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A Multicenter Study of rhFGF 18 in Patients With Knee Osteoarthritis Not Requiring Surgery

Phase 1
Completed
Conditions
Knee Osteoarthritis
Interventions
Biological: AS902330
Registration Number
NCT01033994
Lead Sponsor
Merck KGaA, Darmstadt, Germany
Brief Summary

Osteoarthritis (OA) is one of the most common diseases affecting the joints, usually those that are weight bearing such as the knees. OA is considered to be a disease of the cartilage in the joints even though it involves the whole joint, including the bone and synovium (thin lining of the joints which produces synovial fluid). With time, more and more of the cartilage is destroyed by the disease with inflammation commonly occurring.

AS902330 is expected to increase the production and development of specific bone cells: chondrocytes and osteoblasts (cells that produce and maintain bone and cartilage). This is expected to lead to repair and generation of the cartilage, and a narrowing of the space width between the knee joints in a selected region of the knee cartilage. The purpose of this study is to see how safe treatment with AS902330 is, and to evaluate its effect on the knee cartilage. In addition, the study will also measure the effects of AS902330 in the blood, which reflect disease activity.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
192
Inclusion Criteria
  1. Male or female >= 40 years of age; females must be postmenopausal or surgically sterile
  2. Established diagnosis of primary femoro-tibial OA of the target knee by standard American College of Rheumatology Criteria for at least six months (clinical AND radiological criteria)
  3. Radiological disease stage 2 or 3 (i.e., clear evidence of OA, but not most advanced disease) in the target knee according to the Kellgren-Lawrence grading of knee OA
  4. No major knee surgery (e.g., partial or total knee replacement, interventional arthroscopy) in the target knee planned for at least 12 months after first injection of the study drug
  5. Documented need for symptomatic PRN (as needed)-treatment for OA in the target knee with systemic non-steroidal anti-inflammatory drugs (NSAIDs) and/or other analgesics.
  6. Total WOMAC score between 24 and 72 (out of 96, corresponding to mild, moderate, or severe, but not extreme OA symptoms) for the target knee while on oral symptomatic treatment at baseline
  7. Full understanding of the requirements of the study and willingness to comply with all study visits and assessments
  8. Patients must have read and understood the informed consent form, and must have signed it prior to any study-related procedure
Exclusion Criteria
  • any condition, including laboratory findings and findings in the medical history or in the pre-study assessments, that in the opinion of the Investigator constitutes a risk or contraindication for participation in the study or that could interfere with the study objectives, conduct or evaluation
  • clinically significant abnormal hematology (hemoglobin, leucocytes, and platelets), or blood chemistry values (aspartate aminotransferase (AST), alanine aminotransferase (ALT), alkaline phosphatase (ALP), bilirubin, and creatinine
  • receipt of any investigational product or any experimental therapeutic procedure within the last 12 weeks preceding screening
  • participation in FIH study 27575 or in a different cohort of this study
  • i.a. treatment of the target knee with steroids or hyaluronic acid derivatives within the 3 months before baseline
  • for MAD cohorts, any contra-indications to MRI according to MRI guidelines
  • any condition that would interfere with efficacy or safety assessments in the target knee
  • any drug or food supplement with potential disease-modifying effect (glucosamine, diacerin, chondroitin sulfate) unless given at a stable dose over at least 4 weeks prior to first injection
  • use of electrotherapy or acupuncture for OA, unless there is a stable regimen for at least 4 weeks before baseline
  • any known active infections, including suspicion of intra-articular infection and/or infections that may compromise the immune system such as HIV, Hepatitis B or Hepatitis C infection
  • history of sarcoma and/or of other active malignancy within five years, except adequately treated basal cell or squamous cell carcinoma of the skin
  • signs and symptoms suggestive of transmissible spongiform encephalopathy
  • secondary osteoarthritis: e.g., joint dysplasias, aseptic osteonecrosis, acromegaly, Paget's disease, Ehlers-Danlos syndrome, Gaucher's disease, Stickler's syndrome, joint infection, hemophilia, hemochromatosis, calcium pyrophosphate deposition disease, or neuropathic arthropathy whatever the cause

