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Phase II Study Using Thalidomide for the Treatment of ALS

Phase 2
Completed
Conditions
Amyotrophic Lateral Sclerosis
ALS
Registration Number
NCT00140452
Lead Sponsor
Dartmouth-Hitchcock Medical Center
Brief Summary

The use of Thalidomide in patients with ALS who have disease progression.

Detailed Description

Phase II open labeled trial testing the efficacy of thalidomide for ALS in the setting of disease progression.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
24
Inclusion Criteria
  • Clinically proven ALS
  • Disease duration less than or equal to 5 years
  • ALSFRS-R score equal to or greater then 30
Exclusion Criteria
  • Patients with known deep venous thrombosis or hyper coagulable state will be excluded
  • Patients with FVC less than 80%

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Primary Outcome Measures
NameTimeMethod
To evaluate the effect of Thalidomide in the rate of progression in ALS at 9 months and hence determine preliminary efficacy in the treatment of ALSEfficacy will be gauged according to the slopeof the expected average decline at nine months after starting Thalidomide
Secondary Outcome Measures
NameTimeMethod
To evaluate 1) toxicity 2) quality of life 3) cytokine profile 4) PFT's 5) sleep questionnaire and 6) survival of thalidomide in the treatment of ALSsurvival and progression free suvival will be assessed from the date of initial therapy on study to date od death. Survival and progresion free survival wil be analyzed using the Kaplan Meier method

Trial Locations

Locations (1)

Dartmouth Hichcock Medical Center

🇺🇸

Lebanon, New Hampshire, United States

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