MedPath

Comparison of Ridinilazole Versus Vancomycin Treatment for Clostridium Difficile Infection

Phase 3
Completed
Conditions
Clostridioides Difficile Infection
Interventions
Registration Number
NCT03595553
Lead Sponsor
Summit Therapeutics
Brief Summary

Summit is developing ridinilazole as a novel antimicrobial for Clostridioides difficile Infection (CDI), formerly known as Clostridium difficile Infection, with the goal of demonstrating an improved Sustained Clinical Response rate in subjects treated with ridinilazole as compared to subjects treated with vancomycin.

A phase 2 proof of concept study, with vancomycin as comparator, demonstrated these attributes with a comparable safety profile. A high fecal concentration of ridinilazole and little systemic exposure were noted.

The rationale for this phase 3 study is to confirm the improvement in sustained clinical response of CDI over vancomycin and to compare the safety and tolerability of ridinilazole to that of vancomycin.

Ridinilazole plasma concentration will be assessed in a subset of patients.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
759
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
vancomycinVancomycinvancomycin 125 mg qid
ridinilazoleRidinilazoleridinilazole 200mg bid
Primary Outcome Measures
NameTimeMethod
Number of Participants With Sustained Clinical Response (SCR) Defined as Clinical Response and no Recurrence of CDI Through 30 Days Post End of Treatment (EOT).Day 40

This primary outcome measures the number of participants with Sustained Clinical Response (SCR). SCR is defined as Clinical Response and no recurrence of CDI through 30 days post End of Treatment (EOT). At D40, D70 and D100 the Investigator or medically qualified designee will determine if the patient has a sustained clinical response or experienced RECURRENCE since the previous assessment. The Investigator will assess cure/failure and recurrence based on available information which includes, but is not limited to, improvement from baseline in the number of UBMs, signs \& symptoms of CDI, and the requirement for CDI medication. The Investigator should assess cure/failure in a way that best reflects the Investigator's standard clinical practice.

Secondary Outcome Measures
NameTimeMethod
Clinical ResponseDay 12

defined as

* less than 3 unformed bowel movements (UBMs) for consecutive days and maintained through EOT without further CDI treatment at EOT + 2 days, or

* the investigator's assessment that the subject no longer needs specific CDI antimicrobial treatment after completion of the course of study medication.

Clinical CureDay 12

defined as the resolution of diarrhea (\<3 UBMs in the 1-day period immediately prior to EOT, that is maintained for 2 days after EOT).

Sustained Clinical Response Over 60 DaysDay 70

defined as Clinical Response and no recurrence of CDI through 60 days post EOT

Sustained Clinical Response Over 90 DaysDay 100

defined as Clinical Response and no recurrence of CDI through 90 days post EOT

Relative Abundance of the 3 Main Bile Acid Groups (Conjugated Primary, Primary and Secondary Bile Acids) From Baseline to EOT.Day 10

This secondary outcome measures the relative abundance of the 3 main Bile Acid Groups (Conjugated Primary, Primary and Secondary Bile Acids) from Baseline to EOT.

Percentage of Change of α-diversity (Shannon Index) of the Microbiota in Stool Samples From Baseline to EOT.Day 10

This secondary outcome measures the percentage of change of α-diversity (Shannon Index) of the microbiota in stool samples from baseline to EOT. Shannon index is a weighted statistic measuring both species richness and evenness. The Shannon Index is calculated by taking the relative abundance of each species and sums the relative abundance times the natural log of the relative abundance for each species. The value is converted into a positive value by times minus one. A higher Shannon Index means higher diversity

Measure of β-diversity of the Gut Microbiota Between Baseline and EOT Stool Samples (Bray-Curtis Index/Dissimilarity).Day 10

This secondary outcome measures the β-diversity of the gut microbiota in stool samples from baseline to EOT. Bray-Curtis index/dissimilarity measures how different two samples are in the microbiome composition. The Bray-Curtis dissimilarity is graded between 0 and 1, where 0 means the two samples have the same composition (that is they share all the species and every species has the same abundance), and 1 means the two samples do not share any species.

Trial Locations

Locations (149)

DCC1-Sliven Ltd.

