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Ledipasvir/Sofosbuvir Fixed-Dose Combination Plus Ribavirin in Participants With Chronic HCV With Advanced Liver Disease or Post-Liver Transplant

Phase 2
Completed
Conditions
Chronic HCV Infection
Interventions
Drug: LDV/SOF
Registration Number
NCT02010255
Lead Sponsor
Gilead Sciences
Brief Summary

This study will evaluate ledipasvir/sofosbuvir (LDV/SOF) fixed-dose combination (FDC) plus ribavirin (RBV) in participants with advanced liver disease or posttransplant and chronic genotype 1 or 4 hepatitis C virus (HCV) infection.

* Cohort A: decompensated cirrhosis (advanced liver disease), no prior liver transplant;

* Cohort B: post-liver transplant, with or without cirrhosis;

* Group assignment within cohorts is based on severity of liver impairment at screening (Child-Pugh-Turcotte (CPT) score for participants with cirrhosis; fibrosis; or presence of disease for fibrosing cholestatic hepatitis (FCH) groups)

* Randomization is 1:1 within groups to 12 or 24 weeks of LDV/SOF+RBV treatment.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
334
Inclusion Criteria
  • Able to provide written informed consent
  • Chronic genotype 1 and/or 4 HCV infection
  • Normal ECG
  • Negative serum pregnancy test for female subjects
  • Male subjects and female subjects of childbearing potential must agree to use contraception
  • Able to comply with the dosing instructions for study drug and able to complete the study schedule of assessments, including all required post treatment visits
Exclusion Criteria
  • Serious or active medical or psychiatric illness
  • HIV or hepatitis B viral (HBV) infection
  • Stomach disorder that could interfere with the absorption of the study drug
  • Treated with an anti-HCV medication in the last 30 days
  • Any prior exposure to an HCV nonstructural protein (NS)5a-specific inhibitor
  • Use of human granulocyte-macrophage colony-stimulating factor (GM-CSF), epoetin alfa or other therapeutic hematopoietic agents within 2 weeks of screening
  • History of clinically significant medical condition associated with other chronic liver disease
  • Active spontaneous bacterial peritonitis at screening
  • Females who are breastfeeding
  • Infection requiring systemic antibiotics
  • Participated in a clinical study with an investigational drug or biologic within the last 30 days
  • Active or history (last 6 months) of drug or alcohol abuse
  • History of organ transplant other than liver, kidney, or corneal.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Cohort A, Group 1 (12 wk): CPT Class B (7-9)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class B (CPT score 7-9)
Cohort A, Group 1 (12 wk): CPT Class B (7-9)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class B (CPT score 7-9)
Cohort A, Group 1 (24 wk): CPT Class B (7-9)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class B (CPT score 7-9)
Cohort A, Group 1 (24 wk): CPT Class B (7-9)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class B (CPT score 7-9)
Cohort A, Group 2 (12 wk): CPT Class C (10-12)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class C (CPT score 10-12)
Cohort A, Group 2 (12 wk): CPT Class C (10-12)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class C (CPT score 10-12)
Cohort A, Group 2 (24 wk): CPT Class C (10-12)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class C (CPT score 10-12)
Cohort A, Group 2 (24 wk): CPT Class C (10-12)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class C (CPT score 10-12)
Cohort B, Group 3 (12 wk): F0-F3 FibrosisLDV/SOFLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 12 weeks in participants with Fibrosis Stage F0-F3
Cohort B, Group 3 (12 wk): F0-F3 FibrosisRBVLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 12 weeks in participants with Fibrosis Stage F0-F3
Cohort B, Group 3 (24 wk): F0-F3 FibrosisLDV/SOFLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 24 weeks in participants with Fibrosis Stage F0-F3
Cohort B, Group 3 (24 wk): F0-F3 FibrosisRBVLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 24 weeks in participants with Fibrosis Stage F0-F3
Cohort B, Group 4 (12 wk): CPT Class A (5-6)LDV/SOFLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 12 weeks in participants with CPT Class A (CPT score 5-6)
Cohort B, Group 4 (12 wk): CPT Class A (5-6)RBVLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 12 weeks in participants with CPT Class A (CPT score 5-6)
Cohort B, Group 4 (24 wk): CPT Class A (5-6)LDV/SOFLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 24 weeks in participants with CPT Class A (CPT score 5-6)
Cohort B, Group 4 (24 wk): CPT Class A (5-6)RBVLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 24 weeks in participants with CPT Class A (CPT score 5-6)
Cohort B, Group 5 (12 wk): CPT Class B (7-9)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class B (CPT score 7-9)
Cohort B, Group 5 (12 wk): CPT Class B (7-9)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class B (CPT score 7-9)
Cohort B, Group 5 (24 wk): CPT Class B (7-9)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class B (CPT score 7-9)
Cohort B, Group 5 (24 wk): CPT Class B (7-9)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class B (CPT score 7-9)
Cohort B, Group 6 (12 wk): CPT Class C (10-12)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class C (CPT score 10-12)
Cohort B, Group 6 (12 wk): CPT Class C (10-12)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 12 weeks in participants with CPT Class C (CPT score 10-12)
Cohort B, Group 6 (24 wk): CPT Class C (10-12)LDV/SOFLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class C (CPT score 10-12)
Cohort B, Group 6 (24 wk): CPT Class C (10-12)RBVLDV/SOF (90/400 mg) plus RBV (starting at 600 mg, then adjusted ± based on tolerability \[weight-based maximum: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg\]) for 24 weeks in participants with CPT Class C (CPT score 10-12)
Cohort B, Group 7 (12 wk): FCHLDV/SOFLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 12 weeks in participants with FCH
Cohort B, Group 7 (24 wk): FCHLDV/SOFLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 24 weeks in participants with FCH
Cohort B, Group 7 (12 wk): FCHRBVLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 12 weeks in participants with FCH
Cohort B, Group 7 (24 wk): FCHRBVLDV/SOF (90/400 mg) plus RBV (weight-based: \< 75 kg = 1000 mg, ≥ 75 kg = 1200 mg) for 24 weeks in participants with FCH
Primary Outcome Measures
NameTimeMethod
Percentage of Participants With Sustained Virologic Response (SVR) 12 Weeks After Discontinuation of Therapy (SVR12)Posttreatment Week 12