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
AS902330AS902330-
PlaceboAS902330-
Primary Outcome Measures
NameTimeMethod
Change in cartilage thickness in the medial femoro-tibial compartment of the target knee joint, assessed by MRI6 and 12 months after first injection
Nature, incidence and severity of local and systemic treatment-emergent adverse events (TEAEs)MAD Cohorts: 1 year + 1 month; SAD Cohorts: 4 Weeks
Proportion of subjects experiencing AIRs defined as increase of pain by 30mm on a 100mm visual analogue scale (VAS) associated with a self-reported synovial fluid effusion within 3 days following i.a. injectionMAD Cohorts: Week 1, 2, 3, 13 14 and 15 (injections weeks); SAD Cohorts: Week 1
Laboratory assessments, including blood chemistry, hematology, urinalysis, and ECGMAD Cohorts: Week 0, 4, 13, 17, 52; SAD Cohorts: Weeks 0 & 4
Secondary Outcome Measures
NameTimeMethod
Change in cartilage thickness in the medial femoro-tibial compartment of the target knee joint, assessed by MRI52 Weeks
Change in total cartilage volume and thickness in the other compartments of the target knee joint, assessed by MRI52 Weeks
Change over time of structural as well as compositional parameters of the knee joint (e.g. cartilage and bone), evaluated by MRI52 Weeks
Change in WOMAC (Western Ontario MacMaster Osteoarthritis Questionaire) total score in the target knee from 5-point Likert scales52 Weeks
Change in WOMAC Function and Pain index scores in the target knee52 Weeks
Change in osteoarthritis (OA) pain in the target knee on a 100mm visual analogue scale (VAS)52 Weeks
Change in JSW in the target knee by x-ray52 Weeks
Presence of anti-AS902330 antibodies52 Weeks
Blood levels of AS90233052 Weeks
MRI at 3 months, score on WOMAC questionnaire at 3, 6 and 12 months.6 days

Trial Locations

Locations (28)

SKDS Research, Inc.

🇨🇦

Newmarket, Canada

Oulu University Hospital, Surgical and Intensive Care Division

🇫🇮

Oulu, Finland

Kells Medical Research Group

🇨🇦

Pointe Claire, Canada

PAREXEL International GmbH

🇩🇪

Berlin, Germany

London Road Diagnostic Clinic

🇨🇦

Sarnia, Canada

UMHAT "Sv. Ivan Rilski", Clinical Research Unit for Phase I

🇧🇬

Sofia, Bulgaria

Centre de rhumatologie St-Louis

🇨🇦

Quebec, Canada

Groupe de Recherche en Maldies Osseuses de Quebec

🇨🇦

Quebec, Canada

Polyclinic for internal medicine, gynecology, radiology, physical medicine and rehabilitation

🇭🇷

Zagreb, Croatia

Clinical hospital Split

🇭🇷

Split, Croatia

Albion Finch Medical Centre

🇨🇦

Toronto, Canada

Clinical Hospital "Sestre Milosrdnice"

🇭🇷

Zagreb, Croatia

Turku University Central Hospital, Orthopedic Research Unit

🇫🇮

Turku, Finland

NZOZ Centrum Medyczne Artur Racewicz

🇵🇱

Bialystok, Poland

REUMED Sp. z o.o.,

🇵🇱

Lublin, Poland

Niepubliczny Zaklad Opieki Zdrowotnej Nasz Lekarz

🇵🇱

Torun, Poland

Centrum Leczenia Chorob Cywilizacyjnych

🇵🇱

Warsaw, Poland

Institute of Rheumatology Resavska 69

🇷🇸

Beograd, Serbia

FARMOVS-PAREXEL (Pty) Ltd, University of the Free State

🇿🇦

Bloemfontein, South Africa

Ortopediska mottagningen

🇸🇪

Hässleholm, Sweden

PAREXEL-Port Elizabeth, Mercantile Hospital

🇿🇦

Port Elizabeth, South Africa

Kirurg- och ortopedkliniken Kungälvs sjukhus, 442 83 Kungälv

🇸🇪

Kungälv, Sweden

PAREXEL -George

🇿🇦

George, South Africa

Kuopio University Hospital, Department of Ortopaedics

🇫🇮

Kuopio, Finland

• Name: Institute of diagnostic, prevention and rechabilitation of cardiovascular and rheumatoid diseases

🇷🇸

Niska Banja, Serbia

Krakowskie Centrum Medyczne NZOZ

🇵🇱

Cracow, Poland

Centrum Medyczne OSTEOMED Sp. z o.o.

🇵🇱

Warsaw, Poland

Clinical Hospital Center Bezanijska Kosa

🇷🇸

Beograd, Serbia

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