radiological disease progression or study end (approximately 3 years)

PFS is defined as the time interval from the date of the first dose of the study treatment until the first date at which disease progression is objectively documented, or death due to any cause, whichever occurs first. PFS will be censored for participants without documented disease progression or death.

Disease Control Rate (DCR) as Assessed by the Investigator and IRCUntil the radiological disease progression or study end (approximately 3 years)

DCR is defined as the percentage of participants who have achieved CR, PR or stable disease (SD) (in the case of SD, measurements must have met the SD criteria at least once after study entry at a minimum interval of 6 weeks) after the initiation of study treatment. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis. PR: at least a 30% decrease in the SLD of target lesions taking as reference the baseline sum diameters. SD: Neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD.

Duration of Response (DOR) as Assessed by the Investigator and IRCUntil the radiological disease progression or study end (approximately 3 years)

DOR is defined as the time interval from the time that the measurement criteria are first met for CR or PR until the first date that the progressive disease (PD) is objectively documented, or death. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis. PR: at least a 30% decrease in the SLD of target lesions taking as reference the Baseline sum diameters. PD: SLD increased by at least 20% from the smallest value on study (including Baseline, if that is the smallest). SLD must also demonstrate an absolute increase of at least 5 mm (2 lesions increasing from, for example, 2 mm to 3 mm, does not qualify).

Time to Response as Assessed by the Investigator and IRCUntil the radiological disease progression or study end (approximately 3 years)

Time to response is defined as the time interval from the date of the first dose of the study treatment until the initial observation of CR or PR. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis. PR: at least a 30% decrease in the SLD of target lesions taking as reference the baseline sum diameters.

Confirmed Intracranial Objective Response Rate (iORR) in Participants With Brain Metastases at Baseline, as Assessed by the IRCUntil the radiological disease progression or study end (approximately 3 years)

Confirmed iORR is defined as the proportion of the participants who have achieved CR or PR in the brain per a modification of RECIST version 1.1, after the initiation of study treatment, in participants with intracranial brain metastases at baseline. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis. or partial response or PR: at least a 30% decrease in the SLD of target lesions taking as reference the baseline sum diameters.

Duration of Intracranial Response in Participants With Brain Metastases at Baseline, as Assessed by the IRCUntil the radiological disease progression or study end (approximately 3 years)

Duration of intracranial response is defined as the time interval from the time that the measurement criteria are first met for CR or PR until the first date that PD (including baseline, if that is the smallest). SLD must also demonstrate an absolute increase of at least 5 mm. (2 lesions increasing from, for example, 2 mm to 3 mm, does not qualify) in the brain is objectively documented or death, in participants with intracranial metastases at baseline. CR: disappearance of all extranodal target lesions and all pathological lymph nodes must have decreased to \<10 mm in short axis. or partial response or PR: at least a 30% decrease in the SLD of target lesions taking as reference the baseline sum diameters in the brain. PD: SLD increased by at least 20% from the smallest value on study.

Intracranial Progression-Free Survival (iPFS) in Participants With Brain Metastases at Baseline, as Assessed by the IRCUntil the radiological disease progression or study end (approximately 3 years)

iPFS is defined as the time interval from the date of the first dose of the study treatment until the first date at which intracranial brain disease progression is objectively documented, or death due to any cause, whichever occurs first, in participants with intracranial metastases at enrollment. iPFS will be censored for participants without documented intracranial disease progression or death.

Overall Survival (OS)Until the radiological disease progression or study end (approximately 3 years)

OS is defined as the time interval from the date of the first dose of the study treatment until death due to any cause. It will be censored on the date of last contact for those participants who are alive.

Number of Participants With One or More Treatment-emergent Adverse Event (TEAE)First dose of study drug up to 30 days after last dose (approximately 3 years)

An adverse event (AE) means any untoward medical occurrence in a participant administered a pharmaceutical product; the untoward medical occurrence does not necessarily have a causal relationship with this treatment. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease temporally associated with the use of a medicinal (investigational) product whether or not it is related to the medicinal product. This includes any newly occurring event, or a previous condition that has increased in severity or frequency since the administration of study drug.

