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AMR PH GL 2007 CL001 Phase 3 Trial in Patients With Small Cell Lung Cancer After Failure of First-Line Chemotherapy

Phase 3
Completed
Conditions
Small Cell Lung Cancer
Interventions
Registration Number
NCT00547651
Lead Sponsor
Celgene
Brief Summary

This study drug (Amrubicin) is believed to work by stopping the tumor cells in your body from growing. The purpose of this study is to evaluate the effect of amrubicin compared to topotecan in the treatment of small cell lung cancer.

Detailed Description

Small cell lung cancer represents approximately 13% of the cancers of the lung and presents as extensive stage disease in 60% to 70% of patients. Sites of metastases include bone (35%), liver (25%), bone marrow (20%), brain (10%), extrathoracic lymph nodes (5%), and subcutaneous masses (5%). Small-cell lung cancer has prominent markers of neuroendocrine differentiation.

The staging classification for SCLC is the 2-stage Veterans Administration Lung Study Group system that categorizes patients as having limited or extensive disease. Limited stage SCLC is disease confined to 1 hemithorax with or without adjacent mediastinal and/or supraclavicular lymph node involvement, but without a pleural effusion. This extent of disease can be included in a tolerable radiation field. Extensive-disease SCLC is any disease beyond the definition of limited-stage disease.

There are few proven treatment options for SCLC patients who fail first-line chemotherapy. New treatment strategies must be evaluated. The need to discover active agents with better toxicity profiles continues to be of great importance. Amrubicin may be an effective treatment for this population.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
637
Inclusion Criteria
  • Histological or cytological diagnosis of SCLC at study entry according to the International Association for the Study of Lung Cancer (IASLC) histopathologic classification. Mixed or combined subtypes according to the IASLC are not allowed;
  • SCLC that is either sensitive (defined as a response including stable disease to first-line platinum-based chemotherapy, with subsequent progression >/= 90 days after completing first-line chemotherapy) or refractory (defined as best response to first-line platinum-based chemotherapy or progression < 90 days after completing first-line chemotherapy);
  • Extensive or limited disease; patients with limited disease who are candidates for local or regional salvage radiation therapy must have been offered such treatment prior to participation in this study;
  • Radiographically documented progression after first-line treatment with platinum-based chemotherapy;
  • No more than 1 prior chemotherapy regimen;
  • At least 18 years of age;
  • ECOG performance status of 0 - 1
Exclusion Criteria
  • Chest radiotherapy with curative intent to the primary disease complex </= 28 days prior to first dose; CNS radiotherapy </= 21 days prior to first dose; radiotherapy to all other areas </= 7 days prior to first dose;
  • Prior anthracycline, topotecan, or irinotecan treatment.
  • Prior anthracycline or topotecan treatment.
  • Patients with know history of seropositive human immunodeficiency virus (HIV) or patients who are receiving immunosuppressive medications that would increase the risk of serious neutropenic complications

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
AmrubicinAmrubicinAmrubicin
TopotecanTopotecanTopotecan
Primary Outcome Measures
NameTimeMethod
The primary objective is to demonstrate superiority in overall survival of amrubicin compared with topotecan hydrochloride in patients with small cell lung cancer (SCLC) after failure of first-line chemotherapy.Until death from any cause
Secondary Outcome Measures
NameTimeMethod
To further characterize the clinical benefit of amrubicin compared with topotecan in terms of objective response rateUntil death
To further characterize the clinical benefit of amrubicin compared with topotecan in terms of safetyUntil death
To further characterize the clinical benefit of amrubicin compared with topotecan in terms of time to tumor progressionUntil death
To further characterize the clinical benefit of amrubicin compared with topotecan in terms of duration of responseUntil death
To further characterize the clinical benefit of amrubicin compared with topotecan in terms of quality of lifeUntil death
To further characterize the clinical benefit of amrubicin compared with topotecan in terms of progression-free survival.Until death

Trial Locations

Locations (138)

Northwest Alabama Cancer Center

🇺🇸

Muscle Shoals, Alabama, United States

Cedars-Sinai Outpatient Cancer Center

🇺🇸

Los Angeles, California, United States

Cancer Care Associates of Fresno Medical Group, Inc.

🇺🇸

Fresno, California, United States

Medical Oncology Associates of Augusta

🇺🇸

Augusta, Georgia, United States

Joliet Oncology-Hematology Associates, Ltd.