SVR12 was defined as HCV RNA \< the lower limit of quantitation (LLOQ; ie, 15 IU/mL) at 12 weeks after stopping study treatment.

Percentage of Participants Who Discontinued Study Drug Due to an Adverse EventUp to 24 weeks
Secondary Outcome Measures
NameTimeMethod
HCV RNA Levels and Change From Baseline at Week 4Baseline; Week 4
Percentage of Participants With HCV RNA < LLOQ at Week 6Week 6
Percentage of Participants With Virologic FailureUp to Posttreatment Week 24

Virologic failure was defined as:

* On-treatment virologic failure:

* Breakthrough (confirmed HCV RNA ≥ LLOQ after having previously had HCV RNA \< LLOQ on 2 consecutive measurements while on treatment), or

* Rebound (confirmed \> 1 log10 IU/mL increase in HCV RNA from nadir while on treatment)

* Virologic relapse:

* Confirmed HCV RNA ≥ LLOQ during the posttreatment period having achieved HCV RNA \< LLOQ at last on-treatment visit.

Percentage of Participants With Posttransplant Virologic Response (pTVR) at Posttransplant Week 12Posttreatment Week 12

pTVR was defined as HCV RNA \< LLOQ at Week 12 after transplant.

Percentage of Participants With SVR 4 Weeks After Discontinuation of Therapy (SVR4)Posttreatment Week 4

SVR4 was defined as HCV RNA \< LLOQ at 4 weeks after stopping study treatment.

Percentage of Participants With SVR 8 Weeks After Discontinuation of Therapy (SVR8)Posttreatment Week 8

SVR8 was defined as HCV RNA \< LLOQ at 8 weeks after stopping study treatment.

Percentage of Participants With HCV RNA < LLOQ at Week 1Week 1
Percentage of Participants With HCV RNA < LLOQ at Week 12Week 12
Percentage of Participants With SVR 2 Weeks After Discontinuation of Therapy (SVR2)Posttreatment Week 2

SVR2 was defined as HCV RNA \< LLOQ at 2 weeks after stopping study treatment.

Percentage of Participants With SVR 24 Weeks After Discontinuation of Therapy (SVR24)Posttreatment Week 24

SVR24 was defined as HCV RNA \< LLOQ at 24 weeks after stopping study treatment.

