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Prevention of bronchiectasis in infants with cystic fibrosis

Phase 3
Active, not recruiting
Conditions
bronchiectasis in cystic fibrosis
Respiratory - Other respiratory disorders / diseases
Registration Number
ACTRN12610001072000
Lead Sponsor
Telethon Kids Institute
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Active, not recruiting
Sex
All
Target Recruitment
130
Inclusion Criteria

1. Children of either sex with a diagnosis of CF following detection via New Born Screening (NBS);
2. Participants who, in the opinion of the Investigator, are able to comply with the protocol for its duration;
3. Written informed consent signed and dated by parent/legal guardian according to local regulations

Exclusion Criteria

1. Born <30 weeks gestation;
2. Prolonged mechanical ventilation in the first 3 months of life;
3. Participation in another randomized controlled trial within the 3 months preceding inclusion in this study;
4. A significant medical disease or condition other than CF that is likely to interfere with the child’s ability to complete the entire protocol;
5. Previous major surgery except for meconium ileus;
6. Macrolide hypersensitivity

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Proportion of children with radiologically-defined bronchiectasis[three years of age]
Secondary Outcome Measures
NameTimeMethod
extent and severity of bronchiectasis[three years of age];CF-related quality of life[three years of age];time to first pulmonary exacerbation[3 years of age];proportion of participants experiencing a pulmonary exacerbation[3 years of age];number of courses of inhaled or oral antibiotics[3 years of age];number of days of inhaled antibiotics[3 years of age];incidence of hospitalizations/Accident & Emergency visitsfor acute respiratory exacerbations[3 years of age];number of days of hospitalization and number of days of intravenous antibiotics for acute respiratory exacerbations[3 years of age];volume of trapped gas at age 3 years assessed using a low dose volumetric computed tomography scan[3 years of age];Body mass index[3 years of age]
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