🇺🇸

Joliet, Illinois, United States

Cancer & Hematology Specialists of Chicago (Main)

🇺🇸

Niles, Illinois, United States

Cancer Care at Blessing Hospital

🇺🇸

Quincy, Illinois, United States

Hope Center

🇺🇸

Terre Haute, Indiana, United States

Alliance Hematology Oncology, P.A. (Main)

🇺🇸

Westminster, Maryland, United States

Kalamazoo Hematology and Oncology

🇺🇸

Kalamazoo, Michigan, United States

Missouri Cancer Associates

🇺🇸

Columbia, Missouri, United States

St. Joseph Oncology, Inc.

🇺🇸

Saint Joseph, Missouri, United States

New York Oncology Hematology, P.C.

🇺🇸

Latham, New York, United States

SUNY Upstate Medical University - Regional Oncology Center

🇺🇸

Syracuse, New York, United States

Lineberger Comprehensive Cancer Center

🇺🇸

Chapel Hill, North Carolina, United States

Cancer Centers of North Carolina (Main)

🇺🇸

Raleigh, North Carolina, United States

Gabrail Cancer Center

🇺🇸

Canton, Ohio, United States

Greater Dayton Cancer Center (Main)

🇺🇸

Kettering, Ohio, United States

Cancer Care Associates

🇺🇸

Tulsa, Oklahoma, United States

Medical Oncology Associates

🇺🇸

Kingston, Pennsylvania, United States

UPMC Cancer Pavilion

🇺🇸

Pittsburgh, Pennsylvania, United States

Texas Oncology, P.A.

🇺🇸

Webster, Texas, United States

Thomas Jefferson Memorial Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Coastal Bend Cancer Center

🇺🇸

Corpus Christi, Texas, United States

Texas Cancer Center at Medical City (Main)

🇺🇸

Dallas, Texas, United States

West Texas Cancer Center-Texas Oncology

🇺🇸

Odessa, Texas, United States

Texas Oncology, P.A. (Main)

🇺🇸

Dallas, Texas, United States

Virginia Oncology Associates

🇺🇸

Norfolk, Virginia, United States

Fairfax Northern Virginia Hematology/Oncology

🇺🇸

Fairfax, Virginia, United States

Texoma Cancer Center

🇺🇸

Wichita Falls, Texas, United States

Blue Ridge Cancer Care

🇺🇸

Roanoke, Virginia, United States

Northwest Cancer Specialists - Vancouver (Main)

🇺🇸

Vancouver, Washington, United States

Royal North Shore Hospital

🇦🇺

St. Leonards, New South Wales, Australia

New South Wales Southern Medical Day Care Centre

🇦🇺

Wollongong, New South Wales, Australia

The Queen Elizabeth Hospital

🇦🇺

Woodville South, Australia

MHAT "Tsaritsa Yoanna"

🇧🇬

Sofia, Bulgaria

London Regional Cancer Centre

🇨🇦

London, Ontario, Canada

Humber River Regional Hospital

🇨🇦

Weston, Ontario, Canada

Fakultni Nemocnice Ostrava

🇨🇿

Ostrava-Poruba, Czechia

Fakultní Thomayerova nemocnice s poliklinikou

🇨🇿

Praha, Czechia

Faculty Hospital Motol

🇨🇿

Praha 5, Czechia

Masarykova nemocnice v Ústí nad Labem

🇨🇿

Ústí nad Labem, Czechia

Herlev Hospital, Onkologisk afdeling R

🇩🇰

Herlev, Denmark

CHU Montpellier - Unité de Cancérologie Thoracique

🇫🇷

Montpellier Cedex, France

Krankenhaus Grosshansdorf, Zentrum fur Pneumologie und Thoraxchirurgie

🇩🇪

Grosshansdorf, Germany

Klinikum Mannheim GmbH, Chirugische Klinik, Thorakale Onkologie

🇩🇪

Mannheim, Germany

Policlinico di Modena - University of Modena & Reggio Emilia, Dept Oncology & Hematology

🇮🇹

Modena, Italy

Nederlands Kanker Instituut - Antoni van Leeuwenhoek Ziekenhuis

🇳🇱

Amsterdam, Netherlands

Ospedale S.S. Trinita

🇮🇹

Sora, Italy

VU University Medical Center Amsterdam

🇳🇱

Amsterdam, Netherlands

Wielkopolskie Centrum Pulmonologii i Tarakochirurgii Oddzial Onkologii Klinicznej z Pododdzialem Dziennej Chemioterapii