Percentage of Participants With HCV RNA < LLOQ at Week 2Week 2
Percentage of Participants With HCV RNA < LLOQ at Week 4Week 4
Percentage of Participants With HCV RNA < LLOQ at Week 8Week 8
Percentage of Participants With HCV RNA < LLOQ at Week 16Week 16
Percentage of Participants With HCV RNA < LLOQ at Week 20Week 20
Percentage of Participants With HCV RNA < LLOQ at Week 24Week 24
HCV RNA Levels and Change From Baseline at Week 8Baseline; Week 8
Percentage of Participants With a Decrease, No Change, or Increase Between Baseline and Posttreatment Week 4 in CPT ScoreBaseline to Posttreatment Week 4

CPT scores grade the severity of cirrhosis and are used to determine the need for liver transplantation. Scores can range from 5 to 15 (maximum score for entry into the study was 12); higher scores/increased scores indicate greater severity of disease. Groups are arranged by cohort, then by duration of treatment, then by CPT class at baseline.

HCV RNA Levels and Change From Baseline at Week 1Baseline; Week 1
HCV RNA Levels and Change From Baseline at Week 2Baseline; Week 2
HCV RNA Levels and Change From Baseline at Week 6Baseline; Week 6
HCV RNA Levels and Change From Baseline at Week 12Baseline; Week 12
Percentage of Participants With a Decrease, No Change, or Increase Between Baseline and Posttreatment Week 4 in MELD ScoreBaseline to Posttreatment Week 4

Model for End-Stage Liver Disease (MELD) scores are used to assess prognosis and suitability for liver transplantation. Scores can range from 6 to 40; higher scores/increased scores indicate greater severity of disease.

Trial Locations

Locations (34)

Hospital Mondor \\ Service d'Hépatologie et de Gastroentérologie,

🇫🇷

Créteil, France

Medizinische Universitat Wien

🇦🇹

Wien, Austria

Universitätsklinikum RWTH Aachen

🇩🇪

Aachen, Germany

Division of Gastroenterology, University of Alberta, Edmonton

🇨🇦

Edmonton, Alberta, Canada

Universitair Ziekenhuis Gent

🇧🇪

Gent, Belgium

IRCCS Cà Grande Ospedale Maggiore Policlinico

🇮🇹

Milano, Italy

McGill University Health Centre \\ Royal Victoria Hospital

🇨🇦

Montreal, Quebec, Canada

UCL St-Luc Brussels

🇧🇪

Brussels, Belgium

Hospital General Universitari Vall d' Hebron

🇪🇸

Barcelona, Spain

Hopital Paul Brousse

🇫🇷

Villejuif Cedex, France

Hospital Beaujon

🇫🇷

Clichy Cedex, France

Austin Repatriation Hospital (Melbourne) // Victorian Transplant Centre

🇦🇺

Heidelberg, Victoria, Australia

Hopital St. Luc

🇨🇦

Montreal, Quebec, Canada

Medizinische Universitaet Innsbruck

🇦🇹

Innsbruck, Austria

Hopital Saint-Eloi

🇫🇷

Montpellier, France

Medical School of Hannover

🇩🇪

Hannover, Germany

Erasmus MC in Rotterdam

🇳🇱

Rotterdam, Netherlands

Royal Infirmary of Edinburgh \\ Scottish Liver Transplant Unit-Edinburgh

🇬🇧

Edinburgh, United Kingdom

Leids Universitair Medisch Centrum

🇳🇱

Leiden, Netherlands

University Hospitals Birmingham NHS Foundation Trust

🇬🇧

Birmingham, United Kingdom

Royal Prince Alfred Hospital, University of Sydney

🇦🇺

Camperdown, New South Wales, Australia

University Health Network // Toronto General Hospital

🇨🇦

Toronto, Ontario, Canada

Universitätsklinikum Essen - klinikum für Gastroenterolgie und Hepatologie

🇩🇪

Essen, Germany

Azienda Ospedaliera San Giovanni, Battista di Torino \\ Professor of Gastroenterology-San Giovanni Battista Hospital-University of Torino

🇮🇹

Torino, Italy

University Hospital Johann Wolfgang Goethe University, Department of Internal Medicine I

🇩🇪

Frankfurt, Germany

Auckland City Hospital

🇳🇿

Auckland, New Zealand

Hospital Universitario y Politecnico La Fe de Valencia

🇪🇸

Valencia, Spain

University of Berne

🇨🇭

Bern, Switzerland

Puerta de Hierro, Madrid

🇪🇸

Madrid, Spain

Kings College Hospital, Institute of Liver Studies

🇬🇧

London, United Kingdom

University Hospital Zurich

🇨🇭

Zurich, Switzerland

Hospital Clinic i Provincial

🇪🇸

Barcelona, Spain

University of British Columbia and Vancouver General Hospital

🇨🇦

Vancouver, British Columbia, Canada

London Health Sciences Centre-University Hospital

🇨🇦

London, Ontario, Canada

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