🇧🇬

Sliven, Bulgaria

''Tzaneio'' General Hospital of Piraeus

🇬🇷

Piraeus, Greece

Dr. Kenessey Albert Kórház Rendelőintézet, Tüdőgyógyászati Aktív Osztály

🇭🇺

Balassagyarmat, Hungary

Csongrad County Dr. Bugyi Istvan Hospital, Dept. Of Internal Medicine

🇭🇺

Szentes, Hungary

Országos Korányi Pulmonológiai Intézet, Központi Intenzív osztály

🇭🇺

Budapest, Hungary

Klinika Chorób Zakaźnych i Hepatologii Wojewódzki Szpital Obserwacyjno-Zakaźny im. Tadeusza Browicza

🇵🇱

Bydgoszcz, Poland

Wojewódzki Szpital Specjalistyczny im. J. Gromkowskiego we Wrocławiu; I Oddział Chorób Zakaźnych

🇵🇱

Wroclaw, Poland

SUUMC-Boli infectioase

🇷🇴

Bucuresti, Romania

Clinical Hospital of Infectious and Tropical Diseases "Dr. Victor Babes"

🇷🇴

Bucuresti, Romania

Szpital Specjalistyczny w Chorzowie

🇵🇱

Chorzów, Poland

Spitalul Clinic de Boli Infectioase Constanta

🇷🇴

Constanta, Romania

Spitalul Clinic de Boli Infectioase- Sfanta Parascheva

🇷🇴

Iasi, Romania

David Geffen School of Medicine at UCLA

🇺🇸

Los Angeles, California, United States

Carle Foundation Hospital

🇺🇸

Urbana, Illinois, United States

University of Maryland School of Medicine

🇺🇸

Baltimore, Maryland, United States

University of Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Moncton Hospital/Horizon Health Network

🇨🇦

Moncton, New Brunswick, Canada

Phoenix Medical Research LLC

🇺🇸

Miami, Florida, United States

The University of Kansas Medical Center

🇺🇸

Kansas City, Kansas, United States

Hospital Ernesto Dornelles

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Hospital Vera Cruz

🇧🇷

Belo Horizonte, Minas Gerais, Brazil

Santa Casa De Misericordia De Belo Horizonte

🇧🇷

Belo Horizonte, Minas Gerais, Brazil

Unidade de Pesquisa - NCS - Hospital Felício Rocho

🇧🇷

Belo Horizonte, Minas Gerais, Brazil

Santa Casa de Misericordia de Porto Alegre

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

AB Clinical Trials

🇺🇸

Las Vegas, Nevada, United States

ECU Adult Specialty Care

🇺🇸

Greenville, North Carolina, United States

Monument Health Clinical Research

🇺🇸

Rapid City, South Dakota, United States

St. Vincent Mercy Medical Center

🇺🇸

Toledo, Ohio, United States

GI Alliance - Texas Digestive Disease Consultants - San Marcos

🇺🇸

San Marcos, Texas, United States

Centro Médico Talar

🇦🇷

El Talar, Buenos Aires, Argentina

Hospital Alemao Oswaldo Cruz

🇧🇷

Sao Paulo, Brazil

Monash Medical Center

🇦🇺

Clayton, Victoria, Australia

Hospital das Clinicas de Porto Alegre

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Westmead Hospital

🇦🇺

Westmead, New South Wales, Australia

Fiona Stanley Hospital

🇦🇺

Murdoch, Western Australia, Australia

Hospital Italiano de Buenos Aires

🇦🇷

Buenos Aires, Argentina

Mater Misericordiae

🇦🇺

South Brisbane, Queensland, Australia

Princess Alexandra Hospital

🇦🇺

Woolloongabba, Queensland, Australia

MHAT "Sv.Ivan Rilski-2003"OOD

🇧🇬

Dupnitsa, Kyustendil, Bulgaria

"MHAT - Blagoevgrad, EOOD Department of Gastroenterology"

🇧🇬

Blagoevgrad, Bulgaria

General Hospital of Athens ''Evangelismos'

🇬🇷

Athens, Greece

University Hospital of Patras

🇬🇷

Patras, Greece

Medical center - Izgrev

🇧🇬

Sofia, Bulgaria

Centre Hospitalier de l'Universite de Montreal

🇨🇦

Montréal, Quebec, Canada

"Pathophysiology Department Athens University Medical School"

🇬🇷

Athens, Greece

"'Hygeia'' Hospital 2nd Department of Medicine and Infectious Diseases"

🇬🇷

Athens, Greece

Pest Megyei Flór Ferenc Kórház, V. Belgyógyászat

🇭🇺

Kistarcsa, Pest Megye, Hungary

Békés Megyei Központi Kórház Pándy Kálmán Tagkórház, Infektológia-Hepatológia Osztály

🇭🇺

Gyula, Békés, Hungary

Javorszy Odon Hospital

🇭🇺

Vác, Hungary

Hallym University Kangnam Sacred Heart Hospital

🇰🇷

Anyang-si, Seoul, Korea, Republic of

SP ZOZ w Bochni Szpital Powiatowy im. B. Marty Wieckiej

🇵🇱

Bochnia, Poland

Specjalistyczne Gabinety Sp z o.o.

