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Safety, Pharmacokinetic and Preliminary Efficacy Study of AC0010 in Patients With EGFR T790M Positive NSCLC

Phase 1
Conditions
Metastatic Non-small Cell Lung Cancer
Interventions
Drug: AC0010
Registration Number
NCT02330367
Lead Sponsor
Hangzhou ACEA Pharmaceutical Research Co., Ltd.
Brief Summary

AC0010 is a novel, potent, small molecule irreversible tyrosine kinase inhibitor (TKI) that selectively targets mutant forms of the epidermal growth factor receptor (EGFR) while sparing wild-type (WT) EGFR. The purpose of the study is to evaluate the pharmacokinetic (PK) and safety profile of oral AC0010; to determine the maximum tolerated dose (MTD) and/or recommended Phase 2 dose (RP2D) of oral AC0010; to assess the safety and efficacy of AC0010 in previously treated mutant EGFR in NSCLC patients with EGFR T790M mutation.

Detailed Description

Lung cancer remains the most common cancer worldwide with non-small cell lung cancer (NSCLC) accounting for 85% of cases. Molecularly targeted therapies have proven to be superior to chemotherapy for NSCLC patients whose tumors have mutations in EGFR. Recent studies have established tyrosine kinase inhibitors (TKIs) as the gold standard for treating EGFR-mutation-positive NCSLC. However, patients on TKIs eventually progress, and in approximately 50% of cases, progression is due to development of an additional mutation called T790M. AC0010 may provide an effective therapy for a patient population with few alternative treatment options. Pre-clinical data demonstrated that AC0010 inhibits T790M. It is anticipated that AC0010 may promote cell death in tumor cells with the T790M mutation, thus providing possible therapeutic benefit in patients who have developed T790M-mediated resistance to previous TKIs.

This is a two-part, open-label study of oral AC0010 administered twice-daily in previously treated NSCLC patients who have documented evidence of an activating mutation in the EGFR gene and have failed treatment with an EGFR inhibitor such as erlotinib, gefitinib or afatinib.

This study will include 2 parts:

phase 1 : Dose-escalation Period with 28-day cycles; Optional Treatment Extension Period starting on Day 29

phase 2 : Evaluation of activity and safety in patients with the EGFR T790M mutation

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
368
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
AC0010AC0010Oral AC0010 monotherapy
Primary Outcome Measures
NameTimeMethod
ORR(Objective Response Rate)Every 6 weeks from time of first dose until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 11 months

To assess the overall objective response rate (ORR) of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

Secondary Outcome Measures
NameTimeMethod
OS (Overall survival)Every 6 weeks from time of first dose until objective disease progression, then every 3 months until death of lost of follow-up, up to approximately 18 months

To assess the overall survival (OS) of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

PFS (Progression-free survival)Every 6 weeks from time of first dose until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 11 months

To assess the progression-free survival (PFS) of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

Adverse eventsFrom screening to 30days after end of treatment, which is assessed through study completion

To assess the safety of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

DoR (Duration of Response)Every 6 weeks from time of first dose until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 11 months

To assess the duration of response (DOR) of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

DCR (Disease control rate)Every 6 weeks from time of first dose until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 11 months

To assess the disease control rate (DCR) of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

EORTC QLQ-C30 and LC-13 questionnaireFrom screening to the end of survival follow-up, which is assessed though study completion

To assess the safety of AC0010 in EGFR T790M mutation-positive patients with advanced non-small cell lung cancer (NSCLC).

Trial Locations

Locations (17)

Jiangsu Province Hospital

🇨🇳

Nanjing, Jiangsu, China

Jilin Cancer Hospital

🇨🇳

Chang Chun, Jilin, China

Beijing Cancer Hospital

🇨🇳

Beijing, Beijing, China

Peking Union Medical College Hospital

🇨🇳

Beijing, Beijing, China

Guangdong Provincial People's Hospital

🇨🇳

Guangzhou, Guangdong, China

Jiangsu Cancer Hospital

🇨🇳

Nanjing, Jiangsu, China

The Second Affiliated Hospital of Zhejiang University School of Medicine

🇨🇳

Hanzhou, Zhejiang, China

Shanghai Chest Hospital

🇨🇳

Shanghai, Shanghai, China

Chinese PLA General Hospital

🇨🇳

Beijing, Beijing, China

307 Hospital of PLA

🇨🇳

Beijing, Beijing, China

Cancer Hospital Chinese Academy of Medical Sciences

🇨🇳

Beijing, Beijing, China

Fujian Medical University Union Hospital

🇨🇳

Fuzhou, Fujian, China

Sun Yat-sen University Cancer Center

🇨🇳

Guangzhou, Guangdong, China

Hunan Cancer Hospital

🇨🇳

Changsha, Hunan, China

Nanjing General Hospital of Nanjing Military Command

🇨🇳

Nanjing, Jiangsu, China

West China Hospital,Sichuan University

🇨🇳

Chendu, Sichuan, China

The First Affiliated Hospital, Zhejiang University

🇨🇳

Hangzhou, Zhejiang, China

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