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Hemodynamic Response to Exercise in HFpEF Patients After Upregulation of SERCA2a

Early Phase 1
Completed
Conditions
Heart Failure, Congestive
Interventions
Other: Exercise
Registration Number
NCT02772068
Lead Sponsor
Benjamin Levine
Brief Summary

Heart failure with preserved ejection fraction or HFpEF, represents nearly 50% of all heart failure cases and is particularly common in the elderly. The disease has no current treatment options. Symptoms typically occur during exertion or exercise and is likely the result of increased cardiac and pulmonary congestion as a result of impaired diastolic function. Istaroxime is a novel activator of SERCA2a, an important regulator of calcium uptake within the myocyte. We will test the hypothesis that Istaroxime will improve diastolic function during exercise in HFpEF patients which in turn will reduce cardiac and pulmonary congestion.

Detailed Description

About half of all elderly patients with a diagnosis of congestive heart failure have apparently normal systolic function, so called "heart failure with a preserved ejection fraction" or HFpEF. To date, no effective therapy for HFpEF has been found, in part because of failure to discern key pathophysiologic pathways.

An extensive amount of pre-clinical work has identified that altered sarcoplasmic reticulum (SR) Ca2+ uptake, storage, and release play a major role in the changes in cardiac relaxation associated with aging, especially regarding sequestration of Ca++ by the sarcoplasmic reticular Ca++-ATPase (SERCA2a), which causes cardiac muscle relaxation by reducing cytosolic Ca++. Istaroxime is a relatively new drug that augments lusitropic function by upregulating SERCA2a activity in the heart.

Because of the clear importance of slowed relaxation in HFpEF, and the evidence that depressed SERCA2a activity contributes to the slowed relaxation with aging, the proposed study may be establish the "impairment of SERCA2a" hypothesis as a mechanism of impaired relaxation in HFpEF subjects.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
26
Inclusion Criteria
  • age > 60 years
Exclusion Criteria
  • Coronary Ischemia
  • No chronic medical problems
  • BMI > 30 kg/m2

HFpEF Subjects

Inclusion Criteria:

  • age > 60 years
  • signs and symptoms of heart failure
  • ejection fraction > 50%
  • objective evidence of diastolic dysfunction

Exclusion Criteria:

  • Coronary Ischemia
  • Chronic Kidney Disease, stage 4 or greater
  • Persistent atrial fibrillation
  • Severe valvular disease
  • BMI > 45 kg/m2

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Healthy Senior ControlIstaroximeFifteen healthy senior subjects will perform light exercise at a fixed heart rate of 100 beats per minute. Subjects will then be given either placebo infusion (normal saline) or Istaroxime infusion for one hour. Subjects will be blinded to which infusion they are receiving. Subjects will then repeat light exercise at a fixed heart rate of 100 beats per minute. Primary outcome is changes in cardiac filling pressures during exercise.
Healthy Senior ControlExerciseFifteen healthy senior subjects will perform light exercise at a fixed heart rate of 100 beats per minute. Subjects will then be given either placebo infusion (normal saline) or Istaroxime infusion for one hour. Subjects will be blinded to which infusion they are receiving. Subjects will then repeat light exercise at a fixed heart rate of 100 beats per minute. Primary outcome is changes in cardiac filling pressures during exercise.
Heart failure patientsExerciseFifteen HFpEF subjects will perform light exercise at a fixed heart rate of 100 beats per minute. Subjects will then be given either placebo infusion (normal saline) or Istaroxime infusion for one hour. Subjects will be blinded to which infusion they are receiving. Subjects will then repeat light exercise at a fixed heart rate of 100 beats per minute. Primary outcome is changes in cardiac filling pressures during exercise.
Heart failure patientsIstaroximeFifteen HFpEF subjects will perform light exercise at a fixed heart rate of 100 beats per minute. Subjects will then be given either placebo infusion (normal saline) or Istaroxime infusion for one hour. Subjects will be blinded to which infusion they are receiving. Subjects will then repeat light exercise at a fixed heart rate of 100 beats per minute. Primary outcome is changes in cardiac filling pressures during exercise.
Primary Outcome Measures
NameTimeMethod
Change in cardiac filling pressures (pulmonary capillary wedge pressure) during exercise with IstaroximeImmediate; 90 minutes after infusion

Change in cardiac filling pressures (pulmonary capillary wedge pressure) during exercise with Istaroxime

Secondary Outcome Measures
NameTimeMethod
Change in cardiac relaxation time (isovolumic relaxation time) during exercise with Istaroxime90 minutes

Change in cardiac relaxation time (isovolumic relaxation time) during exercise

Trial Locations

Locations (1)

The Institute for Exercise and Environmental Medicine

🇺🇸

Dallas, Texas, United States

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