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A Study Measuring Quality of Life, Treatment Preference and Satisfaction of ADPKD Patients in Europe

Conditions
Autosomal Dominant Polycystic Kidney Disease
Registration Number
NCT02848521
Lead Sponsor
Otsuka Pharmaceutical Europe Ltd
Brief Summary

This is a prospective, non-interventional study (NIS) measuring health-related quality of life (HRQoL), treatment satisfaction, and other patient-reported outcomes (PROs) of ADPKD patients in Europe.

Detailed Description

This is a prospective, non-interventional study (NIS) measuring HRQoL, treatment satisfaction, and other PROs of ADPKD patients in Europe. The study aims to enrol at least 486 patients. Data will be prospectively collected at clinics, from medical notes and via PRO measures for each patient at Baseline, Month 1, Month 3 and subsequently at 3 month intervals up to and including the final assessment (18 months maximum follow-up time). No visits with the patients' treating physician will be imposed by the protocol. Any clinical visits will occur as per normal clinical practice

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
407
Inclusion Criteria
  • Male and female aged ≥ 18 years.
  • Patient has a diagnosis of ADPKD between CKD Stages 1-3, and is deemed by their treating physician to likely have rapidly progressing disease.
  • Patient has a life expectancy greater than 18 months at time of enrolment.
  • Patient is able and willing to give informed consent, if required according to local regulations.
  • Patient is fluent in local language.
Exclusion Criteria
  • Patient is currently participating in, or has in the last 12 months participated in an interventional clinical trial.
  • Presence of any condition/circumstance which in the opinion of the investigator could significantly limit the complete follow up of the patient.
  • Inability of the patient to complete PROs remotely.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Mean rate of change (%) in Physical Health Composite Scale (PCS) scores of the 12-Item Short Form Survey (SF-12)From Baseline to end of study (maximum of 18 months)

Mean rate of change (%) in Physical Health Composite Scale (PCS) scores of the SF-12 from baseline to end of study, in the overall sample and per chronic kidney disease (CKD) stage.

Secondary Outcome Measures
NameTimeMethod
Description of real-world ADPKD treatment patterns (percentage of subjects taking different treatments)From Baseline to end of study (maximum of 18 months)
Mean Treatment Satisfaction Questionnaire for Medication (TSQM-9) score changesFrom Baseline to end of study (maximum of 18 months)

Mean TSQM-9 score changes from baseline to end of study, in the overall sample and per CKD stage (effectiveness, convenience and global satisfaction domain scores will be reported and analysed).

Mean ADPKD-IS score changesFrom Baseline to end of study (maximum of 18 months)

Mean ADPKD-IS scores changes from baseline to end of study, in the overall sample and per CKD stage (physical, emotional and fatigue domain scores will be reported and analysed).

Mean rate of change (%) in Mental Health Composite Scale (MCS) scores of the SF-12From Baseline to end of study (maximum of 18 months)

Mean rate of change (%) in Mental Health Composite Scale (MCS) scores of the SF-12 from baseline to end of study, in the overall sample and per CKD stage.

Mean ADPKD-Urinary Impact Scale (UIS) score changesFrom Baseline to end of study (maximum of 18 months)

Mean ADPKD-UIS score changes from baseline to end of study, in the overall sample and per CKD stage (frequency, urgency and nocturia domain scores will be reported and analysed).

Description of real-world ADPKD treatment patterns (number of subjects taking different treatments)From Baseline to end of study (maximum of 18 months)

Trial Locations

Locations (26)

LKH Villach

🇦🇹

Villach, Austria

UZ Leuven/Gasthuisberg KUL

🇧🇪

Leuven, Belgium

CHU Nimes - Hôpital CAREMEAU

🇫🇷

Nimes, France

Necker Hospital

🇫🇷

Paris, France

Clinique La Louviere

🇫🇷

Lille, France

Hopital Tenon

🇫🇷

Paris, France

CHU TOURS - Hôpital Bretonneau

🇫🇷

Tours, France

University Medical Center Schleswig-Holstein

🇩🇪

Lubeck, Germany

Charite Berlin

🇩🇪

Berlin, Germany

Universitätsmedizin Göttingen

🇩🇪

Gottingen, Germany

Fundación Puigvert

🇪🇸

Barcelona, Spain

Hospital Clinic

🇪🇸

Barcelona, Spain

Hospital Vall d'Hebron

🇪🇸

Barcelona, Spain

Hospital Universitario de Getafe

🇪🇸

Getafe, Spain

Edinburgh Royal Infirmary

🇬🇧

Edinburgh, United Kingdom

Royal Free Hospital

🇬🇧

London, United Kingdom

Queen Elizabeth University Hospital

🇬🇧

Glasgow, United Kingdom

Aintree University Hospital

🇬🇧

Liverpool, United Kingdom

Royal London Hospital

🇬🇧

London, United Kingdom

Freeman Hospital

🇬🇧

Newcastle, United Kingdom

AKH Wien

🇦🇹

Vienna, Austria

University Hospital of Zurich

🇨🇭

Zürich, Switzerland

UZ Brussels

🇧🇪

Brussels, Belgium

University Hospital of Geneve

🇨🇭

Genève, Switzerland

CHU Liège - Domaine Universitaire du Sart Tilman

🇧🇪

Liege, Belgium

UCL Brussels

🇧🇪

Brussels, Belgium

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