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Butyrate in Pediatric Inflammatory Bowel Disease

Not Applicable
Completed
Conditions
Inflammatory Bowel Diseases
Interventions
Dietary Supplement: sodium butyrate
Other: placebo
Registration Number
NCT05456763
Lead Sponsor
Centre of Postgraduate Medical Education
Brief Summary

The first prospective randomised placebo-controlled study in the IBD pediatric population was conducted to evaluate the effectiveness of oral sodium butyrate as add-on therapy in IBD.

Detailed Description

Butyric acid's effectiveness has not yet been assessed in the pediatric inflammatory bowel disease (IBD) population. This study aimed to evaluate the effectiveness of oral sodium butyrate as an add-on to standard therapy in children and adolescents with newly diagnosed IBD.

This was a prospective, randomized, placebo-controlled multicentre study. Patients aged 6-18 years with colonic Crohn's disease or ulcerative colitis, who received standard therapy depending on the disease's severity, were randomized to receive 150 mg sodium butyrate twice a day (group A) or placebo (group B). The primary outcome was the difference in disease activity and fecal calprotectin concentration between the two study groups measured at 12 weeks of the study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
100
Inclusion Criteria
  • 6 to 18 years of age;
  • newly diagnosed, based on the modified Porto criteria, IBD with colon involvement;
  • informed consent of the child's parents or guardians to participate in the study.
Exclusion Criteria
  • age <6 years;
  • taking probiotics or dietary supplements in the last 2 weeks prior to study enrollment;
  • lack of consent of parents or guardians to participate in the study.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
group Asodium butyrate150 mg sodium butyrate twice a day for 12 weeks
group Bplaceboplacebo capsules twice a day for 12 weeks
Primary Outcome Measures
NameTimeMethod
difference in remission rate (PUCAI ulcerative colitis)12 weeks

The Pediatric Ulcerative Colitis Activity Index (PUCAI) measured in points of activity was used to assess UC activity.

Severity of the disease:

\<10 points = remission 10-34 points = mild ulcerative colitis 35-64 points = moderate ulcerative colitis

≥65 points = severe ulcerative colitis

In this scale addominal pain (mild or moderate/severe), number of stools per day, blood in the stool, stool consistency, nocturnal stools and activity level (no limitation, occasional or restricted), are assessed. The scale is validated and used in daily clinical practice.

Remission was defined as less than 10 points for both PCDAI and PUCAI scores.

difference in remission rate (PCDAI for Crohn's disease)12 weeks

The Pediatric Crohn's Disease Activity Index (PCDAI) measured in points of activity was used to assess CD activity.

Severity of the disease:

\<10 points = remission 10-27.5 points = mild Crohn's Disease 30-37.5 points = moderate Crohn's Disease

≥40 points = severe Crohn's Disease

In this scale addominal pain (mild or moderate/severe), number of stools per day, general well being (good, below par, very poor), antropometric measures, palpable mass in the abdomen and perianal fistulas are assessed. The scale is validated and used in daily clinical practice.

Remission was defined as less than 10 points for both PCDAI and PUCAI scores.

Secondary Outcome Measures
NameTimeMethod
difference in disease activity for CD and UC patients12 weeks

assessed separately, calcultated in points (described above)

difference in calprotectin concentration12 weeks

measured in µg/g assessed in different soubgroups (lower result is better, remission = less than 50.

side effects12 weeks

assessed for both groups (descriptive)

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