🇵🇱

Poznan, Poland

Szpital Specjalistyczny w Prabutach

🇵🇱

Prabuty, Poland

Hospital Universitario Germans Trias i Pujol

🇪🇸

Barcelona, Spain

Fundación Jiménez Díaz. Universidad Autónoma de Madrid

🇪🇸

Madrid, Spain

Duran i Reynals Institut Catala d'Oncologia

🇪🇸

L'Hospitalet de Llobregat, Spain

Hospital Universitario Virgin de la Victoria

🇪🇸

Malaga, Spain

Hospital General Universitario de Valencia

🇪🇸

Valencia, Spain

Edinburgh Cancer Research Centre

🇬🇧

Edinburgh, United Kingdom

Beatson West of Scotland Cancer Centre

🇬🇧

Glasgow, United Kingdom

The Royal Marsden NHS Foundation Trust

🇬🇧

Surrey, United Kingdom

Christie Hospital NHS Foundation Trust

🇬🇧

Manchester, United Kingdom

Little Rock Hematology Oncology Associates

🇺🇸

Little Rock, Arkansas, United States

Arizona Oncology Associates

🇺🇸

Tucson, Arizona, United States

Ocala Oncology Center

🇺🇸

Ocala, Florida, United States

Cancer Centers of Florida, P.A.

🇺🇸

Ocoee, Florida, United States

Jayne Gurtler MD, Laura Brizn MD, Angelo Russo MD, and Janet Burroff MD, APMC

🇺🇸

Metairie, Louisiana, United States

Florida Oncology Associates

🇺🇸

Orange Park, Florida, United States

Sacred Heart Medical Oncology

🇺🇸

Pensacola, Florida, United States

Maine Center for Cancer Medicine and Blood Disorders

🇺🇸

Scarborough, Maine, United States

Michigan Hematology & Oncology Institute

🇺🇸

Southgate, Michigan, United States

Marshfield Clinic

🇺🇸

Marshfield, Wisconsin, United States

Cancer Centers of the Carolinas (Main)

🇺🇸

Greenville, South Carolina, United States

Klinikum Weis-Grieskirchen GmbH

🇦🇹

Wels, Austria

Krankenhaus Hietzing, 5 Med. Abteilung mit Onkologie

🇦🇹

Wien, Austria

The Princess Alexandra Hospital, Dept of Respiratory Medicine

🇦🇺

Woolloongabba, Queensland, Australia

Flinders Medical Centre

🇦🇺

Bedford Park, South Australia, Australia

Allgemeines Krankenhaus der Stadt Linz, Abteilung fur Atem und Lungenkrankheiten

🇦🇹

Linz, Austria

University Multiprofile Hospital for Active Treatment "Sveta Marina"

🇧🇬

Varna, Bulgaria

Princess Margaret Hospital

🇨🇦

Toronto, Ontario, Canada

Allegemeines Krankenhaus Wien, Univ. Klinik fur Innere, Medizin I

🇦🇹

Wien, Austria

III-rd Internal Department, District Dispensary for Oncology diseases with stationary(DDOncDIU)

🇧🇬

Plovdiv, Bulgaria

UZ Brussel, Medical Oncology and Hematology

🇧🇪

Brussel, Belgium

Centre Hospitalier Notre-Dame et Reine Fabiola

🇧🇪

Charleroi, Belgium

Fraser Valley Cancer Centre-Surrey Memorial Hospital

🇨🇦

Surrey, British Columbia, Canada

Universitair Ziekenhuis Antwerpen, Dept. Respiratory Diseases

🇧🇪

Edegem, Belgium

UZ Gasthuisberg, UZ Leuven

🇧🇪

Leuven, Belgium

C.H.U. Sart-Tilman

🇧🇪

Liege, Belgium

Hôpital de la Croix-Rousse

🇫🇷

Lyon Cedex 04, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

Royal Victoria Hospital

🇨🇦

Montreal, Quebec, Canada

DDOncDIU Sofia District

🇧🇬

Sofia, Bulgaria

Charité Universitätsmedizin Berlin

🇩🇪

Berlin, Germany

Centre François Baclesse

🇫🇷

Caen Cedex 5, France

Universitätsklinikum Essen Innere Klinik und Poliklinik

🇩🇪

Essen, Germany

Azienda Ospedaliera San Camillo Forlanini

🇮🇹

Roma, Italy

Zentralklinik Bad Berka GmbH

🇩🇪

Bad Berka, Germany

Elkerliek Ziekenhuis, Locatie Helmond

🇳🇱

Helmond, Netherlands

Klinika Nowotworow Ukladowych i Uogolnionych Centrum Onkologii, Instytut im. Marii Sklodowskiej-Curie