Health-Related Quality of Life (HRQOL) From European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire (EORTC QLQ-C30) ScoreFirst dose of study drug up to 30 days after last dose (approximately 3 years)

EORTC QLQ-C30 incorporates 5 functional scales (physical functioning, role functioning, emotional functioning, cognitive functioning, and social functioning), 1 global health status scale, 3 symptom scales (fatigue, nausea and vomiting, and pain), and 6 single items (dyspnea, insomnia, appetite loss, constipation, diarrhea, and financial difficulties). EORTC QLQ-C30 contains 28 questions (4-point scale where 1=Not at all \[best\] to 4=Very Much \[worst\]) and 2 questions (7-point scale where 1=Very poor \[worst\] to 7= Excellent \[best\]). Raw scores are converted into scale scores ranging from 0 to 100. For the functional scales and the global health status scale, higher scores represent better quality of life (QOL); for the symptom scales, lower scores represent better QOL.

HRQOL From EORTC QLQ- Lung Cancer (LC) 13First dose of study drug up to 30 days after last dose (approximately 3 years)

HRQOL scores will be assessed with EORTC, its lung cancer module QLQ-LC13. QLQ-LC13 contains 13 questions assessing lung cancer-associated symptoms (cough, hemoptysis, dyspnea, and site-specific pain), treatment-related side effects (sore mouth, dysphagia, peripheral neuropathy, and alopecia), and use of pain medication. Scale score range: 0 to 100. Higher symptom score = greater degree of symptom severity.

Trial Locations

Locations (79)

The First Affiliated Hospital of Guangzhou Medical University

🇨🇳

Guangzhou, Guangdong, China

Jilin Provincial Cancer Hospital (Changchun Cancer Hospital)

🇨🇳

Changchun, Jilin, China

Shanghai Pulmonary Hospital

🇨🇳

Shanghai, Shanghai, China

University of California Irvine Health Chao Family Comprehensive Cancer Center

🇺🇸

Orange, California, United States

The Oncology Institute of Hope and Innovation

🇺🇸

Whittier, California, United States

Peninsula & South Eastern Haematology and Oncology Group

🇦🇺

Frankston, Victoria, Australia

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

USOR - Rocky Mountain Cancer Centers - Pueblo

🇺🇸

Pueblo, Colorado, United States

Saint Vincent's Hospital Melbourne

🇦🇺

Fitzroy, Victoria, Australia

Klinikum Klagenfurt Am Worthersee

🇦🇹

Klagenfurt, Carinthia, Austria

Levine Cancer Institute - Southpark

🇺🇸

Charlotte, North Carolina, United States

Sarah Cannon Research Institute

🇺🇸

Nashville, Tennessee, United States

Evangelisches Krankenhaus Hamm

🇩🇪

Hamm, Nordrhein-westfalen, Germany

Queen Elizabeth Hospital

🇭🇰

Kowloon, Hong Kong

Azienda Ospedaliero - Universitaria San Luigi Gonzaga

🇮🇹

Orbassano, Torino, Italy

Sir Charles Gairdner Hospital

🇦🇺

Nedlands, Western Australia, Australia

Chungbuk National University Hospital

🇰🇷

Cheongju-si, Gyeongsangbuk-do, Korea, Republic of

Centre de Lutte Contre le Cancer Centre Leon Berard

🇫🇷

Lyon, Rhone-alpes, France

Pius Hospital Oldenburg

🇩🇪

Oldenburg, Niedersachsen, Germany

Istituto Europeo di Oncologia

🇮🇹

Milano, Italy

Universitatsklinikum Ulm

🇩🇪

Ulm, Baden-wuerttemberg, Germany

Centre Hospitalier Intercommunal de Creteil

🇫🇷

Creteil, Ile-de-france, France

Hopital Larrey, CHU de Toulouse, Service de Pneumologie

🇫🇷

Toulouse Cedex 9, Midi-pyrenees, France

Thoraxklinik Heidelberg gGmbH

🇩🇪

Heidelberg, Baden-wuerttemberg, Germany

Queen Mary Hospital

🇭🇰

Hong Kong, Hong Kong

Ludwig-Maximilians-Universitat Munchen

🇩🇪

Munchen, Bayern, Germany

Gachon University Gil Medical Center

🇰🇷

Incheon, Gyeonggi-do, Korea, Republic of

Istituto Nazionale Tumori IRCCS Fondazione Pascale

🇮🇹

Napoli, Italy

Azienda USL della Romagna

🇮🇹

Ravenna, Italy

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Skanes Universitetssjukhus i Lund

