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Evolocumab Pregnancy Exposure Registry

Terminated
Conditions
Hypercholesterolemia; ASCVD; Pregnancy
Interventions
Registration Number
NCT02957604
Lead Sponsor
Amgen
Brief Summary

This is a prospective observational registry study to evaluate fetal, infant and childhood outcomes in women exposed to evolocumab during pregnancy

Detailed Description

This pregnancy registry will be conducted by University of California Research Center for the Organization of Teratology Information Specialists (OTIS) which is a network of university and health department based telephone information centers serving pregnant women and healthcare providers throughout North America. Participants will be enrolled on an ongoing basis through year 10 of the study and each will be followed from the time they enroll, through the 5-year postnatal follow up period for an overall study period of 15 years. Participants are recruited concurrently from callers to OTIS centers, from healthcare providers and through direct to consumer marketing efforts.

Recruitment & Eligibility

Status
TERMINATED
Sex
Female
Target Recruitment
140
Inclusion Criteria
  • For all groups: Qualified subjects will agree to the conditions and requirements of the study including the interview schedule, release of medical records, the physical examination of live born infants, and 5 years of follow-up.
  • For the Specific Evolocumab-Exposed Cohort: Currently pregnant women (maternal report validated by medical records) diagnosed with ASCVD, or hypercholesterolemia associated with FH who have been exposed to evolocumab for any number of days, at any dose, and at any time from the first day of the LMP up to and including the end of pregnancy.
  • For Comparison Group I: Currently pregnant women (maternal report validated by medical records) diagnosed with ASCVD, or hypercholesterolemia associated with FH but who were not exposed to evolocumab during pregnancy or any time within 90 days prior to the first day of the LMP.
  • For Comparison Group II: Currently pregnant women not diagnosed with ASCVD, or hypercholesterolemia associated with FH who have not been exposed to evolocumab during pregnancy or any time within 90 days prior to the first day of the LMP, and who have no exposure to any known human teratogens as determined by the OTIS Research Center
  • For General Evolocumab-Exposed Case Series group: Women with exposure to evolocumab during pregnancy who do not meet the criteria for the Specific Evolocumab-Exposed cohort for reasons including (but not limited to): they do not have ASCVD and/or hypercholesterolemia associated with FH (off-label use), they were exposed to evolocumab but the pregnancy has already completed, they enrolled in the cohort study with a previous pregnancy, or they already have a prenatal diagnosis of a major birth defect
Exclusion Criteria

For all groups except the General Evolocumab Exposed Case Series Group:

  • Women who first contact the Registry after prenatal diagnosis of a major structural defect
  • Women who were exposed to a different PCSK9 inhibitor during their current pregnancy or at any time within 5 half-lives prior to the first day of the LMP
  • Women who have enrolled in this Registry with a previous pregnancy

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Specific Evolocumab-Exposed CohortevolocumabWomen diagnosed with Atherosclerotic Cardiovascular Disease (ASCVD), or hypercholesterolemia associated with Familial Hypercholesterolemia (FH), who were exposed to Evolocumab (Repatha) during pregnancy
General Evolocumab-Exposed Case SeriesevolocumabWomen who were exposed to Evolocumab (Repatha) but do not fulfill eligibility criteria for the Specific Evolocumab-Exposed Cohort
Primary Outcome Measures
NameTimeMethod
Rate of major structural defectsUp to 1 year of age

Rate of major structural defects, defined and classified by the Centers for Disease Control and Prevention (CDC) Metropolitan Atlanta Congenital Defects Program (MACDP) 6 Digit Code Defects List coding manual (CDC, 2007)

Secondary Outcome Measures
NameTimeMethod
Pregnancy Outcome: Rate of spontaneous abortionUp to 19 wks post LMP

Rate of spontaneous abortion where spontaneous abortion is defined as non-deliberate fetal death which occurs prior to 19 completed weeks post-last menstrual period (LMP)

Infant Outcome: Rate of minor structural defectsBetween birth and 12 months post natal

Rate of minor structural defects where a minor structural defect is defined as a structural anomaly which has neither cosmetic nor functional significance to the child.

Infant Outcome: Rate of postnatal growth deficiencyUp to 1 year of age

Rate of postnatal growth deficiency where postnatal growth deficiency is defined as postnatal size (weight, length, or head circumference) less than/equal to the 10th centile for sex and age using standard pediatric growth curves, and adjusted for postnatal age for premature infants if the postnatal measurement is obtained at less than 1 year of age.

Infant Outcome: Rate of postnatal hospitalizationsThrough 5 years postnatal

Rate of postnatal hospitalizations as assessed throughout the 5-year postnatal follow-up period.

Pregnancy Outcome: Rate of elective abortionThrough 9 month pregnancy period

Rate of elective abortion where elective abortion is defined as deliberate termination of pregnancy at any time in gestation

Pregnancy Outcome: Rate of stillbirthAt or after 19 completed weeks post LMP

Rate of stillbirth where stillbirth is defined as non-deliberate fetal death anytime in gestation at or after 19 completed weeks post-LMP

Infant Outcome: Rate of small for gestational ageAt birth

Rate of small for gestational age where small for gestational age is defined as birth size (weight, length, or head circumference) less than/equal to the 10th centile for sex and gestational age using standard pediatric CDC growth curves for full term or preterm infants

Breastfeeding/Lactation Outcome: Proportion of women who breastfedThrough 6 weeks post delivery

Proportion of women who breastfed (at all) in the first 6 weeks after delivery

Breastfeeding/Lactation Outcome: Proportion who breastfed exclusivelyThrough the first 2 weeks postnatal

Among women who breastfed (in the first 6 weeks after delivery), the proportion who breastfed exclusively during the first 2 weeks of life

Infant Outcome: Pattern of minor structural defectsBetween birth and 12 months postnatal

Pattern of minor structural defects where a minor structural defect is defined as a structural anomaly which has neither cosmetic nor functional significance to the child and a pattern is defined as the same 3 or more minor structural defects in 2 or more children.

Pregnancy Outcome: Rate of premature deliveryPrior to 37 weeks of gestation

Rate of premature delivery where premature delivery is defined as live birth prior to 37.0 weeks gestation as counted from LMP (or ultrasound adjusted date)

Infant Outcome: Rate of postnatal serious infectionsThrough 5 years postnatal

Rate of postnatal serious infections as assessed throughout the 5-year postnatal follow-up period.

Infant Outcome: Rate of infant reactions to scheduled vaccinationsThrough 5 years postnatal

Rate of infant reactions to scheduled vaccinations as assessed throughout the 5-year postnatal follow-up period.

Infant Outcome: Infant response to IgG-tetanus antibodyBetween 6-12 months of age

Infant response to IgG-tetanus antibody as a biological marker to evaluate humoral immune response via a standardized assay test.

Infant Outcome: Adverse neurodevelopment outcomesBetween 16 months to 17 months 30 days of age and between 3.5-5 years of age

Adverse neurodevelopmental outcomes as assessed during 2 periods (between 16 months to 17 months 30 days of age and between 3.5-5 years of age) via standardized tests of performance

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