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Use of Azithromycin as Immunomodulatory Therapy in Grave&Apos;s Orbitopathy

Phase 1
Withdrawn
Conditions
Graves Ophthalmopathy
Interventions
Registration Number
NCT01379196
Lead Sponsor
Rabin Medical Center
Brief Summary

The purpose of this study is to examine the effects of Azithromycin (a macrolide class antibiotic), given three times weekly, for patients with active moderate-severe, non sight-threatening, Graves Orbitopathy.

Indices for follow-up will include:

* Clinical activity score

* Anti-TSH receptor antibody levels

* Thickening of extraocular muscles per ultrasound

* Quality of life score for Graves Orbitopathy patients

Detailed Description

Graves Orbitopathy (GO) is an autoimmune inflammatory disorder causing visual morbidity, cosmetic morbidity and interference with quality of life. The disease has an inflammatory stage and a non-inflammatory, fibrotic stage.

Treatment of inflammatory stage moderate-severe GO includes steroids, as recommended by the EUGOGO consortium. However, the length of treatment needed and the risk of steroid side-effects may lead to multiple undesired treatment induced morbidity.

Antibiotics of the macrolide group posses known immune-modulatory effects that are separate from their antibacterial mode of action. This mode of action has lead to the routine use of macrolide antibiotics for delaying graft rejection following lung transplants.

We propose to test the effect of this class of antibiotics for non-sight threatening, moderate-severe, inflammatory GO.

Recruitment & Eligibility

Status
WITHDRAWN
Sex
All
Target Recruitment
Not specified
Inclusion Criteria
  • Clinical diagnosis of Graves Orbitopathy
  • Clinical activity score higher than 2
  • Must be able to swallow tablets
Exclusion Criteria
  • sight-threatening Graves Orbitopathy
  • Diplopia in primary gaze
  • Macrolide allergy or intolerance

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Azithromycin PO three times weeklyAzithromycinTablets Azithromycin 500 mg PO three times weekly for three months
Primary Outcome Measures
NameTimeMethod
Change in clinical activity score between baseline and after three monthsThree months

Change in the clinical activity score between baseline and after 3 months

(Clinical Activity Score is a validated index of Graves Ophthalmopathy that assigns one point to the presence of: 1.spontaneous retrobulbar pain, 2. pain on up/downgaze, 3. redness of eyelids, 4. redness of conjunctiva, 5. swelling of eyelids, 6. inflammation of caruncle/plica, 7. chemosis). The maximal clinical activity score is thus 7.

Secondary Outcome Measures
NameTimeMethod
ANTI TSH Receptor antibody levels0, 3 and 6 months

Serum measurements of ANTI TSH Receptor antibody levels

Measurement of extraocular muscle thickening3 months

Ultrasonic measurement of extraocular muscle thickening

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