IRCT20210413050958N7尚未招募1 期
The effects of N-Acetyl-L-Leucine on the improvement of symptoms in patients with Spinocerebellar ataxia
适应症
试验速览
- 阶段
- 1 期
- 状态
- 尚未招募
- 入组人数
- 4
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional
入排标准
- 年龄范围
- 6 years 至 no limit（—）
- 性别
- All
入选标准
- •Age above 6 years
- •Patients with a definitive diagnosis of Spinocerebellar ataxia
- •Having clinical signs
- •If the patient is taking any medication, he/she should maintain a constant dose/not change his/her treatment during the study period.
- •Have not taken any forbidden drugs including any variant of N-acetyl-DL-leucine, aminopyridines, Riluzole, gabapentin, Varenicline, Chlorzoxazone, sulfasalazine, Rosuvastatin at least 4 weeks before visit 1 and throughout the duration of the study
- •Signed informed consent form by the subjects or their parents after explaining the study objectives by the research team
- •Patient satisfaction
排除标准
- •Having chronic diarrhea, visual loss, malignancies or insulin-dependent diabetes mellitus
- •History of hypersensitivity to the N-Acetyl-Leucine
- •Having severe vision or hearing impairment
- •Having arthritis or other musculoskeletal disorders
研究者
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