🇸🇪

Lund, Skane, Sweden

Karolinska Universitetssjukhuset

🇸🇪

Stockholm, Sweden

Okayama University Hospital

🇯🇵

Okayama-city, Okayama, Japan

Hospital Universitario Ramon Y Cajal

🇪🇸

Madrid, Spain

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Fujita Health University Hospital

🇯🇵

Toyoake, Aichi, Japan

Korea University Anam Hospital

🇰🇷

Seoul, Gyeonggi-do, Korea, Republic of

Sendai Kousei Hospital

🇯🇵

Sendai, Miyagi, Japan

Kanagawa Cancer Center

🇯🇵

Yokohama, Kanagawa, Japan

Complejo Hospitalario Universitario A Coruna

🇪🇸

A Coruna, LA Coruna, Spain

Keimyung University Dongsan Medical Center

🇰🇷

Daegu, Korea, Republic of

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Uppsala Akademiska Sjukhus

🇸🇪

Uppsala, Sweden

Hospital Universitario Vall d'Hebron

🇪🇸

Barcelona, Spain

Providence Portland Medical Center

🇺🇸

Portland, Oregon, United States

Toronto University Health Network

🇨🇦

Toronto, Ontario, Canada

McGill University Health Centre

🇨🇦

Montreal, Quebec, Canada

National Cancer Center

🇰🇷

Goyang-si, Gyeonggi-do, Korea, Republic of

Severance Hospital

🇰🇷

Seoul, Korea, Republic of

USOR - Virginia Cancer Specialists - Fairfax Office

🇺🇸

Fairfax, Virginia, United States

Cross Cancer Institute

🇨🇦

Edmonton, Alberta, Canada

Beijing Cancer Hospital

🇨🇳

Beijing, Beijing, China

Hopital Haut-Leveque

🇫🇷

Pessac, Aquitaine, France

Zhejiang Cancer Hospital

🇨🇳

Hangzhou, Zhejiang, China

Assistance Publique-Hopitaux de Marseille Hopital Nord

🇫🇷

Marseille, Provence Alpes COTE D'azur, France

HELIOS Klinikum Emil von Behring

🇩🇪

Berlin, Germany

Azienda Ospedaliero Universitaria di Parma

🇮🇹

Parma, Italy

Azienda Ospedaliera San Camillo Forlanini

🇮🇹

Roma, Lazio, Italy

Centro di Riferimento Oncologico di Aviano

🇮🇹

Aviano, Pordenone, Italy

Kansai Medical University Hirakata Hospital

🇯🇵

Hirakata-shi, Osaka, Japan

The Cancer Institute Hospital of Japanese Foundation for Cancer Research

🇯🇵

Koto-ku, Tokyo, Japan

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Vrije Universiteit Medisch Centrum

🇳🇱

Amsterdam, Noord-holland, Netherlands

Institut Catala d'Oncologia Badalona - Hospital Germans Trias i Pujol

🇪🇸

Badalona, Barcelona, Spain

Erasmus University Medical Center

🇳🇱

Rotterdam, Zuid-holland, Netherlands

Hospital Universitario Puerta de Hierro - Majadahonda

🇪🇸

Madrid, Spain

Tom Baker Cancer Center

🇨🇦

Calgary, British Columbia, Canada

Changhua Christian Hospital

🇨🇳

Changhua City, Changhwa, Taiwan

Princess Margaret Hospital - Hong Kong

🇭🇰

Kowloon, Hong Kong

Klinikum Kempten-Oberallgau

🇩🇪

Kempten, Bavaria, Germany

Barbara Ann Karmanos Cancer Institute

🇺🇸

Detroit, Michigan, United States

Krankenhaus Elisabethinen Linz

🇦🇹

Linz, Upper Austria, Austria

National Cheng Kung University

🇨🇳

Tainan, Tainan CITY, Taiwan

China Medical University Hospital

🇨🇳

Taichung, Taiwan

Taichung Veterans General Hospital

🇨🇳

Taichung, Taiwan

Maastricht University Medical Centre

🇳🇱

Maastricht, Limburg, Netherlands

Florida Hospital Medical Group

🇺🇸

Orlando, Florida, United States

The First Affiliated Hospital of Zhejiang University School of Medicine

🇨🇳

Hangzhou, Zhejiang, China

Prince of Wales Hospital

🇭🇰

Shatin, New Territories, Hong Kong

© Copyright 2025. All Rights Reserved by MedPath