🇵🇱

Krakow, Poland

Waikato District Health Board Waikato Hospital

🇳🇿

Hamilton, Waikato, New Zealand

Asan Medical Center

🇰🇷

Soeul, Korea, Republic of

Szpital Bocheński SP ZOZ w Bochni

🇵🇱

Bochnia, Poland

Spitalul Minicipal Caracal

🇷🇴

Caracal, Romania

Waitemata District Health Board WDHB North Shore Hospital

🇳🇿

Takapuna, Auckland, New Zealand

Taranaki District Health Board TDHB - Taranaki Base Hospital

🇳🇿

New Plymouth, Taranki, New Zealand

Hospital Universitario Reina Sofía. Hospital Provincial

🇪🇸

Córdoba, Spain

Lakeridge Health

🇨🇦

Oshawa, Ontario, Canada

Foothills Medical Centre, South Tower

🇨🇦

Calgary, Alberta, Canada

Recherche Médicale St-Jérôme Inc

🇨🇦

Quebec, Canada

University of Alabama - Birmingham

🇺🇸

Birmingham, Alabama, United States

Infectious Disease Specialists of Atlanta

🇺🇸

Decatur, Georgia, United States

Southern Illinois University School of Medicine

🇺🇸

Springfield, Illinois, United States

Hallym University Chuncheon Sacred Heart Hospital

🇰🇷

Chuncheon, Gangwon-do, Korea, Republic of

Hanyang University Guri Hospital

🇰🇷

Guri-Si, Gyeonggi-do, Korea, Republic of

Hospital Ramos Mejía

🇦🇷

Buenos Aires, Argentina

Instituto Medico ALAS

🇦🇷

Salta, Argentina

Gasteroenterology Group of Naples

🇺🇸

Naples, Florida, United States

Fundacao Faculdade Regional de Medicina de Sao Jose do Rio Preto

🇧🇷

Sao Jose do Rio Preto, Sao Paulo, Brazil

GI Alliance - Arizona Digestive Health - Sun City

🇺🇸

Sun City, Arizona, United States

Facey Medical Foundation

🇺🇸

Mission Hills, California, United States

Midway Immunology and Research Center

🇺🇸

Fort Pierce, Florida, United States

University Of California Davis

🇺🇸

Sacramento, California, United States

Alliance Medical Research LLC

🇺🇸

Lighthouse Point, Florida, United States

Paradigm Clinical Research Centers, Inc

🇺🇸

Redding, California, United States

San Marcus Research

🇺🇸

Miami Lakes, Florida, United States

Pines Care Research Center Inc.

🇺🇸

Pembroke Pines, Florida, United States

Professional Health Care of Pinellas

🇺🇸

Saint Petersburg, Florida, United States

Bardmoor Gastroenterology

🇺🇸

Seminole, Florida, United States

Florida Medical Clinic P.A.

🇺🇸

Zephyrhills, Florida, United States

GI Alliance - Illinois Gastro Group - Glenview

🇺🇸

Glenview, Illinois, United States

Grand Teton Research Group PLLC

🇺🇸

Idaho Falls, Idaho, United States

UnityPoint Health Peoria/Proctor

🇺🇸

Peoria, Illinois, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

St. Vincent Hospital

🇺🇸

Worcester, Massachusetts, United States

Detroit Receiving Hospital Department of Pharmacy Services

🇺🇸

Detroit, Michigan, United States

Aa Mrc Llc

🇺🇸

Flint, Michigan, United States

Harper Hospital Department of Pharmacy Services

🇺🇸

Detroit, Michigan, United States

William Beaumont Hospital

🇺🇸

Royal Oak, Michigan, United States

Revival Research Institute, LLC.

🇺🇸

Southfield, Michigan, United States

Mercury Street Medical Group PLLC

🇺🇸

Butte, Montana, United States

James J. Peters VAMC

🇺🇸

Bronx, New York, United States

New York Presbyterian Hospital Weill Cornell

🇺🇸

New York, New York, United States

Chattanooga Research and Medicine CHARM

🇺🇸

Chattanooga, Tennessee, United States

GI Alliance - Texas Digestive Disease Consultants - Arlington

🇺🇸

Arlington, Texas, United States

FMC Science

🇺🇸

Lampasas, Texas, United States

GI Alliance - Texas Digestive Disease Consultants - Webster

🇺🇸

Webster, Texas, United States

Instituto Medico Platense

🇦🇷

Buenos Aires, Argentina

Infectious Diseases Associates of Central VA

🇺🇸

Lynchburg, Virginia, United States

Hospital Privado Centro Medico Cordoba

🇦🇷

Cordoba, Argentina

Sunshine Coast University Hospital

🇦🇺

Birtinya, Queensland, Australia

DCC Alexandrovska

🇧🇬

Sofia, Bulgaria

Centre integre universitaire de sante et de services sociaux de la Mauricie-et-du-Centre-du-Quebec