🇵🇱

Kraków, Poland

Centrum Onkologii Ziemi Lubelskiej

🇵🇱

Lublin, Poland

Wojewódzki Szpital Chorób Pluc im Alojzego Pawelca w Wodzislawiu Slaskim

🇵🇱

Wodzislaw Slaski, Poland

Kantonsspital Aarau

🇨🇭

Aarau, Switzerland

Asklepios Fachkliniken Muenchen Gauting

🇩🇪

Gauting, Germany

Staedtisches Krankenhaus Martha-Maria Halle-Doelau

🇩🇪

Halle (Saale), Germany

DEODEC

🇭🇺

Debrecen, Hungary

Thoraxklinik am Universitätsklinikum Heidelberg AG

🇩🇪

Heidelberg, Germany

Katholisches Klinikum Mainz, St. Hildegardis Krankenhaus

🇩🇪

Mainz, Germany

County Hospital Baranya

🇭🇺

Pecs, Hungary

Erzsébet Hospital Sopron

🇭🇺

Sopron, Hungary

St. Vincentius-Kliniken Karlsruhe, Hamatologie, Med Onkologie und Immunologie

🇩🇪

Karlsruhe, Germany

Semmelweis University of Medicine

🇭🇺

Budapest, Hungary

Országos Korányi Tbc és Pulmonológiai Intézet

🇭🇺

Budapest, Hungary

Matrai Gyogyintezet

🇭🇺

Matrahaza, Hungary

Ospedale S. Maria della Misericordia

🇮🇹

Perugia, Italy

Specjalistyczny Zespol Chorob Pluc i Gruzlicy w Bystrej

🇵🇱

Bystra, Poland

University Medical Center Groningen

🇳🇱

Groningen, Netherlands

Erasmus MC - Daniel den Hoed

🇳🇱

Rotterdam, Netherlands

Zespol nr 1 Szpitala im. St. Leszczynskiego

🇵🇱

Katowice, Poland

Akademickie Centrum Kliniczne

🇵🇱

Gdansk, Poland

Kantonsspital Graubünden

🇨🇭

Chur, Switzerland

Universitätsspital Zürich

🇨🇭

Zurich, Switzerland

Kansas City Cancer Center (Main)

🇺🇸

Overland Park, Kansas, United States

Advanced Medical Specialties

🇺🇸

Miami, Florida, United States

Central Indiana Cancer Centers

🇺🇸

Indianapolis, Indiana, United States

University of Minnesota Medical Center, Cancer Center

🇺🇸

Minneapolis, Minnesota, United States

Comprehensive Care Centers of Nevada (Main)

🇺🇸

Las Vegas, Nevada, United States

Regional Cancer Care

🇺🇸

Durham, North Carolina, United States

The Sarah Cannon Research Institute/TN Oncology

🇺🇸

Nashville, Tennessee, United States

Odense Universitetshospital,Onkologisk afdeling R

🇩🇰

Odense C, Denmark

Rikshospitalet, Finsen Center

🇩🇰

Copenhagen, Denmark

Rocky Mountain Cancer Center - Midtown (Main)

🇺🇸

Denver, Colorado, United States

University of Colorado Health Science Centre

🇺🇸

Aurora, Colorado, United States

Center for Cancer and Blood Disorders

🇺🇸

Bethesda, Maryland, United States

Illinois Cancer Care

🇺🇸

Peoria, Illinois, United States

Piedmont Hematology Oncology Associates

🇺🇸

Winston-Salem, North Carolina, United States

Cancer Center of Kansas

🇺🇸

Wichita, Kansas, United States

Tulane University Health Sciences Center

🇺🇸

New Orleans, Louisiana, United States

Willamette Valley Cancer Center (Main)

🇺🇸

Eugene, Oregon, United States

Sinai Hospital of Baltimore, Inc.

🇺🇸

Baltimore, Maryland, United States

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