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Level of Adherence of Subjects Receiving SAIZEN® Via Easypod™ Electromechanical Device for Growth Hormone Treatment

Completed
Conditions
Growth Disorders
Registration Number
NCT01438528
Lead Sponsor
Merck KGaA, Darmstadt, Germany
Brief Summary

This is a Chinese, Multicentre, Observational Study to study Adherence and Long Term Outcomes of Therapy in paediatric subjects using easypod™ electromechanical device for growth hormone treatment to assess the level of adherence of subject receiving SAIZEN® via easypod™.

Detailed Description

Subjects will be enrolled in a multicenter longitudinal observational study. Parents/subjects will provide their Informed Consent/assent to upload their data for population-based analyses and, ultimately, clinical outcomes. Adherence data will be primarily derived from the easypod™ device combined with physician data entry of outcome measures. Data will be collected retrospectively and prospectively. This will allow the establishment of adherence profiles and subsequent clinical outcomes. Collected data will be also analyzed in a multinational pooled analysis of comparable national studies.

Primary Objective:

* To assess the level of adherence of subjects receiving SAIZEN® via easypod™ Secondary Objectives:

* To describe the impact of adherence on clinical outcomes for subject receiving SAIZEN® via easypod™

* To identify adherence subject profiling

* To asses the impact of adherence on Insulin-like Growth Factor 1 (IGF1) (i.e. above, below or within normal ranges)

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
75
Inclusion Criteria
  • Over the age of >2 years
  • Under <18 years of age, or over 18 without fusion of growth plates
  • Patients diagnosed with growth hormone deficiency
  • Naïve to growth hormone treatment
  • Parent's or guardian's written informed consent, given before entering data into the observational study, with the understanding that the subject or parent/guardian may withdraw consent at any time without prejudice to future medical care. If the child is old enough (16 years old) to read and write, a separate assent form will be given as defined in the appropriate jurisdiction of each country.
Exclusion Criteria
  • Subjects taking growth hormone in whom growth plates have fused (i.e. for taking growth hormone for it's metabolic effects)
  • Contra-indications to SAIZEN® as defined in the Summary of Product Characteristics (SmPC)
  • Use of an investigational drug or participation in another interventional clinical study

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Mean percent of daily recorded adherenceAt least 6 months and up to 5 years
Secondary Outcome Measures
NameTimeMethod
Correlation of adherence and growth outcome after each year of SAIZEN® treatment with easypod™At least 6 months and up to 5 years

Correlation of adherence and growth outcome (change in: height velocity (HV), height velocity-standard deviation score (HV-SDS), height, height-standard deviation score(height SDS)) after each year of SAIZEN® treatment with easypod™

Subject adherence profile based on age, gender, indication, self-injection or not, time on treatmentAt least 6 months and up to 5 years
Correlation of adherence with current IGF-1 status (i.e. above, below or within normal ranges)At least 6 months and up to 5 years

Trial Locations

Locations (1)

For Recruiting Locations in China

🇨🇳

Please Contact The Merck KGaA Communication Center, China

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