🇨🇦

Trois-Rivières, Quebec, Canada

" ATTIKON University Hospital"

🇬🇷

Athens, Greece

Institut Universitaire de Cardiologie et de Pneumologie de Québec- ULaval

🇨🇦

Quebec, Canada

General Hospital of Athens ''Alexandra''

🇬🇷

Athens, Greece

University Hospital of Heraklion

🇬🇷

Heraklion, Greece

"Dél-Pesti Centrumkórház-OHII Szent László Kórház Infektológiai Osztály "

🇭🇺

Budapest, Hungary

Békés Megyei Központi Kórház Dr. Réthy Pál Tagkórház IV. Belgyógyászat - 2. Gasztroenterológia

🇭🇺

Békéscsaba, Hungary

Pécsi Tudományegyetem Klinikai Központi Gyógyszertár

🇭🇺

Pécs, Hungary

CRU Hungary Kft BAZ Megyei Kórház és Egyetemi Oktatókórház, Szent Ferenc Tagkórház

🇭🇺

Miskolc, Hungary

"Pécsi Tudományegyetem I. sz. Belgyógyászat i Klinika, Infektológiai tanszék"

🇭🇺

Pécs, Hungary

Wonju Severance Christian Hospital

🇰🇷

Ilsan-dong, Gangwondo, Korea, Republic of

Korea University Ansan Hospital

🇰🇷

Ansan-si, Gyeonggi-do, Korea, Republic of

Samsung Medical Center

🇰🇷

Irwon-dong, Seoul, Korea, Republic of

Hanyang University Seoul Hospital

🇰🇷

Ansan, Seoul, Korea, Republic of

Keimyung University Dongsan Hospital

🇰🇷

Daegu, Yeongnam, Korea, Republic of

Inje University Seoul Paik Hospital

🇰🇷

Junggu, Korea, Republic of

Kangdong Sacred Heart Hospital

🇰🇷

Seoul, Korea, Republic of

Kangbuk Samsung Hospital

🇰🇷

Seoul, Korea, Republic of

Korea University Guro Hospital

🇰🇷

Soeul, Korea, Republic of

Gabinet Lekarski Bartosz Korczowski

🇵🇱

Rzeszów, Podkarpackie, Poland

Szpital Zakonu Bonifratrów

🇵🇱

Katowice, Poland

Korczowski Bartosz Gabinet

🇵🇱

Rzeszow, Poland

ENDOSKOPIA Sp. z o.o.

🇵🇱

Sopot, Poland

Centralny Szpital Kliniczny MSWiA Klinika Chorób Wewnętrznych i Gastroenterologii

🇵🇱

Warszawa, Poland

Klinika Chorób Wewnętrznych i Gastroenterologii z Pododdziałem Leczenia Nieswoistych Chorób Zapalnych Jelit Centralny Szpital Kliniczny MSWiA

🇵🇱

Warszawa, Poland

Spitalul Clinic de Boli Infectioase si Tropicale

🇷🇴

Bucuresti, Romania

S.C. Sana Monitoring Srl

🇷🇴

Bucuresti, Romania

Spitalul Clinic de Boli Infectioase

🇷🇴

Iaşi, Romania

Spitalul Clinic Judetean de Urgenta Timisoara

🇷🇴

Timișoara, Romania

" State Budgetary Institution of Healthcare "City Clinical Hospital of n.a. V.M.Buyanova" "

🇷🇺

Moscow, Russian Federation

State budget healthcare institution of Novosibirsk region "City clinical hospital #2"

🇷🇺

Novosibirsk, Russian Federation

Hospital Universitario Cruces

🇪🇸

Barakaldo, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

"Hospital Universitario Marqués de Valdecilla "

🇪🇸

Santander, Spain

"Hospital Universtiario Donostia "

🇪🇸

Donostia, Spain

Hospital General Universitario Gregorio Marañon

🇪🇸

Madrid, Spain

Hospital Universitario de Balme

🇪🇸

Sevilla, Spain

Hospital Universitari Sant Joan de Reus

🇪🇸

Tarragona, Spain

Yeungnam University Medical Center

🇰🇷

Daegu, Seoul, Korea, Republic of

Kyungpook National University Hospital

🇰🇷

Daegu, Seoul, Korea, Republic of

HeuerMD Research Inc

🇺🇸

Orlando, Florida, United States

PMG Research of Winston-Salem

🇺🇸

Winston-Salem, North Carolina, United States

DM Clinical Research (Conroe Regional Hospital)

🇺🇸

Conroe, Texas, United States

GI Alliance - Texas Digestive Disease Consultants - Cedar Park

🇺🇸

Cedar Park, Texas, United States

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