MedPath

Treatment of Epidermolysis Bullosa Dystrophica by Polyphenon E (Epigallocatechin 3 Gallate)

Phase 2
Completed
Conditions
Epidermolysis Bullosa Dystrophica
Interventions
Drug: Polyphenon E before Placebo
Drug: placebo before treatment
Registration Number
NCT00951964
Lead Sponsor
Centre Hospitalier Universitaire de Nice
Brief Summary

Dystrophic epidermolysis bullosa hereditaria are genodermatosis responsible for formation of cutaneous bullous lesion arising spontaneously or after mechanical trauma.

These lesions are due to mutation on gene COL7A1 coding for collagen VII. There is no treatment available. Cares are consisting to dress lesions and to protect the skin.

The investigators have recently observed on patients having residual expression of collagen VII that phenotype severity is modulated by activation degree of dermic metalloproteinase. The investigators have also observed that epigallocatechin-3-gallate (Polyphenon E®) could be regulated this activity.

The primary purpose of this study is to assessing the efficacity of Polyphenon E to decrease the number of cutaneous bullosa after four month of treatment.

The primary outcome measure is the rate of patient presenting a decrease of 20% or more of the number of cutaneous bullosa.

Secondary outcomes are: severity of mucosa impairment, affected cutaneous surface, the average duration of cicatrisation and treatment tolerance.

This study foresees the inclusion of 22 patients older than 2 years old in 5 centers.

When patients are included, they will be randomized and receive the treatment (or placebo) for 4 months.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
18
Inclusion Criteria
  • known mutation of COL7A1
Exclusion Criteria
  • tea drinkers
  • patient receiving induction treatment,protease inhibitor treatment
  • liver failure

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
1Polyphenon E before Placebopatients receive the treatment in first and placebo in second part of study
2placebo before treatmentpatients receive placebo in first and treatment in second part of study
Primary Outcome Measures
NameTimeMethod
decrease of number of cutaneous bullosaafter 4 months of treatment
Secondary Outcome Measures
NameTimeMethod
efficacity of treatmentat 4 , 6, 7 10 months after beginnig of treatment and at year 1
tolerance tio treatmentat 1, 4, 6, 7, 10 and 12 months after beginnig the treatment

Trial Locations

Locations (5)

Dermatology Department, Necker Enfants Malades, APHP

🇫🇷

Paris, France

Dijon University Hospital, Dermatology Department

🇫🇷

Dijon, France

Dermatology Department, Saint Louis Hospital, APHP

🇫🇷

Paris, France

Toulouse University Hospital, Dermatology Department

🇫🇷

Toulouse, France

Dermatology Department, Bordeaux University Hospital

🇫🇷

Bordeaux, France

© Copyright 2025. All Rights Reserved by MedPath