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Apremilast study in children with active oral ulcers associated with Behçet's Disease or Juvenile Psoriatic Arthritis

Phase 1
Conditions
Subjects with active Behçet's Disease or Juvenile Psoriatic Arthritis
MedDRA version: 21.1Level: LLTClassification code 10004212Term: Behcet's diseaseSystem Organ Class: 100000004866
MedDRA version: 20.0Level: LLTClassification code 10079454Term: Systemic juvenile idiopathic arthritisSystem Organ Class: 100000004859
Therapeutic area: Diseases [C] - Immune System Diseases [C20]
Registration Number
EUCTR2022-003024-41-ES
Lead Sponsor
Amgen Inc
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Authorised-recruitment may be ongoing or finished
Sex
All
Target Recruitment
48
Inclusion Criteria

1. Subject’s legally authorized representative has provided informed consent when the subject is legally too young to provide informed consent and the subject has provided written assent based on local regulations and/or guidelines prior to any study-specific activities/procedures being initiated.
2. Subject must have completed week 52 (Apremilast Active Treatment Phase) of Study 20190529 (from France and Turkey sites only) or Study 20190530 where drug is not commercially available in their country.
3. Subject must have an age and sex specific body mass index (BMI) value no lower in range than the 5th percentile on the Centers for Disease Control (CDC) growth chart (Appendix 11.7) for children and adolescents (CDC, 2000) at randomization.
4. Subject is willing and able to adhere to the study visit schedule and other protocol requirements.
5. Subject must have acceptable benefit/risk for continued treatment with apremilast.
Are the trial subjects under 18? yes
Number of subjects for this age range: 40
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 8
F.1.3 Elderly (>=65 years) no
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

1. Answer Yes” to any question on the Columbia-Suicide Severity Rating Scale (C-SSRS) at the week 52 visit on Study 20190529 (subjects from France and Turkey sites only) or Study 20190530.
2. Scheduled surgery or other interventions that would interrupt the subject’s participation in the study.
3. Female subjects of childbearing potential (for the purpose of this study, a female subject is considered of childbearing potential if she is 12 years old or older or has reached menarche, whichever occurred first) unwilling to use protocol specified method of contraception see Appendix 5 (Section 11.5) during treatment and for an additional 30 days after the last dose of investigational product.
4. Female subjects planning to become pregnant while on study through 30 days after the last dose of investigational product.
5. Female subjects of childbearing potential with a positive pregnancy test assessed at week 0 by a highly sensitive urine or serum pregnancy test.
6. Subject has known sensitivity to any of the products to be administered during dosing.
7. Subject likely to not be available to complete all protocol-required study visits.

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Main Objective: Evaluate the long-term safety of apremilast in subjects 2 years of age or older with oral ulcers associated with Behçets disease or 5 years of age or older with active JPsA that have completed Study 20190530 or Study 20190529;Secondary Objective: Not applicable;Primary end point(s): - Adverse events: Type, frequency, severity, and relationship to apremilast<br>- Columbia-Suicide Severity rating Scale (C-SSRS)<br>- Tanner Staging<br>- Body weight, height, and body mass index (BMI) <br>- Vital signs and laboratory parameters;Timepoint(s) of evaluation of this end point: week 0, 26 , 52, 78, 104, 130 , 156 , 182 , 208 and 212
Secondary Outcome Measures
NameTimeMethod
Secondary end point(s): Not applicable;Timepoint(s) of evaluation of this end point: Not applicable
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