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Double-blind, Multicenter Study to Assess the Efficacy of Bilateral Pallidal Stimulation in Patients With Medically Refractory Primary Cervical Dystonia

Phase 3
Completed
Conditions
Cervical Dystonia
Interventions
Device: Deep brain stimulation (DBS)
Registration Number
NCT00148889
Lead Sponsor
German Parkinson Study Group (GPS)
Brief Summary

The purpose of this study is to investigate the efficacy and safety of bilateral pallidal stimulation in patients with medically refractory primary cervical dystonia.

Detailed Description

Primary cervical dystonia (CD) affects about 20-40/100.000 population. The disease is chronic and life-long. The therapy of choice are local intramuscular Botulinum Toxin injections given every three months. Oral medication such as anticholinergics or dopamine depleting drugs are usually of limited efficacy or their use is limited by intolerable side-effects. About 5-10% of CD patients develop neutralizing antibodies against Botulinum Toxin. Two previous controlled multicenter trials have shown the efficacy and safety of bilateral pallidal stimulation in patients with primary segmental and generalized dystonia (one study was performed by our group).

Following surgery, patients will be randomized 1:1 to verum or placebo stimulation for a period of three months. Primary outcome measure is the TWSTRS (Toronto Western Spasmodic Torticollis Rating Scale) - a validated and widely accepted physician-based outcome measure for cervical dystonia. The independent TWSTRS raters are movement disorders specialists unaware of the stimulation status (verum/placebo) and they compare the TWSTRS-score at baseline and 3-months follow-up. Our hypothesis is that stimulated patients will have a significantly better improvement of dystonia as compared to those without stimulation (placebo group).

After the 3-months period, all patients are unblinded and receive continuous effective stimulation by the implanted system. Regular follow-up visits are scheduled every 12 months for 5 years postoperatively to assess the long-term efficacy of pallidal stimulation. Side-effects are assessed in a standardized way and include the assessment of surgery-induced as well as stimulation-induced side-effects.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
63
Inclusion Criteria
  • Primary cervical dystonia
  • Disease duration 3 years or longer
  • Adult patient (18 years or older)
  • TWSTRS severity score 15 or more
  • Non-response to Botulinum Toxin
  • Non-response to oral antidystonic medication
  • Informed consent
Exclusion Criteria
  • Dementia (Mattis Dementia Rating Scale below 120)
  • Severe depression (Beck Depression Inventory >25)
  • Previous functional stereotactic surgery
  • Hemidystonia or generalized dystonia
  • Severe brain atrophy
  • Contraindication against surgery

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
1Deep brain stimulation (DBS)Active GPI-DBS
2Deep brain stimulation (DBS)Sham-stimulation
Primary Outcome Measures
NameTimeMethod
Toronto Western Spasmodic Torticollis Scale (TWSTRS) at 3 months following surgery (comparison between placebo and control group)3 months
Secondary Outcome Measures
NameTimeMethod
side-effects, quality of life, depression, pain, long-term efficacy5 years

Trial Locations

Locations (10)

Medical University Innsbruck, Department of Neurology

🇦🇹

Innsbruck, Tyrol, Austria

Department of Neurosurgery, Medical University Vienna

🇦🇹

Vienna, Austria

Department of Neurology, University Kiel

🇩🇪

Kiel, Germany

Department of Neurology, University Heidelberg

🇩🇪

Heidelberg, Germany

Department for Stereotaxy and Functional Neurosurgery, University Cologne

🇩🇪

Köln, Germany

Department of Neurology, Charité, Humboldt-University Berlin

🇩🇪

Berlin, Germany

Hertie-Institute for Clinical Brain Research

🇩🇪

Tübingen, Germany

Department of Neurology, University Regensburg

🇩🇪

Regensburg, Germany

Department of Neurology, University Rostock

🇩🇪

Rostock, Germany

Clinic of Neurosurgery, Medical University Hannover

🇩🇪

Hannover, Germany

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