MedPath

Multicentric Prospective Study to Screen Inborn Errors of Metabolism in Non-immune Hydrops (NIH) Fetalis by Massively Parallel Sequencing

Not Applicable
Completed
Conditions
Non-Immune Hydrops Fetalis
Interventions
Diagnostic Test: NON-IMMUNE HYDROPS FETALIS diagnosis
Registration Number
NCT04308603
Lead Sponsor
Hospices Civils de Lyon
Brief Summary

A fetal hydrops, also called a fetal anasarca, is the buildup of fluid in the serosa and / or fetal subcutaneous tissue. The diagnosis is made by ultrasound, possibly from the first trimester of pregnancy.

The etiologies of hydrops can be immune or non-immune. The historically classic immune causes are linked to fetal-maternal alloimmunizations in erythrocyte blood groups. The implementation of systematic prevention of these anti rhesus immunizations since the 1970s has significantly reduced the incidence of immune hydrops Non-immune hydrops (NIH) now represent 90% of fetal hydrops. Known causes of NIH can be classified in several ways depending on the mechanism or organ involved.

The prognosis for NIH is closely linked to the cause. Fetal anemia due to maternal-fetal infections can heal spontaneously or give rise to in utero transfusions. Cardiac rhythm abnormalities are accessible to medical treatment. Chylothorax compressions may benefit from in utero drainage, but chromosomal or metabolic causes cannot benefit from antenatal care. The term of pregnancy in which the hydrops is discovered also has an impact on survival, which however remains poor.

In France, certain pathologies can be considered as particularly serious without the possibility of treatment and give rise to a request for medical termination of pregnancy. This possibility is subject to acceptance by two practitioners who are members of a multidisciplinary prenatal diagnostic center (CPDPN). This preliminary multidisciplinary reflection participates in the development of prenatal counseling with the greatest precision in diagnostic hypotheses. This prenatal advice is essential for a couple on the decision to make a pregnancy in progress but also for future pregnancies, given the 25% risk of recurrence due to the autosomal recessive mode of transmission.

Thus the current screening strategy for inherited metabolic diseases on amniotic fluid is fragmented. The resulting subdiagnosis explains the objective of the study of using the new high throughput sequencing techniques (NGS) in this indication. This approach should make it possible to reduce the number of cases classified as idiopathic, to allow the parents concerned to receive suitable genetic counseling with a view to new pregnancies, and to refine the knowledge of the prenatal epidemiology of these pathologies.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
71
Inclusion Criteria
  • patient> 18 years old
  • Single Pregnancy
  • Progressive pregnancy greater than 11 weeks: Fetal death in utero in a fetus previously known to be a carrier of non Immun Hydrops (NIH) is not an exclusion criterion.
  • Presence of an ultrasound defined as follows and confirmed by a multidisciplinary prenatal diagnostic center CPDPN:
  • Before 14 weeks: Generalized subcutaneous edema descending to the abdomen, associated or not with peri-visceral effusion
  • After 14 weeks: presence of at least 2 of the following criteria: ascites, pleural effusion, pericardial effusion, subcutaneous edema, placental edema, hydramnios.
  • Persistent hygroma after 14 weeks of amenorrhea
  • Persistent isolated perivisceral effusions without etiologies found
  • Patient having an invasive diagnostic sample (amniocentesis)
  • Social insured in France
  • Patient who signed the informed consent of the study
Read More
Exclusion Criteria
  • NIH whose diagnosis is known and confirmed as non-metabolic by a CPDPN
  • Non-progressive pregnancy with Fetal Death in utero with normal previous ultrasound monitoring
  • Refusal of invasive diagnostic sampling
  • Patient under legal protection measure
Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
pregnant patient whose fetuses have an antenatal NIHNON-IMMUNE HYDROPS FETALIS diagnosisAll pregnant patients whose fetuses have an antenatal revelation of NIH from the first trimester ultrasound scan will be included in this study.
Primary Outcome Measures
NameTimeMethod
Proportion of fetuses for which a genetic anomaly responsible for antenatal revelation Non Immun Hydrops by Next Generation Sequencing (NGS) analysisduring pregnancy after the 14th week of amenorrhea

Proportion of fetuses for which a genetic anomaly responsible for antenatal revelation Non Immun Hydrops can be detected by Next Generation Sequencing (NGS) analysis of the gene panel incriminated in inherited metabolic malformation compared to the proportion of fetuses for which a genetic anomaly has been identified by the technique current standard biochemical.

Secondary Outcome Measures
NameTimeMethod
issue of the pregnancyimmediately after the child birth

The percentage of death in utero, the percentage of medical termination of pregnancy, the percentage of neonatal survival and the percentage of pregnancy continued until the end will be calculated

number of week of amenorrhea of gestationimmediately after the child birth

number of week of amenorrhea of gestation will be measured

time to return the results in days of NGS techniquesduring pregnancy after the 14th week of amenorrhea

The delay of answer will be defined by the time to return the results by analysis of the panel of genes tested compared to the current standard biochemical technique, measured between the date of completion of the prenatal diagnosis procedure and the date of communication of the results to the parents.

number of technical failure of these new tools of NGS techniquesduring pregnancy after the 14th week of amenorrhea

Number of technical failures: unable to extract DNA, too little DNA, failed sequencing), and analysis of these failures will be measured and compared to the current standard biochemical technique.

Number of cases where the interpretation of the genetic variants did not lead to a conclusionduring pregnancy after the 14th week of amenorrhea

by the number of cases where the interpretation of the genetic variants highlighted did not allow concluding on the imputability for the clinical picture will be assessed of these new tools of NGS techniques

Comparison of percentage of etiology detected between the NGS technique and the biochemical technique.during pregnancy after the 14th week of amenorrhea

The percentage of the following etiology of interest (Cardiovascular abnormalities, Chromosomal abnormalities, Haematological abnormalities, infections, Thoracic anomalies, Twin-to-twin transfusion syndromes, Uro-Nephrological Anomalies, Abdominal anomalies, Lymphatic dysplasia, Fetal or placental tumors, osteochondrodysplasias. syndromic, Hereditary Metabolism Diseases) will be assessed and compared between the 2 methods.

Trial Locations

Locations (17)

CHU Besan莽on

馃嚝馃嚪

Besan莽on, France

CHU Pellegrin

馃嚝馃嚪

Bordeaux, France

H么pital Femme M猫re Enfant

馃嚝馃嚪

Bron, France

H么pital d'Estaing

馃嚝馃嚪

Clermont-Ferrand, France

H么pital Le Bocage

馃嚝馃嚪

Dijon, France

CHU Grenoble

馃嚝馃嚪

La Tronche, France

CHU Limoges

馃嚝馃嚪

Limoges, France

Hopital Croix Rousse

馃嚝馃嚪

Lyon, France

Hopital Nord

馃嚝馃嚪

Marseille, France

CHU Marseille Timone

馃嚝馃嚪

Marseille, France

CHU Montpellier

馃嚝馃嚪

Montpellier, France

H么pital Archet 2

馃嚝馃嚪

Nice, France

APHP Trousseau

馃嚝馃嚪

Paris, France

Hopital Lyon Sud

馃嚝馃嚪

Pierre-B茅nite, France

CHU Saint Etienne

馃嚝馃嚪

Saint-Priest-en-Jarez, France

H么pital Paule de Viguier;

馃嚝馃嚪

Toulouse, France

CHU de Nancy Brabois,

馃嚝馃嚪

Vand艙uvre-l猫s-Nancy, France

漏 Copyright 2025. All Rights Reserved by MedPath